المؤلفون: Chung, Sook Hyun, Sin, Tzu-Ni, Dang, Brian, Ngo, Taylor, Lo, Therlinder, Lent-Schochet, Daniella, Meleppat, Ratheesh K, Zawadzki, Robert J, Yiu, Glenn

مصطلحات موضوعية: Biochemistry and Cell Biology, Biological Sciences, Human Genome, Biotechnology, Neurodegenerative, Eye Disease and Disorders of Vision, Neurosciences, Aging, Genetics, Macular Degeneration, Aetiology, 2.1 Biological and endogenous factors, AAV, AMD, CRISPR, CRISPR-Cas9, GUIDE-seq, MT: RNA/DNA Editing, gene editing, neovascular AMD, ocular gene therapy, retinal gene therapy, Clinical Sciences, Biochemistry and cell biology

وصف الملف: application/pdf

الوصول الحر: https://escholarship.org/uc/item/5s36q0jsTest
https://escholarship.org/content/qt5s36q0js/qt5s36q0js.pdfTest

المؤلفون: Chung, Sook Hyun, Mollhoff, Iris Natalie, Mishra, Alaknanda, Sin, Tzu-Ni, Ngo, Taylor, Ciulla, Thomas, Sieving, Paul, Thomasy, Sara M, Yiu, Glenn

المصدر: Human Gene Therapy. 32(13-14)

مصطلحات موضوعية: Medical Biotechnology, Biomedical and Clinical Sciences, Immunology, Ophthalmology and Optometry, Neurosciences, Eye Disease and Disorders of Vision, Gene Therapy, Biotechnology, Genetics, 5.2 Cellular and gene therapies, Development of treatments and therapeutic interventions, Eye, Animals, Dependovirus, Genetic Vectors, Immunity, Macaca mulatta, Tissue Distribution, suprachoroidal injection, AAV, ocular gene therapy, host immune response, Clinical Sciences, Medical biotechnology

وصف الملف: application/pdf

الوصول الحر: https://escholarship.org/uc/item/3k82s8ngTest

المؤلفون: Sook Hyun Chung, Tzu-Ni Sin, Brian Dang, Taylor Ngo, Therlinder Lo, Daniella Lent-Schochet, Ratheesh K. Meleppat, Robert J. Zawadzki, Glenn Yiu

المصدر: Molecular Therapy: Nucleic Acids, Vol 28, Iss , Pp 613-622 (2022)

مصطلحات موضوعية: MT: RNA/DNA Editing, ocular gene therapy, AAV, CRISPR, AMD, neovascular AMD, Therapeutics. Pharmacology, RM1-950

وصف الملف: electronic resource

العلاقة: http://www.sciencedirect.com/science/article/pii/S2162253122000919Test; https://doaj.org/toc/2162-2531Test

الوصول الحر: https://doaj.org/article/bfb44be0cc0747e8bd3c8d258b7ce193Test

المؤلفون: Ghoraba HH, Akhavanrezayat A, Karaca I, Yavari N, Lajevardi S, Hwang J, Regenold J, Matsumiya W, Pham B, Zaidi M, Mobasserian A, DongChau AT, Or C, Yasar C, Mishra K, Do D, Nguyen QD

المصدر: Clinical Ophthalmology, Vol Volume 16, Pp 1753-1771 (2022)

مصطلحات موضوعية: ocular gene therapy, gene therapy, viral vectors, ocular inflammation, review, Ophthalmology, RE1-994

وصف الملف: electronic resource

العلاقة: https://www.dovepress.comTest/ocular-gene-therapy-a-literature-review-with-special-focus-on-immune-a-peer-reviewed-fulltext-article-OPTH; https://doaj.org/toc/1177-5483Test

الوصول الحر: https://doaj.org/article/080788d4fa4f4c3196d78307de856ff9Test

المؤلفون: Alan R. Abraham, Panayiotis Maghsoudlou, David A. Copland, Lindsay B. Nicholson, Andrew D. Dick

المصدر: Frontiers in Ophthalmology, Vol 3 (2023)

مصطلحات موضوعية: cell therapy, CAR-Treg, Treg, ophthalmology (MeSH), ocular gene therapy, autoimmune diseases, Medicine

وصف الملف: electronic resource

العلاقة: https://www.frontiersin.org/articles/10.3389/fopht.2023.1184937/fullTest; https://doaj.org/toc/2674-0826Test

الوصول الحر: https://doaj.org/article/8069023c56534c2999718624e633ea58Test

المؤلفون: Ren, Duohao, Fisson, Sylvain, Dalkara, Deniz, Ail, Divya

المساهمون: Institut de la Vision, Institut National de la Santé et de la Recherche Médicale (INSERM)-Sorbonne Université (SU)-Centre National de la Recherche Scientifique (CNRS), Approches génétiques intégrées et nouvelles thérapies pour les maladies rares (INTEGRARE), Université d'Évry-Val-d'Essonne (UEVE)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Université Paris-Saclay-Généthon

المصدر: ISSN: 1999-4923 ; Pharmaceutics ; https://inserm.hal.science/inserm-03806869Test ; Pharmaceutics, 2022, 14 (9), pp.1973. ⟨10.3390/pharmaceutics14091973⟩.

مصطلحات موضوعية: CRISPR-Cas9, Adeno-associated virus, immune responses, innate immune response, adaptive immune response, ocular gene therapy, [SDV.IMM]Life Sciences [q-bio]/Immunology

العلاقة: info:eu-repo/semantics/altIdentifier/pmid/36145721; inserm-03806869; https://inserm.hal.science/inserm-03806869Test; https://inserm.hal.science/inserm-03806869/documentTest; https://inserm.hal.science/inserm-03806869/file/2022-3-Pharmaceutics-Review-DA.pdfTest; PUBMED: 36145721; PUBMEDCENTRAL: PMC9502120

الإتاحة: https://doi.org/10.3390/pharmaceutics14091973Test
https://inserm.hal.science/inserm-03806869Test
https://inserm.hal.science/inserm-03806869/documentTest
https://inserm.hal.science/inserm-03806869/file/2022-3-Pharmaceutics-Review-DA.pdfTest

المؤلفون: Duohao Ren, Sylvain Fisson, Deniz Dalkara, Divya Ail

المصدر: Pharmaceutics; Volume 14; Issue 9; Pages: 1973

مصطلحات موضوعية: CRISPR–Cas9, Adeno-associated virus, immune responses, innate immune response, adaptive immune response, ocular gene therapy

وصف الملف: application/pdf

العلاقة: Gene and Cell Therapy; https://dx.doi.org/10.3390/pharmaceutics14091973Test

الإتاحة: https://doi.org/10.3390/pharmaceutics14091973Test

المؤلفون: Marie Pastor, Sandra Johnen, Nina Harmening, Mickäel Quiviger, Julie Pailloux, Martina Kropp, Peter Walter, Zoltán Ivics, Zsuzsanna Izsvák, Gabriele Thumann, Daniel Scherman, Corinne Marie

المصدر: Molecular Therapy: Nucleic Acids, Vol 11, Iss C, Pp 57-67 (2018)

مصطلحات موضوعية: age-related macular degeneration, electroporation, RPE cells, antibiotic-free pFAR4 vector, Sleeping Beauty transposon, ocular gene therapy, transfection, PEDF, VEGF, Therapeutics. Pharmacology, RM1-950

وصف الملف: electronic resource

العلاقة: http://www.sciencedirect.com/science/article/pii/S2162253117303189Test; https://doaj.org/toc/2162-2531Test

الوصول الحر: https://doaj.org/article/c0102cc49ae944f381497e5360d1481bTest

المؤلفون: Khanna, Hemant

مصطلحات موضوعية: medical history, medical archives, ophthalmology, visual sciences, ocular gene therapy, Eyes to the Past, Eye Diseases, Health Sciences and Medical Librarianship, History of Science, Technology, and Medicine, Medical Education, Medical Humanities

العلاقة: http://hdl.handle.net/20.500.14038/28755Test; https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=1000&context=eyes-to-the-past-presentations&unstamped=1Test; https://escholarship.umassmed.edu/eyes-to-the-past-presentations/1Test; eyes-to-the-past-presentations/1

الإتاحة: https://doi.org/10.13028/d22g-n975Test
https://doi.org/20.500.14038/28755Test
https://hdl.handle.net/20.500.14038/28755Test
https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=1000&context=eyes-to-the-past-presentations&unstamped=1Test
https://escholarship.umassmed.edu/eyes-to-the-past-presentations/1Test

المؤلفون: Auricchio, A, Smith, AJ, Ali, RR

المصدر: Human Gene Therapy , 28 (11) pp. 982-987. (2017)

مصطلحات موضوعية: eye, AAV, ocular gene therapy trials

وصف الملف: text

العلاقة: https://discovery.ucl.ac.uk/id/eprint/1571514/1/Auricchio_Future_25_years_Retinal_Gene_Therapy.pdfTest; https://discovery.ucl.ac.uk/id/eprint/1571514Test/

الإتاحة: https://discovery.ucl.ac.uk/id/eprint/1571514/1/Auricchio_Future_25_years_Retinal_Gene_Therapy.pdfTest
https://discovery.ucl.ac.uk/id/eprint/1571514Test/