-
1دورية أكاديمية
المؤلفون: Itzler, Robbin, Buckner, Tyler W., Leebeek, Frank W.G., Miller, Joel, Recht, Michael, Drelich, Douglass, Monahan, Paul E., Pipe, Steven W.
المصدر: Itzler , R , Buckner , T W , Leebeek , F W G , Miller , J , Recht , M , Drelich , D , Monahan , P E & Pipe , S W 2024 , ' Effect of etranacogene dezaparvovec on quality of life for severe and moderately severe haemophilia B participants : Results from the phase III HOPE-B trial 2 years after gene therapy ' , Haemophilia , vol. 30 , no. 3 , pp. 709-719 . https://doi.org/10.1111/hae.14977Test
وصف الملف: application/pdf
الإتاحة: https://doi.org/10.1111/hae.14977Test
https://pure.eur.nl/en/publications/c11d9ffa-6680-4f3e-9a28-be19d9e0cf69Test
https://pure.eur.nl/ws/files/143629828/Effect_of_etranacogene_dezaparvovec_on_quality_of_life_for_severe_and_moderately_severe_haemophilia_B_participants.pdfTest
http://www.scopus.com/inward/record.url?scp=85187413049&partnerID=8YFLogxKTest -
2دورية أكاديمية
المؤلفون: Pipe, Steven W., Collins, Peter W., Dhalluin, Christophe, Kenet, Gili, Schmitt, Christophe, Buri, Muriel, Jiménez-Yuste, Victor, Peyvandi, Flora, Young, Guy, Oldenburg, Johannes, Mancuso, Maria Elisa, Kavakli, Kaan, Kiialainen, Anna, Deb, Sonia, Niggli, Markus, Chang, Tiffany, Lehle, Michaela, Fijnvandraat, Karin
وصف الملف: application/pdf
العلاقة: https://orca.cardiff.ac.uk/id/eprint/165809/1/blood.2023021832.pdfTest; Pipe, Steven W., Collins, Peter W. https://orca.cardiff.ac.uk/view/cardiffauthors/A070283V.htmlTest orcid:0000-0002-6410-1324 orcid:0000-0002-6410-1324, Dhalluin, Christophe, Kenet, Gili, Schmitt, Christophe, Buri, Muriel, Jiménez-Yuste, Victor, Peyvandi, Flora, Young, Guy, Oldenburg, Johannes, Mancuso, Maria Elisa, Kavakli, Kaan, Kiialainen, Anna, Deb, Sonia, Niggli, Markus, Chang, Tiffany, Lehle, Michaela and Fijnvandraat, Karin 2024. Emicizumab prophylaxis in infants with hemophilia A (HAVEN 7): primary analysis of a phase 3b, open-label trial. Blood 14 , pp. 1355-1364. 10.1182/blood.2023021832 https://doi.org/10.1182/blood.2023021832Test file https://orca.cardiff.ac.uk/id/eprint/165809/1/blood.2023021832.pdfTest
الإتاحة: https://doi.org/10.1182/blood.2023021832Test
https://orca.cardiff.ac.uk/id/eprint/165809Test/
https://orca.cardiff.ac.uk/id/eprint/165809/1/blood.2023021832.pdfTest -
3دورية أكاديمية
المؤلفون: Young, Guy, Pipe, Steven W., Kenet, Gili, Oldenburg, Johannes, Safavi, Mariam, Czirok, Tuende, Nissen, Francis, Mahlangu, Johnny
المساهمون: F Hoffmann-La Roche Ltd
المصدر: Research and Practice in Thrombosis and Haemostasis ; page 102415 ; ISSN 2475-0379
مصطلحات موضوعية: Hematology
الإتاحة: https://doi.org/10.1016/j.rpth.2024.102415Test
https://api.elsevier.com/content/article/PII:S2475037924001043?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S2475037924001043?httpAccept=text/plainTest -
4دورية أكاديمية
المؤلفون: Madan, Bella, Ozelo, Margareth C., Raheja, Priyanka, Symington, Emily, Quon, Doris V., Leavitt, Andrew D., Pipe, Steven W., Lowe, Gillian, Kenet, Gili, Reding, Mark T., Mason, Jane, Wang, Michael, von Drygalski, Annette, Klamroth, Robert, Shapiro, Susan, Chambost, Hervé, Dunn, Amy L., Oldenburg, Johannes, Chou, Sheng-Chieh, Peyvandi, Flora, Millar, Carolyn M., Osmond, Dane, Yu, Hua, Dashiell-Aje, Ebony, Robinson, Tara M., Mahlangu, Johnny
المساهمون: BioMarin Pharmaceutical Inc
المصدر: Journal of Thrombosis and Haemostasis ; ISSN 1538-7836
مصطلحات موضوعية: Hematology
الإتاحة: https://doi.org/10.1016/j.jtha.2024.04.001Test
https://api.elsevier.com/content/article/PII:S1538783624001843?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S1538783624001843?httpAccept=text/plainTest -
5دورية أكاديمية
المؤلفون: Mahlangu, Johnny, Jiménez-Yuste, Víctor, Ventriglia, Giuliana, Niggli, Markus, Barlera, Simona, Hermans, Cédric, Lehle, Michaela, Chowdary, Pratima, Jew, Lyle, Windyga, Jerzy, Frenzel, Laurent, Schmitt, Christophe, Castaman, Giancarlo, Pipe, Steven W.
المساهمون: F. Hoffmann-La Roche Ltd
المصدر: Research and Practice in Thrombosis and Haemostasis ; volume 8, issue 2, page 102364 ; ISSN 2475-0379
مصطلحات موضوعية: Hematology
الإتاحة: https://doi.org/10.1016/j.rpth.2024.102364Test
https://api.elsevier.com/content/article/PII:S2475037924000530?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S2475037924000530?httpAccept=text/plainTest -
6دورية أكاديمية
المؤلفون: Kiialainen, Anna, Adamkewicz, Joanne I., Petry, Claire, Oldenburg, Johannes, Pipe, Steven W., Young, Guy, Mahlangu, Johnny, Lehle, Michaela, Niggli, Markus, Castaman, Giancarlo, Jiménez-Yuste, Víctor, Shima, Midori, Négrier, Claude, Schmitt, Christophe
المساهمون: F. Hoffmann-La Roche Ltd, F. Hoffmann-La Roche
المصدر: Research and Practice in Thrombosis and Haemostasis ; volume 8, issue 1, page 102306 ; ISSN 2475-0379
مصطلحات موضوعية: Hematology
الإتاحة: https://doi.org/10.1016/j.rpth.2023.102306Test
https://api.elsevier.com/content/article/PII:S2475037923057345?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S2475037923057345?httpAccept=text/plainTest -
7
المؤلفون: Srivastava, Alok, Santagostino, Elena, Dougall, Alison, Kitchen, Steve, Sutherland, Megan, Pipe, Steven W., Carcao, Manuel, Mahlangu, Johnny, Ragni, Margaret V., Windyga, Jerzy, Llinás, Adolfo, Goddard, Nicholas J., Mohan, Richa, Poonnoose, Pradeep M., Feldman, Brian M., Lewis, Sandra Zelman, van den Berg, H. Marijke, Pierce, Glenn F.
المساهمون: Ljung, Rolf, Creator
المصدر: Haemophilia. 26(S6):1-158
مصطلحات موضوعية: Medicin och hälsovetenskap, Klinisk medicin, Hematologi, Medical and Health Sciences, Clinical Medicine, Hematology
الوصول الحر: https://lup.lub.lu.se/record/5873c772-6a06-475a-8704-bfa26e858b52Test
http://dx.doi.org/10.1111/hae.14046Test -
8
المؤلفون: Chowdary, Pratima, Fischer, Kathelijn, Collins, Peter W., Cotterill, Amy, Konkle, Barbara A., Blanchette, Victor, Pipe, Steven W., Berntorp, Erik, Wolfsegger, Martin, Engl, Werner, Spotts, Gerald
المصدر: Thrombosis and Haemostasis. 120(5):728-736
مصطلحات موضوعية: coagulation factors, factor VIII, hemophilia A/B, pharmacodynamics, Medicin och hälsovetenskap, Klinisk medicin, Hematologi, Medical and Health Sciences, Clinical Medicine, Hematology
الوصول الحر: https://lup.lub.lu.se/record/a090d5f1-3332-441e-91e7-526601dc5290Test
http://dx.doi.org/10.1055/s-0040-1709519Test -
9دورية أكاديمية
المؤلفون: Lowe, Gillian, Fletcher, Simon, Lynch, Patrick James, Mahlangu, Johnny, Ozelo, Margareth C, Pembroke, Luke, Pipe, Steven W, Yamaguti-Hayakawa, Gabriela G, York, Deon, Robinson, Tara M, Yu, Hua, Valentino, Leonard A
المصدر: Future Rare Diseases ; volume 3, issue 4 ; ISSN 2399-5270
-
10دورية أكاديمية
المؤلفون: Srivastava, Alok, Rangarajan, Savita, Kavakli, Kaan, Klamroth, Robert, Kenet, Gili, Khoo, Liane, You, Chur-Woo, Xu, Weiqun, Malan, Niel, Frenzel, Laurent, Bagot, Catherine N., Stasyshyn, Oleksandra, Chang, Chia-Yau, Poloskey, Stacey, Qiu, Zhiying, Andersson, Shauna, Mei, Baisong, Pipe, Steven W.
وصف الملف: text
العلاقة: https://eprints.soton.ac.uk/477603/1/Fitusiran_003_ATLAS_INH_revised_4.0_tracked.docxTest; Srivastava, Alok, Rangarajan, Savita, Kavakli, Kaan, Klamroth, Robert, Kenet, Gili, Khoo, Liane, You, Chur-Woo, Xu, Weiqun, Malan, Niel, Frenzel, Laurent, Bagot, Catherine N., Stasyshyn, Oleksandra, Chang, Chia-Yau, Poloskey, Stacey, Qiu, Zhiying, Andersson, Shauna, Mei, Baisong and Pipe, Steven W. (2023) Fitusiran prophylaxis in people with severe haemophilia A or haemophilia B without inhibitors (ATLAS-A/B): a multicentre, open-label, randomised, phase 3 trial. The Lancet Haematology, 10 (5), e322-e332. (doi:10.1016/S2352-3026(23)00037-6 ).