JEWELFISH: 24-month Safety, Pharmacodynamic and Exploratory Efficacy Data in Non-Treatment-Naïve Patients with Spinal Muscular Atrophy (SMA) Receiving Treatment with Risdiplam (P7-9.004)

التفاصيل البيبلوغرافية
العنوان: JEWELFISH: 24-month Safety, Pharmacodynamic and Exploratory Efficacy Data in Non-Treatment-Naïve Patients with Spinal Muscular Atrophy (SMA) Receiving Treatment with Risdiplam (P7-9.004)
المؤلفون: Claudia Chiriboga, Claudio Bruno, Tina Duong, Dirk Fischer, Janbernd Kirschner, Mariacristina Scoto, Eugenio Mercuri, Marianne Gerber, Ksenija Gorni, Heidemarie Kletzl, Imogen Carruthers, Carmen Martin, Teresa Gidaro, Francesco Muntoni
المصدر: Tuesday, April 25.
بيانات النشر: Lippincott Williams & Wilkins, 2023.
سنة النشر: 2023
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::3391cb63ab291b8f80329faa7c7a8a6aTest
https://doi.org/10.1212/wnl.0000000000203609Test
رقم الانضمام: edsair.doi...........3391cb63ab291b8f80329faa7c7a8a6a
قاعدة البيانات: OpenAIRE