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1دورية أكاديمية
المؤلفون: Bijina Balakrishnan, Xinhua Yan, Marshall D. McCue, Olivia Bellagamba, Aaron Guo, Felicity Winkler, Jason Thall, Lisa Crawford, Rain Dimen, Sara Chen, Sean McEnaney, Yiman Wu, Mike Zimmer, Joe Sarkis, Paolo G.V. Martini, Patrick F. Finn, Kent Lai
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 1, Pp 101191- (2024)
مصطلحات موضوعية: classic galactosemia, gene therapy, mRNA-based therapy, breath test, galactose oxidation, adeno-associated viral vectors, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S232905012400007XTest; https://doaj.org/toc/2329-0501Test
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2دورية أكاديمية
المؤلفون: Maximiliano L. Cacicedo, Christine Weinl-Tenbruck, Daniel Frank, Sebastian Wirsching, Beate K. Straub, Jana Hauke, Jürgen G. Okun, Nigel Horscroft, Julia B. Hennermann, Fred Zepp, Frédéric Chevessier-Tünnesen, Stephan Gehring
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 26, Iss , Pp 294-308 (2022)
مصطلحات موضوعية: hereditary tyrosinemia type 1, fumarylacetoacetate hydrolase, nitisinone supplementation, mRNA-based therapy, mouse model, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050122000985Test; https://doaj.org/toc/2329-0501Test
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3دورية أكاديمية
المؤلفون: Maximiliano L. Cacicedo, Christine Weinl-Tenbruck, Daniel Frank, Maria Jose Limeres, Sebastian Wirsching, Katja Hilbert, Mansure Abdollah Pasha Famian, Nigel Horscroft, Julia B. Hennermann, Fred Zepp, Frédéric Chevessier-Tünnesen, Stephan Gehring
المصدر: Frontiers in Bioengineering and Biotechnology, Vol 10 (2022)
مصطلحات موضوعية: phenylketonuria (PKU), phenylalanine hydroxylase (pah), metabolic diseases, mRNA-based therapy, sapropterin, Biotechnology, TP248.13-248.65
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fbioe.2022.993298/fullTest; https://doaj.org/toc/2296-4185Test
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المؤلفون: Maximiliano L. Cacicedo, Christine Weinl-Tenbruck, Daniel Frank, Maria Jose Limeres, Sebastian Wirsching, Katja Hilbert, Mansure Abdollah Pasha Famian, Nigel Horscroft, Julia B. Hennermann, Fred Zepp, Frédéric Chevessier-Tünnesen, Stephan Gehring
مصطلحات موضوعية: Biotechnology, Biological Engineering, Genetic Engineering, Biomarkers, Biomaterials, Biomechanical Engineering, Biomedical Engineering not elsewhere classified, Synthetic Biology, Agricultural Marine Biotechnology, Bioremediation, Bioprocessing, Bioproduction and Bioproducts, Industrial Biotechnology Diagnostics (incl. Biosensors), Industrial Microbiology (incl. Biofeedstocks), Industrial Molecular Engineering of Nucleic Acids and Proteins, Industrial Biotechnology not elsewhere classified, Medical Biotechnology Diagnostics (incl. Biosensors), Medical Molecular Engineering of Nucleic Acids and Proteins, Regenerative Medicine (incl. Stem Cells and Tissue Engineering), Medical Biotechnology not elsewhere classified, phenylketonuria (PKU), phenylalanine hydroxylase (pah), metabolic diseases, mRNA-based therapy, sapropterin
الإتاحة: https://doi.org/10.3389/fbioe.2022.993298.s001Test
https://figshare.com/articles/dataset/DataSheet1_Phenylalanine_hydroxylase_mRNA_rescues_the_phenylketonuria_phenotype_in_mice_docx/21292761Test -
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المؤلفون: Kenji Kondo, Keiji Itaka, Kazunori Kataoka, Tatsuya Yamasoba, Miyuki Baba
المصدر: Journal of Controlled Release. 201:41-48
مصطلحات موضوعية: Olfactory system, Pathology, medicine.medical_specialty, Pharmaceutical Science, Olfactory dysfunction, Olfaction Disorders, Olfactory Mucosa, Olfactory nerve, Neurotrophic factors, In vivo, Olfactory Marker Protein, Animals, Medicine, natural sciences, RNA, Messenger, Administration, Intranasal, Micelles, health care economics and organizations, Mice, Inbred BALB C, Messenger RNA, Methimazole, Interleukin-6, Tumor Necrosis Factor-alpha, business.industry, Brain-Derived Neurotrophic Factor, Gene Transfer Techniques, Nanostructures, Messenger RNA (mRNA) administration, Cell biology, medicine.anatomical_structure, mRNA-based therapy, Brain-derived neurotrophic factor (BDNF), Nasal administration, business, Olfactory epithelium, geographic locations, Neurological disorders, Sensory nerve
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::d1d4a3fb4a7eea975c0fc69f8657f400Test
https://doi.org/10.1016/j.jconrel.2015.01.017Test -
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المؤلفون: Baba, Miyuki, Itaka, Keiji, Kondo, Kenji, Yamasoba, Tatsuya, Kataoka, Kazunori
مصطلحات موضوعية: Messenger RNA (mRNA) administration, Neurological disorders, Olfactory dysfunction, Brain-derived neurotrophic factor (BDNF), mRNA-based therapy
وصف الملف: application/pdf
العلاقة: http://www.u-tokyo.ac.jp/ja/utokyo-research/research-news/a-new-system-of-geneTest-therapy-using-messenger-rna-mrna.html; http://www.u-tokyo.ac.jp/en/utokyo-research/research-news/a-new-system-of-geneTest-therapy-using-messenger-rna-mrna.html; http://www.sciencedirect.com/science/article/pii/S0168365915000577Test; Journal of controlled release; 201; 41; 48; AA10458678; https://repository.dl.itc.u-tokyo.ac.jp/record/677/files/JCR-D-14-01314R1_author_manuscript.pdfTest