التفاصيل البيبلوغرافية
العنوان: |
Base editing of key residues in the BCL11A-XL-specific zinc finger domains derepresses fetal globin expression |
المؤلفون: |
Rajendiran, Vignesh, Devaraju, Nivedhitha, Haddad, Mahdi, Ravi, Nithin Sam, Panigrahi, Lokesh, Paul, Joshua, Gopalakrishnan, Chandrasekar, Wyman, Stacia, Ariudainambi, Keerthiga, Mahalingam, Gokulnath, Periyasami, Yogapriya, Prasad, Kirti, George, Anila, Sukumaran, Dhiyaneshwaran, Gopinathan, Sandhiya, Pai, Aswin Anand, Nakamura, Yukio, Balasubramanian, Poonkuzhali, Ramalingam, Rajasekaran, Thangavel, Saravanabhavan, Velayudhan, Shaji R., Corn, Jacob E., Mackay, Joel P., Marepally, Srujan, Srivastava, Alok, Crossley, Merlin, Mohankumar, Kumarasamypet M. |
المساهمون: |
Wellcome Trust DBT India Alliance, Australian Medical Council, India Ministry of Science & Technology Department of Biotechnology, Indian Council of Medical Research, Science and Engineering Research Board |
المصدر: |
Molecular Therapy ; volume 32, issue 3, page 663-677 ; ISSN 1525-0016 |
بيانات النشر: |
Elsevier BV |
سنة النشر: |
2024 |
المجموعة: |
ScienceDirect (Elsevier - Open Access Articles via Crossref) |
مصطلحات موضوعية: |
Drug Discovery, Pharmacology, Genetics, Molecular Biology, Molecular Medicine |
نوع الوثيقة: |
article in journal/newspaper |
اللغة: |
English |
DOI: |
10.1016/j.ymthe.2024.01.023 |
الإتاحة: |
https://doi.org/10.1016/j.ymthe.2024.01.023Test https://api.elsevier.com/content/article/PII:S1525001624000236?httpAccept=text/xmlTest https://api.elsevier.com/content/article/PII:S1525001624000236?httpAccept=text/plainTest |
حقوق: |
https://www.elsevier.com/tdm/userlicense/1.0Test/ ; http://creativecommons.org/licenses/by-nc-nd/4.0Test/ |
رقم الانضمام: |
edsbas.A04D2BC5 |
قاعدة البيانات: |
BASE |