التفاصيل البيبلوغرافية
العنوان: |
FIREFISH Parts 1 and 2: 36-month safety and efficacy of risdiplam in Type 1 spinal muscular atrophy (SMA) (P7-9.009) |
المؤلفون: |
Basil Darras, Giovanni Baranello, Odile Boespflug-Tanguy, John Day, Nicholas Deconinck, Andrea Klein, Ricardo Masson, Maria Mazurkiewicz-Bełdzińska, Eugenio Mercuri, Kristy Rose, Dmitry Vlodavets, Hui Xiong, Edmar Zanoteli, Muna El-Khairi, Marianne Gerber, Ksenija Gorni, Heidemarie Kletzl, Laura Palfreeman, Angela Dodman, Laurent Servais |
المصدر: |
Tuesday, April 25. |
بيانات النشر: |
Lippincott Williams & Wilkins, 2023. |
سنة النشر: |
2023 |
الوصول الحر: |
https://explore.openaire.eu/search/publication?articleId=doi_________::6667a1d6337d215483d25780abd97f6aTest https://doi.org/10.1212/wnl.0000000000203624Test |
رقم الانضمام: |
edsair.doi...........6667a1d6337d215483d25780abd97f6a |
قاعدة البيانات: |
OpenAIRE |