التفاصيل البيبلوغرافية
العنوان: |
The avalglucosidase alfa phase 3 COMET trial in late-onset Pompe disease patients: Efficacy and safety results after 97 weeks |
المؤلفون: |
Priya Kishnani, Jordi Díaz-Manera, Hani Kushlaf, Shafeeq Ladha, Tahseen Mozaffar, Volker Straub, Antonio Toscano, Ans T. van der Ploeg, Kenneth I. Berger, Paula R. Clemens, Yin-Hsiu Chien, John W. Day, Sergey Illarioshkin, Mark Roberts, Shahram Attarian, Gerson Carvalho, Young-Chul Choi, Sevim Erdem-Özdamar, Ozlem Goker-Alpan, Anna Kostera-Pruszczyk, Kristina An Haack, Nathan Thibault, Tianyue Zhou, Mazen M. Dimachkie, Benedikt Schoser |
المصدر: |
Molecular Genetics and Metabolism. 135:S66-S67 |
بيانات النشر: |
Elsevier BV, 2022. |
سنة النشر: |
2022 |
مصطلحات موضوعية: |
Endocrinology, Endocrinology, Diabetes and Metabolism, Genetics, Molecular Biology, Biochemistry |
تدمد: |
1096-7192 |
الوصول الحر: |
https://explore.openaire.eu/search/publication?articleId=doi_________::8ca8754c5e69f0b9ffc64a95181c90faTest https://doi.org/10.1016/j.ymgme.2021.11.168Test |
حقوق: |
CLOSED |
رقم الانضمام: |
edsair.doi...........8ca8754c5e69f0b9ffc64a95181c90fa |
قاعدة البيانات: |
OpenAIRE |