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1دورية أكاديمية
المؤلفون: Tran, Duc Q, Benson, Craig C, Boice, Judith A, Chitlur, Meera, Dunn, Amy L, Escobar, Miguel A, Gupta, Kalpna, Johnsen, Jill M, Jorgenson, James, Martin, Scott D, Martin, Suzanne, Meeks, Shannon L, Narvaez, Alfredo A, Quon, Doris V, Reding, Mark T, Reiss, Ulrike M, Savage, Brittany, Schafer, Kim, Steiner, Bruno, Thornburg, Courtney, Volland, Lena M, von Drygalski, Annette
المصدر: Expert Review of Hematology. 16(sup1)
مصطلحات موضوعية: Biomedical and Clinical Sciences, Cardiovascular Medicine and Haematology, Clinical Research, Genetics, Hematology, Health and social care services research, 8.1 Organisation and delivery of services, Good Health and Well Being, Adult, Humans, Child, United States, Hemophilia A, Delivery of Health Care, Medicine, Research, Community, hemophilia, inherited bleeding disorders, National Hemophilia Foundation, patient-centered, research, Cardiorespiratory Medicine and Haematology, Other Medical and Health Sciences, Cardiovascular medicine and haematology
وصف الملف: application/pdf
الوصول الحر: https://escholarship.org/uc/item/5q497038Test
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2
المؤلفون: Iorio, Alfonso, Königs, Christoph, Reding, Mark T., Rotellini, Dawn, Skinner, Mark W., Mancuso, Maria Elisa, Berntorp, Erik
المصدر: Haemophilia. 29(1):33-44
مصطلحات موضوعية: arthropathy, bleeding, episodic/on-demand treatment, non-severe (mild or moderate) haemophilia A or B, prophylactic FVIII or FIX, women with haemophilia (symptomatic carriers), Medicin och hälsovetenskap, Klinisk medicin, Hematologi, Medical and Health Sciences, Clinical Medicine, Hematology
الوصول الحر: https://lup.lub.lu.se/record/edf6e4ca-d655-4b29-9ae3-2eef6f0f9271Test
http://dx.doi.org/10.1111/hae.14676Test -
3دورية أكاديمية
المؤلفون: Reding, Mark T., Álvarez-Román, María Teresa, Castaman, Giancarlo, Janbain, Maissaa, Matsushita, Tadashi, Meijer, Karina, Schmidt, Kathrin, Oldenburg, Johannes
المصدر: Reding , M T , Álvarez-Román , M T , Castaman , G , Janbain , M , Matsushita , T , Meijer , K , Schmidt , K & Oldenburg , J 2024 , ' Interim analyses of the multinational real-world prospective cohort HEM-POWR study evaluating the effectiveness and safety of damoctocog alfa pegol in patients with hemophilia A ' , European Journal of Haematology , vol. 112 , no. 2 , pp. 286-295 . https://doi.org/10.1111/ejh.14114Test
مصطلحات موضوعية: bleeding, half-life, hemophilia A, real-world, safety
وصف الملف: application/pdf
الإتاحة: https://doi.org/10.1111/ejh.14114Test
https://hdl.handle.net/11370/91c360b6-eebf-4f31-9356-c9fb32c5560cTest
https://research.rug.nl/en/publications/91c360b6-eebf-4f31-9356-c9fb32c5560cTest
https://pure.rug.nl/ws/files/896660527/Interim_analyses_of_the_multinational_real-world_prospectivecohort_HEM-POWR_study_evaluating_the_effectiveness_andsafety_of_damoctocog_alfa_pegol_in_patients_with_hemophilia_A.pdfTest
http://www.scopus.com/inward/record.url?scp=85174612602&partnerID=8YFLogxKTest -
4دورية أكاديمية
المؤلفون: Reding, Mark T., Simpson, Mindy, Ducore, Jonathan, Holme, Pål Andrè, Maas Enriquez, Monika, Mancuso, Maria Elisa
المصدر: Acta Haematologica ; page 1-10 ; ISSN 0001-5792 1421-9662
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5دورية أكاديمية
المؤلفون: Madan, Bella, Ozelo, Margareth C., Raheja, Priyanka, Symington, Emily, Quon, Doris V., Leavitt, Andrew D., Pipe, Steven W., Lowe, Gillian, Kenet, Gili, Reding, Mark T., Mason, Jane, Wang, Michael, von Drygalski, Annette, Klamroth, Robert, Shapiro, Susan, Chambost, Hervé, Dunn, Amy L., Oldenburg, Johannes, Chou, Sheng-Chieh, Peyvandi, Flora, Millar, Carolyn M., Osmond, Dane, Yu, Hua, Dashiell-Aje, Ebony, Robinson, Tara M., Mahlangu, Johnny
المساهمون: BioMarin Pharmaceutical Inc
المصدر: Journal of Thrombosis and Haemostasis ; ISSN 1538-7836
مصطلحات موضوعية: Hematology
الإتاحة: https://doi.org/10.1016/j.jtha.2024.04.001Test
https://api.elsevier.com/content/article/PII:S1538783624001843?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S1538783624001843?httpAccept=text/plainTest -
6دورية أكاديمية
المؤلفون: Mahlangu, Johnny, Kaczmarek, Radoslaw, von Drygalski, Annette, Shapiro, Susan, Chou, Sheng-Chieh, Ozelo, Margareth C, Kenet, Gili, Peyvandi, Flora, Wang, Michael, Madan, Bella, Key, Nigel S, Laffan, Michael, Dunn, Amy L, Mason, Jane, Quon, Doris V, Symington, Emily, Leavitt, Andrew D, Oldenburg, Johannes, Chambost, Hervé, Reding, Mark T, Jayaram, Kala, Yu, Hua, Mahajan, Reena, Chavele, Konstantia-Maria, Reddy, Divya B, Henshaw, Joshua, Robinson, Tara M, Wong, Wing Yen, Pipe, Steven W, GENEr8-1 Trial Group, Hermans, Cédric
المساهمون: UCL - SSS/IREC/CARD - Pôle de recherche cardiovasculaire, UCL - (SLuc) Service d'hématologie, UCL - (SLuc) Centre de malformations vasculaires congénitales
المصدر: The New England journal of medicine, Vol. 388, no.8, p. 694-705 (2023)
مصطلحات موضوعية: Humans, Male, Factor VIII, Gene Transfer Techniques, Half-Life, Hemophilia A, Hemorrhage, Recombinant Fusion Proteins
العلاقة: boreal:274106; http://hdl.handle.net/2078.1/274106Test; info:pmid/36812433; urn:ISSN:0028-4793; urn:EISSN:1533-4406
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7دورية أكاديمية
المؤلفون: Reding, Mark T, Pabinger, Ingrid, Holme, PÃ¥l Andrè, Maas Enriquez, Monika, Mancuso, Maria Elisa, Lalezari, Shadan, Miesbach, Wolfgang, Di Minno, Giovanni, Klamroth, Robert, Hermans, Cédric
المساهمون: UCL - SSS/IREC/CARD - Pôle de recherche cardiovasculaire, UCL - (SLuc) Service d'hématologie, UCL - (SLuc) Centre de malformations vasculaires congénitales
المصدر: Therapeutic advances in hematology, Vol. 14, p. [1–11] (2023)
مصطلحات موضوعية: PEGylated, comorbidities, extended half-life, haemophilia A, prophylaxis
العلاقة: boreal:275609; http://hdl.handle.net/2078.1/275609Test; info:pmid/37113811; urn:ISSN:2040-6207; urn:EISSN:2040-6215
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8دورية أكاديمية
المؤلفون: Reding, Mark T., Álvarez‐Román, María Teresa, Castaman, Giancarlo, Janbain, Maissaa, Matsushita, Tadashi, Meijer, Karina, Schmidt, Kathrin, Oldenburg, Johannes
المساهمون: Bayer
المصدر: European Journal of Haematology ; volume 112, issue 2, page 286-295 ; ISSN 0902-4441 1600-0609
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9دورية أكاديمية
المؤلفون: Reding, Mark T., Román, María Teresa Álvarez, Sanabria, Martin, Castaman, Giancarlo, Janbain, Maissa, Matsushita, Tadashi, Meijer, Karina, Schmidt, Kathrin, Oldenburg, Johannes
المصدر: Research and Practice in Thrombosis and Haemostasis ; volume 7, page 100243 ; ISSN 2475-0379
مصطلحات موضوعية: Hematology
الإتاحة: https://doi.org/10.1016/j.rpth.2023.100243Test
https://api.elsevier.com/content/article/PII:S2475037923004272?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S2475037923004272?httpAccept=text/plainTest -
10دورية أكاديمية
المؤلفون: Rafique, Amina, Srivastava, Alok, Abajas, Yasmina, Acharya, Suchitra, Ahuja, Sanjay, Román, María Teresa Álvarez, Carcao, Manuel, Dargaud, Yesim, Dunn, Amy, Hermans, Cédric, McGuinn, Catherine, Miesbach, Wolfgang, Reding, Mark T., Windyga, Jerzy, Bonzo, Daniel, Mitchell, Ian S., Wilkinson, Thomas A., Meeks, Shannon
المصدر: Research and Practice in Thrombosis and Haemostasis ; volume 7, page 100219 ; ISSN 2475-0379
مصطلحات موضوعية: Hematology
الإتاحة: https://doi.org/10.1016/j.rpth.2023.100219Test
https://api.elsevier.com/content/article/PII:S2475037923004089?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S2475037923004089?httpAccept=text/plainTest