دورية أكاديمية
Development of an AAV-Based MicroRNA Gene Therapy to Treat Machado-Joseph Disease
العنوان: | Development of an AAV-Based MicroRNA Gene Therapy to Treat Machado-Joseph Disease |
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المؤلفون: | Martier, Raygene, Sogorb-Gonzalez, Marina, Stricker-Shaver, Janice, Hübener-Schmid, Jeannette, Keskin, Sonay, Klima, Jiri, Toonen, Lodewijk J., Juhas, Stefan, Juhasova, Jana, Ellederova, Zdenka, Motlik, Jan, Haas, Eva, van Deventer, Sander, Konstantinova, Pavlina, Nguyen, Huu Phuc, Evers, Melvin M. |
المساهمون: | European Community’s Seventh Framework Programme, National Sustainability Program I, Czech Ministry of Education, Youth and Sports |
المصدر: | Molecular Therapy - Methods & Clinical Development ; volume 15, page 343-358 ; ISSN 2329-0501 |
بيانات النشر: | Elsevier BV |
سنة النشر: | 2019 |
المجموعة: | ScienceDirect (Elsevier - Open Access Articles via Crossref) |
مصطلحات موضوعية: | Genetics, Molecular Biology, Molecular Medicine |
نوع الوثيقة: | article in journal/newspaper |
اللغة: | English |
DOI: | 10.1016/j.omtm.2019.10.008 |
الإتاحة: | https://doi.org/10.1016/j.omtm.2019.10.008Test https://api.elsevier.com/content/article/PII:S2329050119301160?httpAccept=text/xmlTest https://api.elsevier.com/content/article/PII:S2329050119301160?httpAccept=text/plainTest |
حقوق: | https://www.elsevier.com/tdm/userlicense/1.0Test/ ; http://creativecommons.org/licenses/by-nc-nd/4.0Test/ |
رقم الانضمام: | edsbas.84FAE725 |
قاعدة البيانات: | BASE |
DOI: | 10.1016/j.omtm.2019.10.008 |
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