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1مؤتمر
المؤلفون: Hendrickson, Dean, Cohen, Adam, Garrett, Gary
مصطلحات موضوعية: fish, texas, biodiversity data, occurrence, ichthyology collection, museum data, natural history data
وصف الملف: application/pdf
العلاقة: TNHC - Publications; https://hdl.handle.net/2152/117536Test; http://dx.doi.org/10.26153/tsw/44416Test
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2دورية أكاديمية
المؤلفون: Muntoni, Francesco, Signorovitch, James, Sajeev, Gautam, Goemans, Nathalie, Wong, Brenda L, Tian, Cuixia, Mercuri, Eugenio, Done, Nicolae, Wong, Hallee, Moss, Jackson, Yao, Zhiwen, Ward, Susan J, Manzur, Adnan, Servais, Laurent, Niks, Erik H, Straub, Volker, de Groot, Imelda Jm, McDonald, Craig
المساهمون: Pediatrics
المصدر: Neuromuscular disorders : NMD ; 32 ; 4 ; 271 ; 283 ; United Kingdom ; England
مصطلحات موضوعية: Clinical trials, Drug evaluation, Duchenne muscular dystrophy, External controls, Natural history data, Real-world data
العلاقة: Neuromuscular Disorders; https://doi.org/10.1016/j.nmd.2022.02.009Test; Muntoni F, Signorovitch J, Sajeev G, Goemans N, Wong B, Tian C, Mercuri E, Done N, Wong H, Moss J, Yao Z, Ward SJ, Manzur A, Servais L, Niks EH, Straub V, de Groot IJ, McDonald C; North Star Clinical Network, PRO-DMD-01 Study, The Association Française contre les Myopathies (AFM), The DMD Italian Group, and The Collaborative Trajectory Analysis Project (cTAP). Real-world and natural history data for drug evaluation in Duchenne muscular dystrophy: suitability of the North Star Ambulatory Assessment for comparisons with external controls. Neuromuscul Disord. 2022 Apr;32(4):271-283. doi:10.1016/j.nmd.2022.02.009. Epub 2022 Feb 25. PMID: 35396092.; http://hdl.handle.net/20.500.14038/52313Test; Neuromuscular disorders : NMD
الإتاحة: https://doi.org/10.1016/j.nmd.2022.02.009Test
https://doi.org/20.500.14038/52313Test
https://hdl.handle.net/20.500.14038/52313Test -
3دورية أكاديمية
المؤلفون: Eve Fouarge, Arnaud Monseur, Bruno Boulanger, Mélanie Annoussamy, Andreea M. Seferian, Silvana De Lucia, Charlotte Lilien, Leen Thielemans, Khazal Paradis, Belinda S. Cowling, Chris Freitag, Bradley P. Carlin, Laurent Servais, the NatHis-MTM Study Group
المصدر: Orphanet Journal of Rare Diseases, Vol 16, Iss 1, Pp 1-11 (2021)
مصطلحات موضوعية: Bayesian analysis, Centronuclear myopathy, Complex innovative clinical trial design, Disease progression model, Natural history data, Medicine
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/1750-1172Test
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4دورية أكاديمية
المؤلفون: Muntoni, Francesco, Signorovitch, James, Sajeev, Gautam, Goemans, Nathalie, Wong, Brenda, Tian, Cuixia, Mercuri, Eugenio, Done, Nicolae, Wong, Hallee, Moss, Jackson, Yao, Zhiwen, Ward, Susan J, Manzur, Adnan, Servais, Laurent, Niks, Erik H, Straub, Volker, de Groot, Imelda Jm, McDonald, Craig, North Star Clinical Network, PRO-DMD-01 Study, The Association F
المصدر: Neuromuscular Disorders (2022) (In press).
مصطلحات موضوعية: Clinical trials, Drug evaluation, Duchenne muscular dystrophy, External controls, Natural history data, Real-world data
وصف الملف: application/pdf
العلاقة: https://discovery.ucl.ac.uk/id/eprint/10147153/1/1-s2.0-S096089662200061X-main.pdfTest; https://discovery.ucl.ac.uk/id/eprint/10147153Test/
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5مؤتمر
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6مؤتمر
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7دورية أكاديمية
المؤلفون: Muntoni F., Bertini E., Comi G., Kirschner J., Lusakowska A., Mercuri E., Scoto M., van der Pol W. L., Vuillerot C., Burdeska A., El-Khairi M., Fontoura P., Ives J., Gorni K., Reid C., Fuerst-Recktenwald S.
المساهمون: F. Muntoni, E. Bertini, G. Comi, J. Kirschner, A. Lusakowska, E. Mercuri, M. Scoto, W.L. van der Pol, C. Vuillerot, A. Burdeska, M. El-Khairi, P. Fontoura, J. Ive, K. Gorni, C. Reid, S. Fuerst-Recktenwald
مصطلحات موضوعية: Longitudinal study, Motor function measure, Natural history data, Olesoxime, Spinal muscular atrophy, Settore MED/26 - Neurologia
العلاقة: info:eu-repo/semantics/altIdentifier/pmid/33246887; info:eu-repo/semantics/altIdentifier/wos/WOS:000598364000002; volume:30; issue:12; firstpage:959; lastpage:969; numberofpages:11; journal:NEUROMUSCULAR DISORDERS; http://hdl.handle.net/2434/857391Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85096893348
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8دورية أكاديمية
المؤلفون: Muntoni, F, Bertini, E, Comi, G, Kirschner, J, Lusakowska, A, Mercuri, E, Scoto, M, van der Pol, WL, Vuillerot, C, Burdeska, A, El-Khairi, M, Fontoura, P, Ives, J, Gorni, K, Reid, C, Fuerst-Recktenwald, S
المصدر: Neuromuscular Disorders , 30 (12) pp. 959-969. (2020)
مصطلحات موضوعية: Olesoxime, Spinal muscular atrophy, Motor function measure, Natural history data, Longitudinal study
وصف الملف: text
العلاقة: https://discovery.ucl.ac.uk/id/eprint/10132244/1/1-s2.0-S0960896620306453-main.pdfTest; https://discovery.ucl.ac.uk/id/eprint/10132244Test/
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9مؤتمر
المؤلفون: Macklin,James, Glöckler,Falko, Hoffmann,Jana, Ronquist,Fredrik, Daume,Stefan, Haston,Elspeth
المصدر: Biodiversity Information Science and Standards 1: e20216
مصطلحات موضوعية: Natural History Collection Management System, Information System, Natural History Data, DINA Consortium, Open-Source
وصف الملف: text/html
العلاقة: info:eu-repo/semantics/altIdentifier/eissn/2535-0897
الإتاحة: https://doi.org/10.3897/tdwgproceedings.1.20216Test
https://biss.pensoft.net/article/20216Test/ -
10دورية أكاديمية
المؤلفون: Koch, Gerda, Koch, Walter
المصدر: Mitteilungen der Vereinigung Österreichischer Bibliothekarinnen und Bibliothekare; Bd. 70 Nr. 2 (2017): Metadata - Metadaten; 170-178 ; Communications of the Association of Austrian Librarians; Vol. 70 No. 2 (2017): Metadata - Metadaten; 170-178 ; 2791-4011 ; 1022-2588 ; 10.31263/voebm.v70i2
مصطلحات موضوعية: Verlinkung von Daten, Anreicherung von Daten, Microservices, Datenaggregation, Europeana, Kulturerbedaten, Naturhistorische Daten, Audiosammlungen, Annotationen, Linked data, data enrichment, data aggregation, cultural heritage metadata, natural history data, audio collections, data annotation
وصف الملف: application/pdf
العلاقة: https://journals.univie.ac.at/index.php/voebm/article/view/2071/1595Test; https://journals.univie.ac.at/index.php/voebm/article/view/2071Test