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1دورية أكاديمية
المؤلفون: Benjamin Arnson, Hye Ri Kang, Elizabeth D. Brooks, Dorothy Gheorghiu, Ekaterina Ilich, David Courtney, Jeffrey I. Everitt, Bryan R. Cullen, Dwight D. Koeberl
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 29, Iss , Pp 108-119 (2023)
مصطلحات موضوعية: genome editing, CRISPR-Cas9, adeno-associated virus vectors, inherited disorder of metabolism, glycogen storage disease, glucose-6-phosphatase, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050123000372Test; https://doaj.org/toc/2329-0501Test
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2دورية أكاديمية
المؤلفون: Arnson, Benjamin, Kang, Hye Ri, Brooks, Elizabeth D., Gheorghiu, Dorothy, Ilich, Ekaterina, Courtney, David, Everitt, Jeffrey I., Cullen, Bryan R., Koeberl, Dwight D.
المصدر: Arnson , B , Kang , H R , Brooks , E D , Gheorghiu , D , Ilich , E , Courtney , D , Everitt , J I , Cullen , B R & Koeberl , D D 2023 , ' Genome editing using Staphylococcus aureus Cas9 in a canine model of glycogen storage disease Ia ' , Molecular Therapy: Methods and Clinical Development , vol. 29 , pp. 108-119 . https://doi.org/10.1016/j.omtm.2023.03.001Test
مصطلحات موضوعية: von Gierke disease, glucose-6-phosphatase, genome editing, adeno-associated virus vectors, inherited disorder of metabolism, CRISPR-Cas9, glycogen storage disease
وصف الملف: application/pdf
الإتاحة: https://doi.org/10.1016/j.omtm.2023.03.001Test
https://pure.qub.ac.uk/en/publications/8f3a8120-acfc-4d03-8a45-59b2dc280ec1Test
https://pureadmin.qub.ac.uk/ws/files/451480392/Genome_editing_using_Staphylococcus_aureus_Cas9_in_a_canine_model_of_glycogen_storage_disease_Ia.pdfTest