المؤلفون: Maria Grazia Biferi, Mathilde Cohen-Tannoudji, Andrea García-Silva, Olga Souto-Rodríguez, Irene Viéitez-González, Beatriz San-Millán-Tejado, Andrea Fernández-Carrera, Tania Pérez-Márquez, Susana Teijeira-Bautista, Soraya Barrera, Vanesa Domínguez, Thibaut Marais, África González-Fernández, Martine Barkats, Saida Ortolano

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 20, Iss , Pp 1-17 (2021)

مصطلحات موضوعية: Fabry disease, lysosomal storage disorders, adeno asociated virus-9, gene therapy, blood brain barrier, gene transfer, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050120302205Test; https://doaj.org/toc/2329-0501Test

الوصول الحر: https://doaj.org/article/b2d13278a02c48deb45d598f9f6bd188Test

المؤلفون: Biferi, Maria Grazia, Cohen-Tannoudji, Mathilde, García-Silva, Andrea, Souto-Rodríguez, Olga, Viéitez-González, Irene, San-Millán-Tejado, Beatriz, Fernández-Carrera, Andrea, Pérez-Márquez, Tania, Teijeira-Bautista, Susana, Barrera, Soraya, Domínguez, Vanesa, Marais, Thibaut, González-Fernández, África, Barkats, Martine, Ortolano, Saida

المساهمون: Centre de recherche en Myologie – U974 SU-INSERM, Institut National de la Santé et de la Recherche Médicale (INSERM)-Sorbonne Université (SU), Instituto de Investigación Sanitaria Galicia Sur Vigo, Spain, University of Vigo Pontevedra

المصدر: EISSN: 2329-0501 ; Molecular Therapy - Methods and Clinical Development ; https://hal.sorbonne-universite.fr/hal-03193801Test ; Molecular Therapy - Methods and Clinical Development, 2021, 20, pp.1 - 17. ⟨10.1016/j.omtm.2020.10.016⟩

مصطلحات موضوعية: Fabry disease lysosomal storage disorders adeno asociated virus-9, gene therapy, blood brain barrier, gene transfer, bone involvement, metabolic disorders, X-linked diseases, [SDV.MHEP]Life Sciences [q-bio]/Human health and pathology

العلاقة: hal-03193801; https://hal.sorbonne-universite.fr/hal-03193801Test; https://hal.sorbonne-universite.fr/hal-03193801/documentTest; https://hal.sorbonne-universite.fr/hal-03193801/file/mmc2%281%29.pdfTest

الإتاحة: https://doi.org/10.1016/j.omtm.2020.10.016Test
https://hal.sorbonne-universite.fr/hal-03193801Test
https://hal.sorbonne-universite.fr/hal-03193801/documentTest
https://hal.sorbonne-universite.fr/hal-03193801/file/mmc2%281%29.pdfTest

المؤلفون: Martine Barkats, Irene Viéitez-González, África González-Fernández, Mathilde Cohen-Tannoudji, Andrea Fernandez-Carrera, Beatriz San-Millán-Tejado, Maria Grazia Biferi, Vanesa Domínguez, Saida Ortolano, Susana Teijeira-Bautista, Olga Souto-Rodriguez, Tania Pérez-Márquez, Thibaut Marais, Soraya Barrera, Andrea Garcia-Silva

المساهمون: Centre de recherche en Myologie – U974 SU-INSERM, Institut National de la Santé et de la Recherche Médicale (INSERM)-Sorbonne Université (SU), Instituto de Investigación Sanitaria Galicia Sur [Vigo, Spain], University of Vigo [ Pontevedra], Gestionnaire, HAL Sorbonne Université 5, Thérapie des maladies du muscle strié, Institut National de la Santé et de la Recherche Médicale (INSERM)-Centre National de la Recherche Scientifique (CNRS)-Sorbonne Université (SU), Centre de Recherche en Myologie

المصدر: Investigo. Repositorio Institucional de la Universidade de Vigo
Universidade de Vigo (UVigo)
Molecular Therapy. Methods & Clinical Development
Molecular Therapy-Methods and Clinical Development
Molecular Therapy-Methods and Clinical Development, 2021, 20, pp.1-17. ⟨10.1016/j.omtm.2020.10.016⟩
Molecular Therapy-Methods and Clinical Development, Nature Publishing Group, 2021, 20, pp.1-17. ⟨10.1016/j.omtm.2020.10.016⟩
Molecular Therapy: Methods & Clinical Development, Vol 20, Iss, Pp 1-17 (2021)

مصطلحات موضوعية: 0301 basic medicine, lcsh:QH426-470, bone involvement, Genetic enhancement, Central nervous system, blood brain barrier, 2410.07 Genética Humana, Blood–brain barrier, lysosomal storage disorders, Viral vector, 03 medical and health sciences, chemistry.chemical_compound, 3201 Ciencias Clínicas, 0302 clinical medicine, adeno asociated virus-9, Genetics, medicine, metabolic disorders, Vector (molecular biology), lcsh:QH573-671, gene transfer, Molecular Biology, Fabry disease, [SDV.MHEP] Life Sciences [q-bio]/Human health and pathology, X-linked diseases, biology, lcsh:Cytology, business.industry, Glycosphingolipid, 3201.03 Microbiología Clínica, medicine.disease, gene therapy, 3. Good health, lcsh:Genetics, 030104 developmental biology, medicine.anatomical_structure, Fabry disease lysosomal storage disorders adeno asociated virus-9, chemistry, 030220 oncology & carcinogenesis, Immunology, biology.protein, Molecular Medicine, Original Article, Antibody, business, [SDV.MHEP]Life Sciences [q-bio]/Human health and pathology

وصف الملف: application/pdf

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::2885db2614f355e811d45393c2dc42a5Test
https://linkinghub.elsevier.com/retrieve/pii/S2329050120302205Test