دورية أكاديمية

Development of an AAV-Based MicroRNA Gene Therapy to Treat Machado-Joseph Disease

التفاصيل البيبلوغرافية
العنوان: Development of an AAV-Based MicroRNA Gene Therapy to Treat Machado-Joseph Disease
المؤلفون: Martier, Raygene, Sogorb-Gonzalez, Marina, Stricker-Shaver, Janice, Hübener-Schmid, Jeannette, Keskin, Sonay, Klima, Jiri, Toonen, Lodewijk J., Juhas, Stefan, Juhasova, Jana, Ellederova, Zdenka, Motlik, Jan, Haas, Eva, van Deventer, Sander, Konstantinova, Pavlina, Nguyen, Huu Phuc, Evers, Melvin M.
المساهمون: European Community’s Seventh Framework Programme, National Sustainability Program I, Czech Ministry of Education, Youth and Sports
المصدر: Molecular Therapy - Methods & Clinical Development ; volume 15, page 343-358 ; ISSN 2329-0501
بيانات النشر: Elsevier BV
سنة النشر: 2019
المجموعة: ScienceDirect (Elsevier - Open Access Articles via Crossref)
مصطلحات موضوعية: Genetics, Molecular Biology, Molecular Medicine
نوع الوثيقة: article in journal/newspaper
اللغة: English
DOI: 10.1016/j.omtm.2019.10.008
الإتاحة: https://doi.org/10.1016/j.omtm.2019.10.008Test
https://api.elsevier.com/content/article/PII:S2329050119301160?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S2329050119301160?httpAccept=text/plainTest
حقوق: https://www.elsevier.com/tdm/userlicense/1.0Test/ ; http://creativecommons.org/licenses/by-nc-nd/4.0Test/
رقم الانضمام: edsbas.84FAE725
قاعدة البيانات: BASE