المؤلفون: Rowan H. Elhalag, Karam R. Motawea, Nesreen Elsayed Talat, Samah S. Rouzan, Jaffer Shah

المصدر: Frontiers in Neurology, Vol 14 (2023)

مصطلحات موضوعية: Duchene muscular dystrophy (DMD), vamorolone, neuromuscular, glucocorticoids, steroid naïve, Neurology. Diseases of the nervous system, RC346-429

وصف الملف: electronic resource

العلاقة: https://www.frontiersin.org/articles/10.3389/fneur.2023.1107474/fullTest; https://doaj.org/toc/1664-2295Test

الوصول الحر: https://doaj.org/article/02329c1ecd454f298524b33521db0c1bTest

المؤلفون: Susan Keam

مصطلحات موضوعية: Medicine, vamorolone, First Approval, Adis Drug Review, Adis Insight Report, dissociative corticosteroid, Duchenne Muscular Dystrophy

العلاقة: https://figshare.com/articles/online_resource/Vamorolone_First_Approval/24654435Test

الإتاحة: https://doi.org/10.6084/m9.figshare.24654435.v1Test
https://figshare.com/articles/online_resource/Vamorolone_First_Approval/24654435Test

المؤلفون: Aartsma-Rus, A., Ferlini, A., McNally, E. M., Spitali, P., Sweeney, H. L., Al-Khalili Szigyarto, Cristina, Bello, L., Bronson, A., Brown, K., Buccella, F., Chadwick, J., Frank, D., Hoffman, E., Larkindale, J., McClorey, G., Munschauer, R., Muntoni, F., Owens, J., Schara, U., Straub, V., Tinsley, J., Versnel, J., Vroom, E., Welch, E.

المصدر: Neuromuscular Disorders. 28(1):77-86

مصطلحات موضوعية: Biobank, Biomarker, Duchenne muscular dystrophy, Dystrophin, MRI, alanine aminotransferase, aspartate aminotransferase, biological marker, carbonate dehydratase III, corticosteroid, dysferlin, enolase, fukutin related protein, glucocorticoid receptor, glutamate dehydrogenase, immunoglobulin enhancer binding protein, microRNA, microRNA 133a, microRNA 133b, osteopontin, protein enolase 3, stromelysin, unclassified drug, utrophin, vamorolone, alanine aminotransferase level, aspartate aminotransferase blood level, Becker muscular dystrophy, blood analysis, blood sampling, Conference Paper, corticosteroid therapy, CRISPR-CAS9 system, DNA modification, drug design, exon, exon skipping, gene, gene expression, human, lipidomics, LTBP4 gene, Netherlands, nonhuman, nuclear magnetic resonance imaging, priority journal, protein expression, real time polymerase chain reaction, single nucleotide polymorphism, SPP1 gene, urinalysis, urine sampling, workshop, animal, information dissemination, male, metabolism, non profit organization, validation study, Animals, Biomarkers, Humans, Muscular Dystrophy, Duchenne, Organizations, Nonprofit, Validation Studies as Topic

وصف الملف: print

الوصول الحر: https://urn.kb.se/resolve?urn=urn:nbn:se:kth:diva-282709Test
https://doi.org/10.1016/j.nmd.2017.10.002Test

المؤلفون: Mukesh Kumar, Venugopalan Y Vishnu

المصدر: Journal of Current Research in Scientific Medicine, Vol 5, Iss 2, Pp 78-84 (2019)

مصطلحات موضوعية: duchenne muscular dystrophy, exon skipping, nusinersen, recent advances, risdiplam, spinal muscular atrophy, vamorolone, zolgensma, Medicine

وصف الملف: electronic resource

العلاقة: http://www.jcrsmed.org/article.asp?issn=2455-3069;year=2019;volume=5;issue=2;spage=78;epage=84;aulast=KumarTest; https://doaj.org/toc/2455-3069Test

الوصول الحر: https://doaj.org/article/205992cb4c1c4fdf8cda7cc878780529Test

المؤلفون: Dr Laurie Conklin, Dr Holly Peay, Suzanne Gaglianone, Suzie-Ann Bakker, Elizabeth Vroom, Dr Eric Hoffman, Christina Olsen

مصطلحات موضوعية: Duchenne muscular dystrophy, clinical trial, VISION-DMD, return of patient data, vamorolone

العلاقة: info:eu-repo/grantAgreement/EC/H2020/667078/; https://zenodo.org/communities/vision-dmd-h2020Test; https://zenodo.org/record/4836583Test; https://doi.org/10.5281/zenodo.4836583Test; oai:zenodo.org:4836583

الإتاحة: https://doi.org/10.5281/zenodo.4836583Test
https://doi.org/10.5281/zenodo.4836582Test
https://zenodo.org/record/4836583Test

المؤلفون: Christina Olsen, Ritchie Head, Jane Knerova, Jane Larkindale, Susan Ward, Pietro Spitali, Hermien Kan

مصطلحات موضوعية: Duchenne muscular dystrophy, Vamorolone, Biomarkers

العلاقة: info:eu-repo/grantAgreement/EC/H2020/667078/; https://zenodo.org/communities/vision-dmd-h2020Test; https://zenodo.org/record/5668693Test; https://doi.org/10.5281/zenodo.5668693Test; oai:zenodo.org:5668693

الإتاحة: https://doi.org/10.5281/zenodo.5668693Test
https://doi.org/10.5281/zenodo.5668575Test
https://zenodo.org/record/5668693Test

المؤلفون: Olsen, Christina, Head, Ritchie, Knerova, Jane, Larkindale, Jane, Ward, Susan, Spitali, Pietro, Kan, Hermien

مصطلحات موضوعية: Duchenne muscular dystrophy, Vamorolone, Biomarkers

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::2da9a555da5991a9aa9cdbb1ac59a16bTest

المؤلفون: Hoffman, Eric P., Schwartz, Benjamin D., Mengle-Gaw, Laurel J., Smith, Edward C., Castro, Diana, Mah, Jean K., McDonald, Craig M., Kuntz, Nancy L., Finkel, Richard S., Guglieri, Michela, Bushby, Katharine, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M., Webster, Richard, Smith, Andrea L., Morgenroth, Lauren P., Arrieta, Adrienne, Shimony, Maya, Siener, Catherine, Jaros, Mark, Shale, Phil, McCall, John M., Nagaraju, Kanneboyina, van den Anker, John, Conklin, Laurie S., Cnaan, Avital, Gordish-Dressman, Heather, Damsker, Jesse M., Clemens, Paula R.

مصطلحات موضوعية: Clinical trials Observational study (Cohort, Case control), Class IV, Muscle disease, Duchenne muscular dystrophy, vamorolone

جغرافية الموضوع: United States, United Kingdom, Sweden, Israel, Australia

الوقت: Canada

العلاقة: Hoffman EP, Schwartz BD, Mengle-Gaw LJ, Smith EC, Castro D, Mah JK, McDonald CM, Kuntz NL, Finkel RS, Guglieri M, Bushby K, Tulinius M, Nevo Y, Ryan MM, Webster R, Smith AL, Morgenroth LP, Arrieta A, Shimony M, Siener C, Jaros M, Shale P, McCall JM, Nagaraju K, van den Anker J, Conklin LS, Cnaan A, Gordish-Dressman H, Damsker JM, Clemens PR (2019) Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function. Neurology.; http://hdl.handle.net/10255/dryad.208749Test

الإتاحة: https://doi.org/10.5061/dryad.1rd4hc7Test
https://doi.org/10.5061/dryad.1rd4hc7/2Test
https://doi.org/10.1212/WNL.0000000000008168Test
http://hdl.handle.net/10255/dryad.208749Test

المؤلفون: Dr Laurie Conklin, Dr Holly Peay, Suzanne Gaglianone, Suzie-Ann Bakker, Elizabeth Vroom, Dr Eric Hoffman, Christina Olsen

مصطلحات موضوعية: education, Duchenne muscular dystrophy, clinical trial, VISION-DMD, return of patient data, vamorolone, 3. Good health

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::cc786295c7cee68c7f66480e0a5f6c77Test

المؤلفون: Dr Laurie Conklin, Dr Holly Peay, Gaglianone, Suzanne, Suzie-Ann Bakker, Vroom, Elizabeth, Dr Eric Hoffman, Olsen, Christina

مصطلحات موضوعية: education, Duchenne muscular dystrophy, clinical trial, VISION-DMD, return of patient data, vamorolone, 3. Good health

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::343ea968da3c7524f4f1378ad65a2100Test