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1دورية أكاديمية
المؤلفون: Pratima Chowdary, Margareta Holmström, Johnny N. Mahlangu, Margaret C. Ozelo, Ingrid Pabinger, K. John Pasi, Margaret V. Ragni, Amy Shapiro, Chris Barnowski, Stefan Lethagen
المصدر: Research and Practice in Thrombosis and Haemostasis, Vol 6, Iss 5, Pp n/a-n/a (2022)
مصطلحات موضوعية: factor IX fc fusion protein, factor VIII Fc fusion protein, hemophilia A, hemophilia B, recombinant fusion proteins, safety, Diseases of the blood and blood-forming organs, RC633-647.5
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/2475-0379Test
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2دورية أكاديمية
المؤلفون: Flora Peyvandi, David Lillicrap, Johnny Mahlangu, Claire McLintock, K. John Pasi, Steven W. Pipe, Wendy Scales, Alok Srivastava, Thierry VandenDriessche
المصدر: Research and Practice in Thrombosis and Haemostasis, Vol 4, Iss 4, Pp 644-651 (2020)
مصطلحات موضوعية: gene therapy, hemophilia, knowledge gaps, physicians, respondents, survey, Diseases of the blood and blood-forming organs, RC633-647.5
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/2475-0379Test
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المؤلفون: Steven W. Pipe, Frank W.G. Leebeek, Michael Recht, Nigel S. Key, Giancarlo Castaman, Wolfgang Miesbach, Susan Lattimore, Kathelijne Peerlinck, Paul Van der Valk, Michiel Coppens, Peter Kampmann, Karina Meijer, Niamh O’Connell, K. John Pasi, Daniel P. Hart, Rashid Kazmi, Jan Astermark, Cedric R.J.R. Hermans, Robert Klamroth, Richard Lemons, Nathan Visweshwar, Annette von Drygalski, Guy Young, Shelley E. Crary, Miguel Escobar, Esteban Gomez, Rebecca Kruse-Jarres, Doris V. Quon, Emily Symington, Michael Wang, Allison P. Wheeler, Robert Gut, Ying P. Liu, Ricardo E. Dolmetsch, David L. Cooper, Yanyan Li, Brahm Goldstein, Paul E. Monahan
المساهمون: Vascular Medicine, ACS - Pulmonary hypertension & thrombosis, ACS - Amsterdam Cardiovascular Sciences, Real World Studies in PharmacoEpidemiology, -Genetics, -Economics and -Therapy (PEGET), Hematology
المصدر: New England journal of medicine, 388(8), 706-718. Massachussetts Medical Society
New England Journal of Medicine, 388(8), 706-718. MASSACHUSETTS MEDICAL SOC
New England Journal of Medicine, 388(8), 706-718. Massachussetts Medical Societyمصطلحات موضوعية: Coagulation, Genetics, General Medicine, Genetics General, Childhood Diseases, Hematology/Oncology, Pediatrics
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::18ec00c53efc81770ed02e6372363e8bTest
https://hdl.handle.net/11370/bcd8e7fb-66c2-4b0f-b235-d2995c4d444fTest -
4دورية أكاديمية
المؤلفون: K John Pasi
المصدر: Clinical Medicine Insights: Blood Disorders, Vol 14 (2021)
مصطلحات موضوعية: Diseases of the blood and blood-forming organs, RC633-647.5
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/1179-545XTest
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المؤلفون: Amy D. Shapiro, Roshni Daniel Kulkarni, Margaret V Ragni, Herve Chambost, Johnny N Mahlangu, Johannes Oldenburg, Beatrice Nolan, Margareth C Ozelo, Meredith C Foster, Annemieke Willemze, Chris Barnowski, Nisha Jain, Bent Winding, Jennifer Dumont, Stefan Lethagen, Chris Barnes, K John Pasi
المصدر: Blood Advances.
مصطلحات موضوعية: Hematology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::9b3492f3b3a5f76dd4bbf7bdc817f3ebTest
https://doi.org/10.1182/bloodadvances.2022009230Test -
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المؤلفون: Margareth C, Ozelo, Johnny, Mahlangu, K John, Pasi, Adam, Giermasz, Andrew D, Leavitt, Michael, Laffan, Emily, Symington, Doris V, Quon, Jiaan-Der, Wang, Kathelijne, Peerlinck, Steven W, Pipe, Bella, Madan, Nigel S, Key, Glenn F, Pierce, Brian, O'Mahony, Radoslaw, Kaczmarek, Joshua, Henshaw, Adebayo, Lawal, Kala, Jayaram, Mei, Huang, Xinqun, Yang, Wing Y, Wong, Benjamin, Kim, Annette, Von Drygalski
المصدر: New England Journal of Medicine. 386:1013-1025
مصطلحات موضوعية: Adult, Male, GENEr8-1 Trial Group, Factor VIII, Genetic Vectors, Alanine Transaminase, Hemorrhage, Genetic Therapy, General Medicine, Dependovirus, Hemophilia A, Intention to Treat Analysis, HIV Seronegativity, General & Internal Medicine, Humans, Infusions, Intravenous, 11 Medical and Health Sciences
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::3b7596a3e58a0a0931c39ea2ce694c13Test
https://doi.org/10.1056/nejmoa2113708Test -
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المؤلفون: Emily Symington, Glenn F. Pierce, Adam Giermasz, K. John Pasi, Stefan Tiefenbacher, Stephen J. Zoog, Mary Robinson, Savita Rangarajan, Steffen Rosen, Christian Vettermann, Donnie Mackenzie, Jaydeep K. Srimani, Benjamin Kim, Mei Huang, Terri Christianson
المصدر: Blood. 136:2524-2534
مصطلحات موضوعية: Male, congenital, hereditary, and neonatal diseases and abnormalities, Genetic enhancement, Transgene, Immunology, 030204 cardiovascular system & hematology, Pharmacology, Hemophilia A, Biochemistry, Virus, law.invention, 03 medical and health sciences, 0302 clinical medicine, Thrombin, Parvovirinae, law, hemic and lymphatic diseases, medicine, Humans, media_common.cataloged_instance, Transgenes, European union, media_common, Factor VIII, business.industry, Genetic Therapy, Cell Biology, Hematology, Dependovirus, Coagulation, Recombinant DNA, Specific activity, business, 030215 immunology, medicine.drug
وصف الملف: text
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::b7b54fc4a67379b3e101a905a194db2aTest
https://doi.org/10.1182/blood.2020005683Test -
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المؤلفون: Glenn F. Pierce, Johnny Mahlangu, Thomas Sannié, David Lillicrap, Alok Srivastava, Dawn Rottellini, Donna Coffin, Thierry VandenDriessche, K. John Pasi, Radoslaw Kaczmarek, Alain Weill
المساهمون: Basic (bio-) Medical Sciences, Division of Gene Therapy & Regenerative Medicine
المصدر: Haemophilia. 26:443-449
مصطلحات موضوعية: medicine.medical_specialty, Consensus, media_common.quotation_subject, Genetic enhancement, haemophilia, 030204 cardiovascular system & hematology, Hemophilia A, Haemophilia, 03 medical and health sciences, 0302 clinical medicine, Multidisciplinary approach, Voting, medicine, Humans, Challenges, round table, Genetics (clinical), media_common, Medicine(all), business.industry, Health technology, Gene Therapy, Genetic Therapy, Hematology, General Medicine, global, Payment, medicine.disease, Clinical trial, Round table, Family medicine, business, 030215 immunology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::c38e32ba755156877323ace2a466b82dTest
https://doi.org/10.1111/hae.13971Test -
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المؤلفون: Bent Winding, Keiji Nogami, Guy Young, Chris Barnes, Huixing Yuan, Johannes Oldenburg, Elena Santagostino, Liane Khoo, Beatrice Nolan, Barbara A. Konkle, Joachim Fruebis, K. John Pasi, Ingrid Pabinger, Dan Rudin, Johnny Mahlangu
المصدر: Haemophilia
مصطلحات موضوعية: Adult, Male, medicine.medical_specialty, Adolescent, Recombinant Fusion Proteins, 030204 cardiovascular system & hematology, Haemophilia, Hemophilia A, Recombinant factor viii, bleed rate, 03 medical and health sciences, Young Adult, 0302 clinical medicine, Internal medicine, medicine, Clinical endpoint, Humans, Clinical Haemophilia, Child, Genetics (clinical), rFVIIIFc, Aged, extended half‐life, Factor VIII, business.industry, Hematology, General Medicine, Original Articles, Bleed, Middle Aged, medicine.disease, Confidence interval, Immunoglobulin Fc Fragments, Regimen, Fc fusion, Treatment Outcome, individualized prophylaxis, Child, Preschool, Severe haemophilia A, Original Article, Female, business, perioperative haemostasis, 030215 immunology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::bd4022ccca7aa7b264ac7e5d898662bfTest
http://europepmc.org/articles/PMC7384031Test -
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المؤلفون: K. John Pasi, P. Batty
المصدر: Expert Review of Precision Medicine and Drug Development. 4:259-262
مصطلحات موضوعية: Pharmacology, congenital, hereditary, and neonatal diseases and abnormalities, medicine.medical_specialty, business.industry, Genetic enhancement, Haemophilia A, Haemophilia, medicine.disease, Gastroenterology, Coagulation, hemic and lymphatic diseases, Internal medicine, Drug Discovery, Genetics, medicine, Molecular Medicine, Haemophilia B, business, Factor IX, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::0dcccfbfcfd11cb978b0ca784b79d9f0Test
https://doi.org/10.1080/23808993.2019.1632704Test