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1دورية أكاديمية
المؤلفون: Arjunan, Porkizhi, Kathirvelu, Durga, Mahalingam, Gokulnath, Goel, Ashish Kumar, Zacharaiah, Uday George, Srivastava, Alok, Marepally, Srujan
المصدر: Acta Pharmaceutica Sinica B ; ISSN 2211-3835
الإتاحة: https://doi.org/10.1016/j.apsb.2024.04.015Test
https://api.elsevier.com/content/article/PII:S2211383524001448?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S2211383524001448?httpAccept=text/plainTest -
2دورية أكاديمية
المؤلفون: Rajendiran, Vignesh, Devaraju, Nivedhitha, Haddad, Mahdi, Ravi, Nithin Sam, Panigrahi, Lokesh, Paul, Joshua, Gopalakrishnan, Chandrasekar, Wyman, Stacia, Ariudainambi, Keerthiga, Mahalingam, Gokulnath, Periyasami, Yogapriya, Prasad, Kirti, George, Anila, Sukumaran, Dhiyaneshwaran, Gopinathan, Sandhiya, Pai, Aswin Anand, Nakamura, Yukio, Balasubramanian, Poonkuzhali, Ramalingam, Rajasekaran, Thangavel, Saravanabhavan, Velayudhan, Shaji R., Corn, Jacob E., Mackay, Joel P., Marepally, Srujan, Srivastava, Alok, Crossley, Merlin, Mohankumar, Kumarasamypet M.
المساهمون: Wellcome Trust DBT India Alliance, Australian Medical Council, India Ministry of Science & Technology Department of Biotechnology, Indian Council of Medical Research, Science and Engineering Research Board
المصدر: Molecular Therapy ; volume 32, issue 3, page 663-677 ; ISSN 1525-0016
مصطلحات موضوعية: Drug Discovery, Pharmacology, Genetics, Molecular Biology, Molecular Medicine
الإتاحة: https://doi.org/10.1016/j.ymthe.2024.01.023Test
https://api.elsevier.com/content/article/PII:S1525001624000236?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S1525001624000236?httpAccept=text/plainTest -
3دورية أكاديمية
المؤلفون: Ravi, Nithin Sam, Wienert, Beeke, Wyman, Stacia K, Bell, Henry William, George, Anila, Mahalingam, Gokulnath, Vu, Jonathan T, Prasad, Kirti, Bandlamudi, Bhanu Prasad, Devaraju, Nivedhitha, Rajendiran, Vignesh, Syedbasha, Nazar, Pai, Aswin Anand, Nakamura, Yukio, Kurita, Ryo, Narayanasamy, Muthuraman, Balasubramanian, Poonkuzhali, Thangavel, Saravanabhavan, Marepally, Srujan, Velayudhan, Shaji R, Srivastava, Alok, DeWitt, Mark A, Crossley, Merlin, Corn, Jacob E, Mohankumar, Kumarasamypet M
مصطلحات موضوعية: Biomedical and Clinical Sciences, Cardiovascular Medicine and Haematology, Hematology, Rare Diseases, Sickle Cell Disease, Stem Cell Research, Stem Cell Research - Nonembryonic - Human, Genetics, Aetiology, 2.1 Biological and endogenous factors, Adenine, Anemia, Sickle Cell, CRISPR-Cas Systems, Cell Line, Clustered Regularly Interspaced Short Palindromic Repeats, Cytosine, Fetal Hemoglobin, Gene Editing, Hematopoietic Stem Cells, Humans, Point Mutation, Promoter Regions, Genetic, beta-Globins, beta-Thalassemia, gamma-Globins, base editing, globin regulation, HPFH mutations, beta-hemoglobinopathies, fetal hemoglobin, CRISPR, Cas9, Base editing, Beta hemoglobinopathies, Fetal hemoglobin, Globin regulation, HBGpromoter, Sickle cell disease, Beta-thalassemia, Large deletions, CD34+HSPCs, CRISPR/Cas9, beta hemoglobinopathies, beta-thalassemia, cd34+ hspcs, chromosomes, crispr/cas9, gene expression, genetics, genomics, hbgpromoter, hpfh mutations, large deletions, sickle cell disease, Biochemistry and Cell Biology, Biological sciences, Biomedical and clinical sciences, Health sciences
وصف الملف: application/pdf
الوصول الحر: https://escholarship.org/uc/item/9v15g37tTest
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4دورية أكاديمية
المؤلفون: Mahalingam, Gokulnath, Arjunan, Porkizhi, Periyasami, Yogapriya, Dhyani, Ajay Kumar, Devaraju, Nivedita, Rajendiran, Vignesh, Christopher, Abisha Crystal, KT, Ramya Devi, Dhanasingh, Immanuel, Thangavel, Saravanabhavan, Murugesan, Mohankumar, Moorthy, Mahesh, Srivastava, Alok, Marepally, Srujan
المساهمون: Department of Biotechnology, Ministry of Science and Technology, India
المصدر: Scientific Reports ; volume 13, issue 1 ; ISSN 2045-2322
مصطلحات موضوعية: Multidisciplinary
الإتاحة: https://doi.org/10.1038/s41598-023-35070-2Test
https://www.nature.com/articles/s41598-023-35070-2.pdfTest
https://www.nature.com/articles/s41598-023-35070-2Test -
5دورية أكاديمية
المصدر: Frontiers in Genome Editing ; volume 5 ; ISSN 2673-3439
مصطلحات موضوعية: Education, Cultural Studies
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6دورية أكاديمية
المؤلفون: Lohchania, Brijesh, Christopher, Abisha Crystal, Arjunan, Porkizhi, Mahalingam, Gokulnath, Kathirvelu, Durga, Prasannan, Aishwarya, Venkatesan, Vigneshwaran, Taneja, Pankaj, KM, Mohan Kumar, Thangavel, Saravanabhavan, Marepally, Srujan
المساهمون: Department of Biotechnology, Ministry of Science and Technology, India
المصدر: Frontiers in Bioengineering and Biotechnology ; volume 10 ; ISSN 2296-4185
مصطلحات موضوعية: Biomedical Engineering, Histology, Bioengineering, Biotechnology
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7دورية أكاديمية
المؤلفون: Venkatesan, Vigneshwaran, Christopher, Abisha Crystal, Rhiel, Manuel, Azhagiri, Manoj Kumar K., Babu, Prathibha, Walavalkar, Kaivalya, Saravanan, Bharath, Andrieux, Geoffroy, Rangaraj, Sumathi, Srinivasan, Saranya, Karuppusamy, Karthik V., Jacob, Annlin, Bagchi, Abhirup, Pai, Aswin Anand, Nakamura, Yukio, Kurita, Ryo, Balasubramanian, Poonkuzhali, Pai, Rekha, Marepally, Srujan Kumar, Mohankumar, Kumarasamypet Murugesan, Velayudhan, Shaji R., Boerries, Melanie, Notani, Dimple, Cathomen, Toni, Srivastava, Alok, Thangavel, Saravanabhavan
المصدر: Molecular Therapy - Nucleic Acids ; volume 32, page 671-688 ; ISSN 2162-2531
مصطلحات موضوعية: Drug Discovery, Molecular Medicine
الإتاحة: https://doi.org/10.1016/j.omtn.2023.04.024Test
https://api.elsevier.com/content/article/PII:S2162253123001105?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S2162253123001105?httpAccept=text/plainTest -
8دورية
المؤلفون: Mahalingam, Gokulnath, Rachamalla, Hari Krishnareddy, Arjunan, Porkizhi, Karuppusamy, Karthik V., Periyasami, Yogapriya, Mohan, Aruna, Subramaniyam, Kanimozhi, M, Salma, Rajendran, Vigneshwar, Moorthy, Mahesh, Varghese, George M., Mohankumar, Kumarasamypet M., Thangavel, Saravanabhavan, Srivastava, Alok, Marepally, Srujan
المصدر: Molecular Therapy; May 2024, Vol. 32 Issue: 5 p1284-1297, 14p
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9دورية أكاديمية
المؤلفون: Mahalingam, Gokulnath, Marepally, Srujan
المصدر: Mol Ther ; ISSN:1525-0024 ; Volume:32 ; Issue:4
العلاقة: https://doi.org/10.1016/j.ymthe.2024.03.011Test; https://pubmed.ncbi.nlm.nih.gov/38503298Test; https://www.ncbi.nlm.nih.gov/pmc/articles/PMC11163211Test/
الإتاحة: https://doi.org/10.1016/j.ymthe.2024.03.011Test
https://pubmed.ncbi.nlm.nih.gov/38503298Test
https://www.ncbi.nlm.nih.gov/pmc/articles/PMC11163211Test/ -
10دورية أكاديمية
المؤلفون: Ravi, Nithin Sam, Wienert, Beeke, Wyman, Stacia K., Bell, Henry William, George, Anila, Mahalingam, Gokulnath, Vu, Jonathan T., Prasad, Kirti, Bandlamudi, Bhanu Prasad, Devaraju, Nivedhitha, Rajendiran, Vignesh, Syedbasha, Nazar, Pai, Aswin Anand, Nakamura, Yukio, Kurita, Ryo, Narayanasamy, Muthuraman, Balasubramanian, Poonkuzhali, Thangavel, Saravanabhavan, Marepally, Srujan, Velayudhan, Shaji R., Srivastava, Alok, DeWitt, Mark A., Crossley, Merlin, Corn, Jacob E., Mohankumar, Kumarasamypet M.
المصدر: eLife, 11
مصطلحات موضوعية: CRISPR/Cas9, HPFH mutations, base editing, beta hemoglobinopathies, beta-thalassemia, cd34+ hspcs, chromosomes, fetal hemoglobin, gene expression, genetics, genomics, globin regulation, hbgpromoter, large deletions, sickle cell disease
وصف الملف: application/application/pdf
الإتاحة: https://doi.org/20.500.11850/593666Test
https://doi.org/10.3929/ethz-b-000593666Test
https://doi.org/10.7554/eLife.65421Test
https://hdl.handle.net/20.500.11850/593666Test