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1دورية أكاديمية
المؤلفون: Sherlock, Sarah, Palmer, Jeffrey, Wagner, Kathryn, Abdel-Hamid, Hoda, Bertini, Enrico, Tian, Cuixia, Mah, Jean, Kostera-Pruszczyk, Anna, Muntoni, Francesco, Guglieri, Michela, Brandsema, John, Mercuri, Eugenio, Butterfield, Russell, Charnas, Lawrence, Marraffino, Shannon, McDonald, Craig
المصدر: Journal of Neurology. 269(8)
مصطلحات موضوعية: Biomarkers, Domagrozumab, Duchenne muscular dystrophy, Imaging, MRI, Neuromuscular disease, Antibodies, Monoclonal, Humanized, Biomarkers, Disease Progression, Humans, Magnetic Resonance Imaging, Male, Muscle, Skeletal, Muscular Dystrophy, Duchenne
وصف الملف: application/pdf
الوصول الحر: https://escholarship.org/uc/item/5r0250xcTest
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2دورية أكاديمية
المؤلفون: Sherlock, Sarah P, Palmer, Jeffrey, Wagner, Kathryn R, Abdel-Hamid, Hoda Z, Tian, Cuixia, Mah, Jean K, Muntoni, Francesco, Guglieri, Michela, Butterfield, Russell J, Charnas, Lawrence, Marraffino, Shannon
المصدر: Scientific Reports , 12 (1) , Article 18762. (2022)
مصطلحات موضوعية: Science & Technology, Multidisciplinary Sciences, Science & Technology - Other Topics, DOMAGROZUMAB, SAFETY
وصف الملف: text
العلاقة: https://discovery.ucl.ac.uk/id/eprint/10161003/1/s41598-022-23072-5.pdfTest; https://discovery.ucl.ac.uk/id/eprint/10161003Test/
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3دورية أكاديمية
المؤلفون: Wagner, Kathryn R., Abdel-Hamid, Hoda Z., Mah, Jean K., Campbell, Craig, Guglieri, Michela, Muntoni, Francesco, Takeshima, Yasuhiro, McDonald, Craig M., Kostera-Pruszczyk, Anna, Karachunski, Peter, Butterfield, Russell J., Mercuri, Eugenio, Fiorillo, Chiara, Bertini, Enrico S., Tian, Cuixia, Statland, Jeffery, Sadosky, Alesia B., Purohit, Vivek S., Sherlock, Sarah P., Palmer, Jeffrey P., Binks, Michael, Charnas, Lawrence, Marraffino, Shannon, Wong, Brenda L.
المصدر: Paediatrics Publications
مصطلحات موضوعية: Duchenne muscular dystrophy, myostatin inhibitor, domagrozumab, 4-stair climb, Pediatrics
وصف الملف: application/pdf
العلاقة: https://ir.lib.uwo.ca/paedpub/448Test; https://ir.lib.uwo.ca/context/paedpub/article/1460/viewcontent/Randomized_Phase_2_Trial.pdfTest
الإتاحة: https://doi.org/10.1016/j.nmd.2020.05.002Test
https://ir.lib.uwo.ca/paedpub/448Test
https://ir.lib.uwo.ca/context/paedpub/article/1460/viewcontent/Randomized_Phase_2_Trial.pdfTest -
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المؤلفون: Eugenio Mercuri, Jean K. Mah, C. Tian, Hoda Abdel-Hamid, Craig M. McDonald, Craig Campbell, J. Statland, Michael Binks, Alesia Sadosky, Lawrence Charnas, Jeffrey P. Palmer, Michela Guglieri, Brenda L. Wong, Francesco Muntoni, Yasuhiro Takeshima, Kathryn R. Wagner, Sarah P. Sherlock, Shannon Marraffino, Anna Kostera-Pruszczyk, Enrico Bertini, Peter I. Karachunski, Russell J. Butterfield, Vivek S. Purohit, Chiara Fiorillo
المصدر: Paediatrics Publications
مصطلحات موضوعية: Male, Duchenne muscular dystrophy, 0301 basic medicine, Pediatrics, medicine.medical_specialty, Adolescent, Antibodies, Monoclonal, Humanized, 03 medical and health sciences, 0302 clinical medicine, Outcome Assessment, Health Care, medicine, Humans, In patient, Treatment Failure, Child, Genetics (clinical), business.industry, Myostatin, medicine.disease, Muscular Dystrophy, Duchenne, myostatin inhibitor, 030104 developmental biology, Neurology, 4-stair climb, Pediatrics, Perinatology and Child Health, Ambulatory, Exercise Test, Neurology (clinical), Open label, domagrozumab, business, 030217 neurology & neurosurgery
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::8b3cbadea127d4ce51f63126e99cb373Test
https://doi.org/10.1016/j.nmd.2020.05.002Test -
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المؤلفون: Michael Binks, Sarah P. Sherlock, Shannon Marraffino, Yao Zhang
المصدر: Biomarkers in Medicine
مصطلحات موضوعية: Duchenne muscular dystrophy, Clinical Biochemistry, Thigh, Muscle volume, functional test, 030218 nuclear medicine & medical imaging, 03 medical and health sciences, 0302 clinical medicine, Drug Discovery, DMD, Medicine, four-stair climb, Muscle mri, business.industry, Biochemistry (medical), imaging, Baseline data, medicine.disease, Clinical trial, Muscular Dystrophy, Duchenne, medicine.anatomical_structure, Ambulatory, Biomarker (medicine), business, Nuclear medicine, domagrozumab, 030217 neurology & neurosurgery, Research Article, MRI
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::dc53ce4497d5092ce8b939142356b85dTest
https://pubmed.ncbi.nlm.nih.gov/34155911Test