دورية أكاديمية
RGX-121 GENE THERAPY FOR THE TREATMENT OF SEVERE MUCOPOLYSACCHARIDOSIS TYPE II (MPS II): INTERIM ANALYSIS OF DATA FROM A PHASE 1/2 STUDY
| العنوان: | RGX-121 GENE THERAPY FOR THE TREATMENT OF SEVERE MUCOPOLYSACCHARIDOSIS TYPE II (MPS II): INTERIM ANALYSIS OF DATA FROM A PHASE 1/2 STUDY |
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| المؤلفون: | Ficicioglu, Can, Escolar, Maria, Giugliani, Roberto, Harmatz, Paul, Nevoret, Marie-Laure, Fiscella, Michele, Yang, Lin, Cho, Yoonjin, Phillips, Dawn, Falabella, Paulo |
| المصدر: | Molecular Genetics and Metabolism ; volume 135, issue 4, page 270-271 ; ISSN 1096-7192 |
| بيانات النشر: | Elsevier BV |
| سنة النشر: | 2022 |
| المجموعة: | ScienceDirect (Elsevier - Open Access Articles via Crossref) |
| مصطلحات موضوعية: | Endocrinology, Genetics, Molecular Biology, Biochemistry, Endocrinology, Diabetes and Metabolism |
| نوع الوثيقة: | article in journal/newspaper |
| اللغة: | English |
| DOI: | 10.1016/j.ymgme.2022.01.037 |
| الإتاحة: | https://doi.org/10.1016/j.ymgme.2022.01.037Test https://api.elsevier.com/content/article/PII:S1096719222000610?httpAccept=text/xmlTest https://api.elsevier.com/content/article/PII:S1096719222000610?httpAccept=text/plainTest |
| حقوق: | https://www.elsevier.com/tdm/userlicense/1.0Test/ |
| رقم الانضمام: | edsbas.A9E84C41 |
| قاعدة البيانات: | BASE |
| DOI: | 10.1016/j.ymgme.2022.01.037 |
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