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1دورية أكاديمية
المؤلفون: Matthew Rok, Tatianna Wai Ying Wong, Eleonora Maino, Abdalla Ahmed, Grace Yang, Elzbieta Hyatt, Kyle Lindsay, Sina Fatehi, Ryan Marks, Paul Delgado-Olguín, Evgueni A. Ivakine, Ronald D. Cohn
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 30, Iss , Pp 246-258 (2023)
مصطلحات موضوعية: CRISPR, Duchenne muscular dystrophy, exon skipping, genome editing, in vivo, cardiomyopathy, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050123001043Test; https://doaj.org/toc/2329-0501Test
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المؤلفون: Sina Fatehi, Ryan M. Marks, Matthew J. Rok, Lucie Perillat, Evgueni A. Ivakine, Ronald D. Cohn
المصدر: Human Gene Therapy. 34:388-403
مصطلحات موضوعية: Genetics, Molecular Medicine, Molecular Biology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::8454367100364896b13e8aaa7e9196f4Test
https://doi.org/10.1089/hum.2023.059Test