دورية أكاديمية
P021: Long-term follow-up of cipaglucosidase alfa/miglustat in ambulatory and non-ambulatory patients with Pompe disease: An open-label phase I/II study (ATB200-02)
| العنوان: | P021: Long-term follow-up of cipaglucosidase alfa/miglustat in ambulatory and non-ambulatory patients with Pompe disease: An open-label phase I/II study (ATB200-02) |
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| المؤلفون: | Priya Kishnani, Benedikt Schoser, Drago Bratkovic, Paula Clemens, Ozlem Goker-Alpan, Xue Ming, Mark Roberts, Matthias Vorgerd, Kumaraswamy Sivakumar, Ans van der Ploeg, Mitchell Goldman, Jacquelyn Wright, Fred Holdbrook, Vipul Jain, Sheela Sitaraman Das, Yasmine Wasfi, Tahseen Mozaffar, Barry Byrne |
| المصدر: | Genetics in Medicine Open, Vol 1, Iss 1, Pp 100031- (2023) |
| بيانات النشر: | Elsevier, 2023. |
| سنة النشر: | 2023 |
| المجموعة: | LCC:Genetics LCC:Medicine |
| مصطلحات موضوعية: | Genetics, QH426-470, Medicine |
| نوع الوثيقة: | article |
| وصف الملف: | electronic resource |
| اللغة: | English |
| تدمد: | 2949-7744 |
| العلاقة: | http://www.sciencedirect.com/science/article/pii/S2949774423000316Test; https://doaj.org/toc/2949-7744Test |
| DOI: | 10.1016/j.gimo.2023.100031 |
| الوصول الحر: | https://doaj.org/article/41cbbd3dd64e477caa62c2aca904b5deTest |
| رقم الانضمام: | edsdoj.41cbbd3dd64e477caa62c2aca904b5de |
| قاعدة البيانات: | Directory of Open Access Journals |
Full Text Finder | تدمد: | 29497744 |
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| DOI: | 10.1016/j.gimo.2023.100031 |