FIREFISH Parts 1 and 2: 36-month safety and efficacy of risdiplam in Type 1 spinal muscular atrophy (SMA) (P7-9.009)

التفاصيل البيبلوغرافية
العنوان: FIREFISH Parts 1 and 2: 36-month safety and efficacy of risdiplam in Type 1 spinal muscular atrophy (SMA) (P7-9.009)
المؤلفون: Basil Darras, Giovanni Baranello, Odile Boespflug-Tanguy, John Day, Nicholas Deconinck, Andrea Klein, Ricardo Masson, Maria Mazurkiewicz-Bełdzińska, Eugenio Mercuri, Kristy Rose, Dmitry Vlodavets, Hui Xiong, Edmar Zanoteli, Muna El-Khairi, Marianne Gerber, Ksenija Gorni, Heidemarie Kletzl, Laura Palfreeman, Angela Dodman, Laurent Servais
المصدر: Tuesday, April 25.
بيانات النشر: Lippincott Williams & Wilkins, 2023.
سنة النشر: 2023
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::6667a1d6337d215483d25780abd97f6aTest
https://doi.org/10.1212/wnl.0000000000203624Test
رقم الانضمام: edsair.doi...........6667a1d6337d215483d25780abd97f6a
قاعدة البيانات: OpenAIRE