دورية أكاديمية

P005: Head-to-head trial of pegunigalsidase alfa vs agalsidase beta in Fabry disease: Phase 3 randomized, double-blind, BALANCE Study 2-year results

التفاصيل البيبلوغرافية
العنوان: P005: Head-to-head trial of pegunigalsidase alfa vs agalsidase beta in Fabry disease: Phase 3 randomized, double-blind, BALANCE Study 2-year results
المؤلفون: John Bernat, Eric Wallace, Ozlem Goker-Alpan, William Wilcox, Myrl Holida, Nicola Longo, Derralynn Hughes, Pilar Giraldo, Maria Molnar, Damara Ortiz, Robert Hopkin, Camilla Tondel, Ales Linhart, Patrick Deegan, Ana Jovanovic, Michael Muriello, Bruce Barshop, Virginia Kimonis, Bojan Vujkovac, Albina Nowak, Tarekegn Hiwot, Antonio Pisani, Dominique Germain, Ilkka Kantola, Jasmine Knoll, Ankit Mehta, Stephen Waldek, Einat Almon, Sari Alon, Raul Chertkoff, Rossana Rocco, David Warnock
المصدر: Genetics in Medicine Open, Vol 1, Iss 1, Pp 100015- (2023)
بيانات النشر: Elsevier, 2023.
سنة النشر: 2023
المجموعة: LCC:Genetics
LCC:Medicine
مصطلحات موضوعية: Genetics, QH426-470, Medicine
نوع الوثيقة: article
وصف الملف: electronic resource
اللغة: English
تدمد: 2949-7744
العلاقة: http://www.sciencedirect.com/science/article/pii/S2949774423000158Test; https://doaj.org/toc/2949-7744Test
DOI: 10.1016/j.gimo.2023.100015
الوصول الحر: https://doaj.org/article/343c76656a104fd8b64b93bc346cad1bTest
رقم الانضمام: edsdoj.343c76656a104fd8b64b93bc346cad1b
قاعدة البيانات: Directory of Open Access Journals
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