The avalglucosidase alfa phase 3 COMET trial in late-onset Pompe disease patients: Efficacy and safety results after 97 weeks

التفاصيل البيبلوغرافية
العنوان: The avalglucosidase alfa phase 3 COMET trial in late-onset Pompe disease patients: Efficacy and safety results after 97 weeks
المؤلفون: Priya Kishnani, Jordi Díaz-Manera, Hani Kushlaf, Shafeeq Ladha, Tahseen Mozaffar, Volker Straub, Antonio Toscano, Ans T. van der Ploeg, Kenneth I. Berger, Paula R. Clemens, Yin-Hsiu Chien, John W. Day, Sergey Illarioshkin, Mark Roberts, Shahram Attarian, Gerson Carvalho, Young-Chul Choi, Sevim Erdem-Özdamar, Ozlem Goker-Alpan, Anna Kostera-Pruszczyk, Kristina An Haack, Nathan Thibault, Tianyue Zhou, Mazen M. Dimachkie, Benedikt Schoser
المصدر: Molecular Genetics and Metabolism. 135:S66-S67
بيانات النشر: Elsevier BV, 2022.
سنة النشر: 2022
مصطلحات موضوعية: Endocrinology, Endocrinology, Diabetes and Metabolism, Genetics, Molecular Biology, Biochemistry
تدمد: 1096-7192
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::8ca8754c5e69f0b9ffc64a95181c90faTest
https://doi.org/10.1016/j.ymgme.2021.11.168Test
حقوق: CLOSED
رقم الانضمام: edsair.doi...........8ca8754c5e69f0b9ffc64a95181c90fa
قاعدة البيانات: OpenAIRE