المؤلفون: Anneliene Hechtelt Jonker, Daniel O’Connor, Maria Cavaller-Bellaubi, Christine Fetro, Maria Gogou, Peter A. C. ’T Hoen, Martin de Kort, Heather Stone, Nivedita Valentine, Anna Maria Gerdina Pasmooij

المصدر: Frontiers in Medicine, Vol 11 (2024)

مصطلحات موضوعية: drug repurposing, rare diseases, orphan drugs, unmet need, innovation, therapy development, Medicine (General), R5-920

وصف الملف: electronic resource

العلاقة: https://www.frontiersin.org/articles/10.3389/fmed.2024.1352803/fullTest; https://doaj.org/toc/2296-858XTest

الوصول الحر: https://doaj.org/article/cc6f95ef5fa542e780aabb40d1b8199fTest

المؤلفون: Eugenia Hernandez-Ruiz, Jill Sullivan

المصدر: Voices, Vol 23, Iss 3 (2023)

مصطلحات موضوعية: Mexico, emerging discipline, music therapy development, Music, M1-5000, Psychology, BF1-990

وصف الملف: electronic resource

العلاقة: https://voices.no/index.php/voices/article/view/3785Test; https://doaj.org/toc/1504-1611Test

الوصول الحر: https://doaj.org/article/b6234eee340e4204a6d4ff3c8b8bc459Test

المؤلفون: Cheff, Dorian M, Muotri, Alysson R, Stockwell, Brent R, Schmidt, Edward E, Ran, Qitao, Kartha, Reena V, Johnson, Simon C, Mittal, Plavi, Arnér, Elias SJ, Wigby, Kristen M, Hall, Matthew D, Ramesh, Sanath Kumar

المصدر: Orphanet Journal of Rare Diseases. 16(1)

مصطلحات موضوعية: Rare Diseases, Genetics, Orphan Drug, Aetiology, 2.1 Biological and endogenous factors, Good Health and Well Being, Humans, Osteochondrodysplasias, Sedaghatian-type spondylometaphyseal dysplasia, SSMD, Glutathione peroxidase 4, GPX4, Rare genetic disorder, Therapy development, Roadmap, Ultra-rare disease, Other Medical and Health Sciences, Genetics & Heredity

وصف الملف: application/pdf

الوصول الحر: https://escholarship.org/uc/item/4pb9v6gxTest

المؤلفون: Cummings, Jeffrey, Pinto, Luiz Cortez, Cruz, Manuel, Fischer, Corinne E, Gerritsen, Debby L, Grossberg, George T, Hwang, Tzung-Jeng, Ismail, Zahinoor, Jeste, Dilip V, Koopmans, Raymond, Lanctot, Krista L, Mateos, Raimundo, Peschin, Susan, Sampaio, Cristina, Tsuang, Debby, Wang, Huali, Zhong, Kate, Bain, Lisa J, Sano, Mary

المصدر: American Journal of Geriatric Psychiatry. 28(12)

مصطلحات موضوعية: Health Services and Systems, Biomedical and Clinical Sciences, Health Sciences, Brain Disorders, Mental Health, Neurosciences, Clinical Research, Mental health, Aged, Cognitive Dysfunction, Consensus, Geriatric Psychiatry, Hallucinations, Humans, Psychotic Disorders, Alzheimer's disease, psychosis, major neurocognitive disorder, mild neurocognitive disorder, hallucinations, delusions, diagnoses, therapy development, clinical trials, Clinical Sciences, Public Health and Health Services, Cognitive Sciences, Geriatrics, Clinical sciences, Health services and systems, Clinical and health psychology

وصف الملف: application/pdf

الوصول الحر: https://escholarship.org/uc/item/3m68g42bTest

المؤلفون: Wolff, Andreas, Schumacher, Nicolas Ulrich, Pürner, Dominik, Machetanz, Gerrit, Demleitner, Antonia F, Feneberg, Emily, Hagemeier, Maike Katharina, Lingor, Paul

المصدر: Journal of neural transmission 130(6), 793 - 820 (2023). doi:10.1007/s00702-023-02641-6

مصطلحات موضوعية: info:eu-repo/classification/ddc/610, Humans, Parkinson Disease: drug therapy, Dopamine, Disease Progression, Parkinson’s disease, Disease modification, Healthcare, Symptomatic treatment, Therapy development

جغرافية الموضوع: DE

العلاقة: info:eu-repo/semantics/altIdentifier/issn/0300-9564; info:eu-repo/semantics/altIdentifier/issn/0375-9245; info:eu-repo/semantics/altIdentifier/pmid/pmid:37147404; info:eu-repo/semantics/altIdentifier/issn/0022-3026; info:eu-repo/semantics/altIdentifier/issn/1435-1463; https://pub.dzne.de/record/258095Test; https://pub.dzne.de/search?p=id:%22DZNE-2023-00557%22Test

الإتاحة: https://doi.org/10.1007/s00702-023-02641-6Test
https://pub.dzne.de/record/258095Test
https://pub.dzne.de/search?p=id:%22DZNE-2023-00557%22Test

المؤلفون: Hernandez-Ruiz, Eugenia, Sullivan, Jill

المصدر: Voices: A World Forum for Music Therapy; Vol. 23 No. 3 (2023)

مصطلحات موضوعية: Mexico, emerging discipline, music therapy development, México, disciplina emergente, desarrollo de la musicoterapia

وصف الملف: application/pdf

العلاقة: https://voices.no/index.php/voices/article/view/3785/3715Test; https://voices.no/index.php/voices/article/view/3785/3716Test; https://voices.no/index.php/voices/article/view/3785Test

الإتاحة: https://voices.no/index.php/voices/article/view/3785Test

المؤلفون: Dorian M. Cheff, Alysson R. Muotri, Brent R. Stockwell, Edward E. Schmidt, Qitao Ran, Reena V. Kartha, Simon C. Johnson, Plavi Mittal, Elias S. J. Arnér, Kristen M. Wigby, Matthew D. Hall, Sanath Kumar Ramesh

المصدر: Orphanet Journal of Rare Diseases, Vol 16, Iss 1, Pp 1-15 (2021)

مصطلحات موضوعية: Sedaghatian-type spondylometaphyseal dysplasia, SSMD, Glutathione peroxidase 4, GPX4, Rare genetic disorder, Therapy development, Medicine

وصف الملف: electronic resource

العلاقة: https://doaj.org/toc/1750-1172Test

الوصول الحر: https://doaj.org/article/b03c183bb33b4ee8b5828e0234f4c132Test

المؤلفون: Jackson, Jamaal C, Sanchez, Darren, Johns, Andrew C, Campbell, Matthew T, Aydin, Ahmet M, Gokden, Neriman, Maraboyina, Sanjay, Muesse, Jason L, Ward, John F, Pisters, Louis L, Zacharias, Niki M, Guo, Charles C, Tu, Shi-Ming

المصدر: J Clin Med ; ISSN:2077-0383 ; Volume:13 ; Issue:12

مصطلحات موضوعية: drug resistance, epithelioid trophoblastic tumor, intratumoral heterogeneity, sarcomatoid yolk sac tumor, somatic transformation, testicular cancer, therapy development

العلاقة: https://doi.org/10.3390/jcm13123436Test; https://pubmed.ncbi.nlm.nih.gov/38929965Test; https://www.ncbi.nlm.nih.gov/pmc/articles/PMC11205088Test/

الإتاحة: https://doi.org/10.3390/jcm13123436Test
https://pubmed.ncbi.nlm.nih.gov/38929965Test
https://www.ncbi.nlm.nih.gov/pmc/articles/PMC11205088Test/

المؤلفون: Buist, Nicole, Krzyzaniak, Joseph, Abbas, Shermeen, Alvarez-Nunez, Fernando, Bell, Sammy, Chen, Bei, Chen, George, Chen, Shirlynn, He, Min, Hutchens, Clarice, Ibrahim, Basma, Ingram, Rebecca, Kulkarni, Mehuli, Murthy, Avinash, Tan, David Cheng Thiam, Sood, Ramesh, Ying, William, Roopwani, Rahul

المصدر: J Pharm Sci ; ISSN:1520-6017

مصطلحات موضوعية: Accelerated Assessment, Accelerated drug development, Priority Medicine (PRIME), Sakigake, break through therapy development, fast track approval

العلاقة: https://doi.org/10.1016/j.xphs.2024.05.026Test; https://pubmed.ncbi.nlm.nih.gov/38862091Test

الإتاحة: https://doi.org/10.1016/j.xphs.2024.05.026Test
https://pubmed.ncbi.nlm.nih.gov/38862091Test

المؤلفون: Frances M. Potjewyd, Joel K. Annor‐Gyamfi, Jeffrey Aubé, Shaoyou Chu, Ivie L. Conlon, Kevin J. Frankowski, Shiva K. R. Guduru, Brian P. Hardy, Megan D. Hopkins, Chizuru Kinoshita, Dmitri B. Kireev, Emily R. Mason, Charles T. Moerk, Felix Nwogbo, Kenneth H. Pearce Jr., Timothy I. Richardson, David A. Rogers, Disha M. Soni, Michael Stashko, Xiaodong Wang, Carrow Wells, Timothy M. Willson, Stephen V. Frye, Jessica E. Young, Alison D. Axtman

المصدر: Alzheimer’s & Dementia: Translational Research & Clinical Interventions, Vol 8, Iss 1, Pp n/a-n/a (2022)

مصطلحات موضوعية: AD Informer Set, Alzheimer's disease, chemogenomic set, chemogenomics, target validation, Target Enablement to Accelerate Therapy Development for Alzheimer's Disease, Neurology. Diseases of the nervous system, RC346-429, Geriatrics, RC952-954.6

وصف الملف: electronic resource

العلاقة: https://doaj.org/toc/2352-8737Test

الوصول الحر: https://doaj.org/article/b33c64d9d5fa4d89ad4554a76c6b0930Test