المؤلفون: Lingineni, Karthik, Aggarwal, Varun, Morales, Juan, Conrado, Daniela, Corey, Diane, Vong, Camille, Burton, Jackson, Larkindale, Jane, Romero, Klaus, Schmidt, Stephan, Kim, Sarah

المصدر: CPT: Pharmacometrics and Systems Pharmacology. 11(3)

مصطلحات موضوعية: Child, Computer Simulation, Disease Progression, Humans, Muscular Dystrophy, Duchenne, Vital Capacity

وصف الملف: application/pdf

الوصول الحر: https://escholarship.org/uc/item/3bk5j4rsTest

المؤلفون: Beaverson, Katherine L., Julkowska, Daria, Letinturier, Mary Catherine V., Aartsma-Rus, Annemieke, Austin, Jennifer, Bueren, Juan, Frost, Simon, Hamamura, Misako, Larkindale, Jane, LaRosa, Greg, Magenheim, Rita, Merico, Annamaria, Pasmooij, Anna Maria Gerdina, Pirard, Vinciane, Ekow Thomford, Nicholas, Wada, Michihiko, Wong-Rieger, Durhane, Hartman, Adam L.

المساهمون: European Union’s Horizon 2020 research and innovation programme

المصدر: Therapeutic Advances in Rare Disease ; volume 4 ; ISSN 2633-0040 2633-0040

مصطلحات موضوعية: General Medicine

الإتاحة: https://doi.org/10.1177/26330040231188979Test

المؤلفون: Larkindale, Jane

مرشدي الرسالة: Knight, Marc

مصطلحات موضوعية: 583, Molecular Plant Physiology, Cell Biology (plants), cell signalling, arabidopsis, heat shock, abiotic stress

الإتاحة: http://ethos.bl.uk/OrderDetails.do?uin=uk.bl.ethos.249479Test

المؤلفون: Cheever, Thomas R, Berkley, Dale, Braun, Serge, Brown, Robert H, Byrne, Barry J, Chamberlain, Jeffrey S, Cwik, Valerie, Duan, Dongsheng, Federoff, Howard J, High, Katherine A, Kaspar, Brian K, Klinger, Katherine W, Larkindale, Jane, Lincecum, John, Mavilio, Fulvio, McDonald, Cheryl L, McLaughlin, James, McLeod, Bonnie Weiss, Mendell, Jerry R, Nuckolls, Glen, Stedman, Hansell H, Tagle, Danilo A, Vandenberghe, Luk H, Wang, Hao, Wernett, Pamela J, Wilson, James M, Porter, John D, Gubitz, Amelie K

المصدر: Human Gene Therapy. 26(3)

مصطلحات موضوعية: Muscular Dystrophy, Intellectual and Developmental Disabilities (IDD), Rare Diseases, Brain Disorders, Neurosciences, Mental Health, Orphan Drug, Gene Therapy, Pediatric, Genetics, Clinical Trials as Topic, Genetic Therapy, Government Regulation, Humans, Intellectual Property, Neuromuscular Diseases

وصف الملف: application/pdf

الوصول الحر: https://escholarship.org/uc/item/8z40m0q8Test

المؤلفون: Karpen, Stephen R., White, J. Kael, Mullin, Ariana P., O’Doherty, Inish, Hudson, Lynn D., Romero, Klaus, Sivakumaran, Sudhir, Stephenson, Diane, Turner, Emily C., Larkindale, Jane

المساهمون: U.S. Food and Drug Administration

المصدر: Therapeutic Innovation & Regulatory Science ; volume 55, issue 3, page 591-600 ; ISSN 2168-4790 2168-4804

مصطلحات موضوعية: Pharmacology (medical), Public Health, Environmental and Occupational Health, Pharmacology, Toxicology and Pharmaceutics (miscellaneous)

الإتاحة: https://doi.org/10.1007/s43441-020-00255-8Test

المؤلفون: Mullin, Ariana P., Corey, Diane, Turner, Emily C., Liwski, Richard, Olson, Daniel, Burton, Jackson, Sivakumaran, Sudhir, Hudson, Lynn D., Romero, Klaus, Stephenson, Diane T., Larkindale, Jane

المساهمون: Parent Project Muscular Dystrophy, CHDI Foundation, Food and Drug Administration

المصدر: Clinical and Translational Science ; volume 14, issue 1, page 214-221 ; ISSN 1752-8054 1752-8062

الإتاحة: https://doi.org/10.1111/cts.12845Test

المؤلفون: Schomaker, Shelli, Potter, David, Warner, Roscoe, Larkindale, Jane, King, Nicholas, Porter, Amy C., Owens, Jane, Tomlinson, Lindsay, Sauer, John-Michael, Johnson, Kent, Aubrecht, Jiri

المساهمون: Avila, Matias A.

المصدر: PLOS ONE ; volume 15, issue 5, page e0229753 ; ISSN 1932-6203

الإتاحة: https://doi.org/10.1371/journal.pone.0229753Test

المؤلفون: Seabury, Jamison, Rosero, Spencer, Varma, Anika, Weinstein, Jennifer, Engebrecht, Charlotte, Dilek, Nuran, Heatwole, John, Alexandrou, Danae, Cohen, Brittany, Larkindale, Jane, Lynch, David R., Park, Courtney, Subramony, Sub H., Wagner, Ellen, Walther, Susan, Wells, McKenzie, Zizzi, Christine, Heatwole, Chad

المصدر: Neurology: Clinical Practice; Oct2023, Vol. 13 Issue 5, p1-10, 10p

المؤلفون: Mellion, Michelle, Larkindale, Jane, Lonkar, Pallavi, Goyal, Jaya, Holland, Ashling, Foy, Jeff, Garg, Brijesh, Yu, Shaoxia, Frank, Anthony, Abbott, Chris, Svenstrup, Niels, Cormier, Jennifer, Vacca, Sarah, McArthur, James

المصدر: Neurology ; volume 100, issue 17_supplement_2 ; ISSN 0028-3878 1526-632X

الإتاحة: https://doi.org/10.1212/wnl.0000000000203955Test

المؤلفون: Seabury, Jamison, Alexandrou, Danae, Dilek, Nuran, Cohen, Brittany, Heatwole, John, Larkindale, Jane, Lynch, David R., Park, Courtney, Rosero, Spencer, Subramony, Sub H., Varma, Anika, Wagner, Ellen, Walther, Susan, Weinstein, Jennifer, Wells, McKenzie, Zizzi, Christine, Heatwole, Chad

المصدر: Neurology ; volume 100, issue 8 ; ISSN 0028-3878 1526-632X

الإتاحة: https://doi.org/10.1212/wnl.0000000000201598Test