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1دورية أكاديمية
المؤلفون: Kimberly Goodspeed, Deepa Sirsi, Steven Gray, Matthew Rioux, WeiRui Guo, Susan Iannaccone
المصدر: Journal of Clinical and Translational Science, Vol 7, Pp 127-127 (2023)
مصطلحات موضوعية: Medicine
وصف الملف: electronic resource
العلاقة: https://www.cambridge.org/core/product/identifier/S2059866123004570/type/journal_articleTest; https://doaj.org/toc/2059-8661Test
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2
المؤلفون: Shelagh M. Szabo, Alexa C. Klimchak, Christina Qian, Susan Iannaccone, Evan Popoff, Katherine L. Gooch
المصدر: Journal of neuromuscular diseases. 9(6)
مصطلحات موضوعية: Male, Muscular Dystrophy, Duchenne, Cohort Studies, Neurology, Scoliosis, Wheelchairs, Humans, Neurology (clinical), Cardiomyopathies, United States
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::20f830edb8bba45ff3e23f3e9c4986dbTest
https://pubmed.ncbi.nlm.nih.gov/36245384Test -
3
المؤلفون: Saima Kayani, Xin Chen, Souad Messahel, Veronica Edgar, Susan Iannaccone, Steven Gray, Berge Minassian, Benjamin Greenberg
المصدر: Molecular Genetics and Metabolism. 135:S65
مصطلحات موضوعية: Endocrinology, Endocrinology, Diabetes and Metabolism, Genetics, Molecular Biology, Biochemistry
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::a5f1e0263fe51f937a61f61b820ff3c7Test
https://doi.org/10.1016/j.ymgme.2021.11.164Test -
4
المؤلفون: Victor, Ronald G, Sweeney, H. Lee, Finkel, Richard, Mcdonald, Craig M, Byrne, Barry, Eagle, Michelle, Goemans, Nathalie, Vandenborne, Krista, Dubrovsky, Alberto L, Topaloglu, Haluk, Miceli, M. Carrie, Furlong, Pat, Landry, John, Elashoff, Robert, Cox, David, Hoda, Abdel-Hamid, Susan, Apkon, Richard, Barohn, Elena, Belousova, Enrico, Bertini, John, Brandsema, Claudio, Bruno, William, Burnette, Russell, Butterfield, Barry, Byrne, Craig, Campbell, Jose, Carlo, Jong-Hee, Chae, Saleel, Chandratre, Giacomo, Comi, Anne, Connolly, Imelda De Groot, Nicolas, Deconinck, Joseph, Dooley, Alberto, Dubrovsky, Julien, Durigneux, Erika, Finanger, Richard, Finkel, L Matthew Frank, Nathalie, Goemans, Amy, Harper, Ayako, Hattori, Ozlem, Herguner, Susan, Iannaccone, Joanne, Janas, Yuh-Jyh, Jong, Janberd, Kirschner, Hirofumi, Komaki, Nancy, Kuntz, Wang-Tso, Lee, Edward, Leung, Jean, Mah, Katherine, Mathews, Craig, Mcdonald, Eugenio, Mercuri, Hugh, Mcmillan, Wolfgang, Mueller-Felber, Adolfo Lopez de Munain, Akinori, Nakamura, Erik, Niks, Katsuhisa, Ogata, Samuel, Pascual, Pegoraro, Elena, Yann, Pereon, Ben, Renfroe, Ratna Bhavaraju Sanka, Jens, Schallner, Ulrike, Schara, Kathryn, Selby, Isabel Illa Sendra, Laurent, Servais, Edward, Smith, Susan, Sparks, Haluk, Topaloglu, Ron, Victor, Juan Jose Vilchez, Matthew, Wicklund, Ekkehard, Wilichoswki, Brenda, Wong
المساهمون: L, Servais., Çocuk Sağlığı ve Hastalıkları, Schara, Ulrike (Beitragende*r)
المصدر: Neurology, vol 89, iss 17
Neurology
Neurology, 89(17), 1811-1820
Neurology, 89 (17مصطلحات موضوعية: 0301 basic medicine, Male, Duchenne muscular dystrophy, Vasodilator Agents, International Cooperation, Left, Medizin, Placebo-controlled study, Walking, Ventricular Function, Left, law.invention, Pulmonary function testing, Tadalafil, Efficacy, 0302 clinical medicine, Randomized controlled trial, law, Heart Rate, Ventricular Function, Muscular Dystrophy, Child, Pediatric, Sciences bio-médicales et agricoles, 3. Good health, Respiratory Function Tests, Treatment Outcome, Area Under Curve, 6.1 Pharmaceuticals, Ambulatory, Cognitive Sciences, Walking -- physiology, Drug, medicine.drug, musculoskeletal diseases, Duchenne/ Becker Muscular Dystrophy, medicine.medical_specialty, Adolescent, Intellectual and Developmental Disabilities (IDD), Clinical Trials and Supportive Activities, Clinical Sciences, Vasodilator Agents -- therapeutic use, Tadalafil -- therapeutic use, Placebo, Article, Dose-Response Relationship, 03 medical and health sciences, Rare Diseases, Double-Blind Method, Clinical Research, Internal medicine, medicine, Heart Rate -- physiology, Humans, Glucocorticoids, Neurology & Neurosurgery, Dose-Response Relationship, Drug, business.industry, Neurosciences, Evaluation of treatments and therapeutic interventions, medicine.disease, Duchenne, Glucocorticoids -- therapeutic use, Tadalafil DMD Study Group, Brain Disorders, Muscular Dystrophy, Duchenne, 030104 developmental biology, Musculoskeletal, Muscular Dystrophy, Duchenne -- drug therapy -- psychology, Quality of Life, Neurology (clinical), business, 030217 neurology & neurosurgery, Follow-Up Studies
وصف الملف: application/pdf; Print-Electronic; text/plain; 2 full-text file(s): application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::6e0e6503a882dfb553f43c58e0475c30Test
https://ora.ox.ac.uk/objects/uuid:07acefc6-f3c1-43d6-aaff-dd314f53221cTest -
5دورية أكاديمية
المؤلفون: Victor, Ronald G, Sweeney, H. Lee, Finkel, Richard, Mcdonald, Craig M, Byrne, Barry, Eagle, Michelle, Goemans, Nathalie, Vandenborne, Krista, Dubrovsky, Alberto L, Topaloglu, Haluk, Miceli, M. Carrie, Furlong, Pat, Landry, John, Elashoff, Robert, Cox David, Hoda Abdel-Hamid, Susan Apkon, Richard Barohn, Elena Belousova, Enrico Bertini, John Brandsema, Claudio Bruno, William Burnette, Russell Butterfield, Barry Byrne, Craig Campbell, Jose Carlo, Jong-Hee Chae, Saleel Chandratre, Giacomo Comi, Anne Connolly, Imelda De Groot, Nicolas Deconinck, Joseph Dooley, Alberto Dubrovsky, Julien Durigneux, Erika Finanger, Richard Finkel, L Matthew Frank, Nathalie Goemans, Amy Harper, Ayako Hattori, Ozlem Herguner, Susan Iannaccone, Joanne Janas, Yuh-Jyh Jong, JanBerd Kirschner, Hirofumi Komaki, Nancy Kuntz, Wang-Tso Lee, Edward Leung, Jean Mah, Katherine Mathews, Craig McDonald, Eugenio Mercuri, Hugh McMillan, Wolfgang Mueller-Felber, Adolfo Lopez de Munain, Akinori Nakamura, Erik Niks, Katsuhisa Ogata, Samuel Pascual, Elena Pegoraro, Yann Pereon, Ben Renfroe, Ratna Bhavaraju Sanka, Jens Schallner, Ulrike Schara, Kathryn Selby, Isabel Illa Sendra, Laurent Servais, Edward Smith, Susan Sparks, Haluk Topaloglu, Ron Victor, Juan Jose Vilchez, Matthew Wicklund, Ekkehard Wilichoswki, Brenda Wong
المساهمون: Ronald G, Victor, H. Lee, Sweeney, Richard, Finkel, Craig M, Mcdonald, Barry, Byrne, Michelle, Eagle, Nathalie, Goeman, Krista, Vandenborne, Alberto L, Dubrovsky, Haluk, Topaloglu, M. Carrie, Miceli, Pat, Furlong, John, Landry, Robert, Elashoff, David, Cox, Abdel-Hamid, Hoda, Apkon, Susan, Barohn, Richard, Belousova, Elena, Bertini, Enrico, Brandsema, John, Bruno, Claudio, Burnette, William, Butterfield, Russell, Byrne, Barry, Campbell, Craig, Carlo, Jose, Chae, Jong-Hee, Chandratre, Saleel, Comi, Giacomo, Connolly, Anne, De Groot, Imelda, Deconinck, Nicola, Dooley, Joseph, Dubrovsky, Alberto, Durigneux, Julien, Finanger, Erika, Finkel, Richard, Matthew Frank, L, Goemans, Nathalie, Harper, Amy, Hattori, Ayako, Herguner, Ozlem, Iannaccone, Susan, Janas, Joanne, Jong, Yuh-Jyh, Kirschner, Janberd, Komaki, Hirofumi, Kuntz, Nancy, Lee, Wang-Tso, Leung, Edward, Mah, Jean, Mathews, Katherine, Mcdonald, Craig, Mercuri, Eugenio, Mcmillan, Hugh, Mueller-Felber, Wolfgang, Lopez de Munain, Adolfo, Nakamura, Akinori, Niks, Erik, Ogata, Katsuhisa, Pascual, Samuel, Pegoraro, Elena, Pereon, Yann, Renfroe, Ben, Bhavaraju Sanka, Ratna, Schallner, Jen, Schara, Ulrike, Selby, Kathryn, Illa Sendra, Isabel, Servais, Laurent, Smith, Edward, Sparks, Susan, Topaloglu, Haluk, Victor, Ron, Jose Vilchez, Juan, Wicklund, Matthew, Wilichoswki, Ekkehard, Wong, Brenda
وصف الملف: STAMPA
العلاقة: info:eu-repo/semantics/altIdentifier/pmid/28972192; info:eu-repo/semantics/altIdentifier/wos/WOS:000417674200014; volume:89; issue:17; firstpage:1811; lastpage:1820; numberofpages:10; journal:NEUROLOGY; http://hdl.handle.net/11577/3242500Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85032229798