دورية أكاديمية

ACCELERATE: A Patient-Powered Natural History Study Design Enabling Clinical and Therapeutic Discoveries in a Rare Disorder

التفاصيل البيبلوغرافية
العنوان: ACCELERATE: A Patient-Powered Natural History Study Design Enabling Clinical and Therapeutic Discoveries in a Rare Disorder
المؤلفون: Pierson, Sheila K., Khor, Johnson S., Ziglar, Jasira, Liu, Amy, Floess, Katherine, NaPier, Erin, Gorzewski, Alexander M., Tamakloe, Mark-Avery, Powers, Victoria, Akhter, Faizaan, Haljasmaa, Eric, Jayanthan, Raj, Rubenstein, Arthur, Repasky, Mileva, Elenitoba-Johnson, Kojo, Ruth, Jason, Jacobs, Bette, Streetly, Matthew, Angenendt, Linus, Patier, Jose Luis, Ferrero, Simone, Zinzani, Pier Luigi, Terriou, Louis, Casper, Corey, Jaffe, Elaine, Hoffmann, Christian, Oksenhendler, Eric, Fosså, Alexander, Srkalovic, Gordan, Chadburn, Amy, Uldrick, Thomas S., Lim, Megan, van Rhee, Frits, Fajgenbaum, David C.
المساهمون: Janssen Pharmaceuticals
المصدر: Cell Reports Medicine ; volume 1, issue 9, page 100158 ; ISSN 2666-3791
بيانات النشر: Elsevier BV
سنة النشر: 2020
المجموعة: ScienceDirect (Elsevier - Open Access Articles via Crossref)
مصطلحات موضوعية: General Biochemistry, Genetics and Molecular Biology
نوع الوثيقة: article in journal/newspaper
اللغة: English
DOI: 10.1016/j.xcrm.2020.100158
الإتاحة: https://doi.org/10.1016/j.xcrm.2020.100158Test
https://api.elsevier.com/content/article/PII:S2666379120302056?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S2666379120302056?httpAccept=text/plainTest
حقوق: https://www.elsevier.com/tdm/userlicense/1.0Test/ ; http://creativecommons.org/licenses/by-nc-nd/4.0Test/
رقم الانضمام: edsbas.6024EB3D
قاعدة البيانات: BASE