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1دورية أكاديمية
المصدر: Frontiers in Genome Editing, Vol 5 (2023)
مصطلحات موضوعية: genome editing, neurometabolic, liver, retina, HSPC, metabolic, Biotechnology, TP248.13-248.65, Genetics, QH426-470
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fgeed.2023.1248904/fullTest; https://doaj.org/toc/2673-3439Test
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2دورية أكاديمية
المؤلفون: Alessio Cantore, Alessandro Fraldi, Vasco Meneghini, Angela Gritti
المصدر: Frontiers in Medicine, Vol 8 (2022)
مصطلحات موضوعية: gene therapy, liver, central nervous system, gene editing, translational medicine, Medicine (General), R5-920
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fmed.2021.774618/fullTest; https://doaj.org/toc/2296-858XTest
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3دورية أكاديمية
المؤلفون: Vasco Meneghini, Marco Peviani, Marco Luciani, Giada Zambonini, Angela Gritti
المصدر: Frontiers in Genome Editing, Vol 3 (2021)
مصطلحات موضوعية: astrocytes, oligodendrocytes, microglia, editing, CRISPR/Cas9 system, adeno-associated viral vectors, Biotechnology, TP248.13-248.65, Genetics, QH426-470
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fgeed.2021.644319/fullTest; https://doaj.org/toc/2673-3439Test
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4دورية أكاديمية
المؤلفون: Leslie Weber, Valentina Poletti, Elisa Magrin, Chiara Antoniani, Samia Martin, Charles Bayard, Hanem Sadek, Tristan Felix, Vasco Meneghini, Michael N. Antoniou, Wassim El-Nemer, Fulvio Mavilio, Marina Cavazzana, Isabelle Andre-Schmutz, Annarita Miccio
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 10, Iss , Pp 268-280 (2018)
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050118300767Test; https://doaj.org/toc/2329-0501Test
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5دورية أكاديمية
المؤلفون: Marco Luciani, Angela Gritti, Vasco Meneghini
المصدر: Frontiers in Molecular Biosciences, Vol 7 (2020)
مصطلحات موضوعية: lysosomal storage disorders, central nervous system, induced pluripotent stem cells, neural stem cells, organoids, drug discovery, Biology (General), QH301-705.5
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/article/10.3389/fmolb.2020.00224/fullTest; https://doaj.org/toc/2296-889XTest
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6دورية أكاديمية
المؤلفون: Oriana Romano, Luca Petiti, Tristan Felix, Vasco Meneghini, Michel Portafax, Chiara Antoniani, Mario Amendola, Silvio Bicciato, Clelia Peano, Annarita Miccio
المصدر: iScience, Vol 23, Iss 4, Pp - (2020)
مصطلحات موضوعية: Science
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S2589004220302029Test; https://doaj.org/toc/2589-0042Test
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7
المصدر: Methods in cell biology. 171
مصطلحات موضوعية: Gene Editing, Mice, Animals, Newborn, Neural Stem Cells, Induced Pluripotent Stem Cells, Animals, Humans, Cell Differentiation
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=pmid________::a98beb9e305092b461f027abd808b6a4Test
https://pubmed.ncbi.nlm.nih.gov/35953197Test -
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المصدر: Methods in Cell Biology ISBN: 9780323900188
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::93f674f5e510b7616d8c02975e97c673Test
https://doi.org/10.1016/bs.mcb.2022.04.007Test -
9
المؤلفون: Jean-Paul Concordet, Anne Chalumeau, Tristan Felix, Nadia Othman, Sherazade Aknoun, Annarita Miccio, Mario Amendola, Wassim El Nemer, Sophie Ramadier, Vasco Meneghini, Mégane Brusson, Anna Cereseto, Giacomo Frati, Giulia Maule, Marina Cavazzana, Antonio Casini, Benoit Wattellier, Anne De Cian, Cécile Masson
المساهمون: Anthropologie bio-culturelle, Droit, Ethique et Santé (ADES), Aix Marseille Université (AMU)-EFS ALPES MEDITERRANEE-Centre National de la Recherche Scientifique (CNRS), ANR-16-CE18-0012,STaHR,Stimulation de la Recombinaison Homologue pour la Thérapie Génique(2016)
المصدر: Mol Ther
Molecular Therapy
Molecular Therapy, 2022, 30 (1), pp.145-163. ⟨10.1016/j.ymthe.2021.08.019⟩مصطلحات موضوعية: Transgene, [SDV]Life Sciences [q-bio], Anemia, Sickle Cell, beta-Globins, Biology, medicine.disease_cause, hemic and lymphatic diseases, CRISPR-Associated Protein 9, Drug Discovery, Fetal hemoglobin, Genetics, medicine, Gene silencing, Autologous transplantation, Humans, Progenitor cell, Molecular Biology, ComputingMilieux_MISCELLANEOUS, Fetal Hemoglobin, Pharmacology, Gene Editing, Mutation, Transfection, Haematopoiesis, Cancer research, Molecular Medicine, Original Article
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::786a57c29056b4c4e23fe3fdd9f542f9Test
https://pubmed.ncbi.nlm.nih.gov/34418541Test -
10دورية أكاديمية
المؤلفون: Vasco, Meneghini, BORTOLOTTO, Valeria, Maria, Teresa Francese, Anna, Dellarole, Lorenzo, Carraro, Slavica, Terzieva, GRILLI, Mariagrazia
المساهمون: Vasco, Meneghini, Bortolotto, Valeria, Maria, Teresa Francese, Anna, Dellarole, Lorenzo, Carraro, Slavica, Terzieva, Grilli, Mariagrazia
مصطلحات موضوعية: NF-kappaB, HMGB-1, beta amyloid, oligomer, neurogenesi, Alzheimer's Disease
وصف الملف: STAMPA
العلاقة: info:eu-repo/semantics/altIdentifier/pmid/23554486; info:eu-repo/semantics/altIdentifier/wos/WOS:000317186800018; volume:33; issue:14; firstpage:6047; lastpage:6059; numberofpages:13; journal:THE JOURNAL OF NEUROSCIENCE; http://hdl.handle.net/11579/13186Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-84875991280