-
1
المؤلفون: Coelho, Teresa, Waddington Cruz, Márcia, Chao, Chi-Chao, Parman, Yeşim, Wixner, Jonas, Weiler, Markus, Barroso, Fabio A., Dasgupta, Noel R., Jung, Shiangtung W., Schneider, Eugene, Viney, Nicholas J., Dyck, P. James B., Ando, Yukio, Gillmore, Julian D., Khella, Sami, Gertz, Morie A., Obici, Laura, Berk, John L.
المصدر: Neurology and Therapy. 12:267-287
مصطلحات موضوعية: Amyloid, ATTR, Cardiomyopathy, Eplontersen, Polyneuropathy, Transthyretin amyloidosis
وصف الملف: electronic
الوصول الحر: https://urn.kb.se/resolve?urn=urn:nbn:se:umu:diva-202005Test
https://doi.org/10.1007/s40120-022-00414-zTest
https://umu.diva-portal.org/smash/get/diva2:1722506/FULLTEXT02.pdfTest -
2دورية أكاديمية
المؤلفون: Coelho, Teresa, Ando, Yukio, Benson, Merrill D, Berk, John L, Waddington-Cruz, Márcia, Dyck, Peter J, Gillmore, Julian D, Khella, Sami L, Litchy, William J, Obici, Laura, Monteiro, Cecilia, Tai, Li-Jung, Viney, Nicholas J, Buchele, Gustavo, Brambatti, Michela, Jung, Shiangtung W, St. L. O’Dea, Louis, Tsimikas, Sotirios, Schneider, Eugene, Geary, Richard S, Monia, Brett P, Gertz, Morie
المصدر: Neurology and Therapy. 10(1)
مصطلحات موضوعية: Pharmacology and Pharmaceutical Sciences, Biomedical and Clinical Sciences, Rare Diseases, Clinical Trials and Supportive Activities, Neurosciences, Orphan Drug, Clinical Research, Peripheral Neuropathy, Neurodegenerative, Evaluation of treatments and therapeutic interventions, 6.1 Pharmaceuticals, AKCEA-TTR-L-rx, Antisense oligonucleotide, Clinical trial design, Hereditary transthyretin-mediated amyloid polyneuropathy, Phase 3 clinical trial, AKCEA-TTR-Lrx, Clinical sciences
وصف الملف: application/pdf
الوصول الحر: https://escholarship.org/uc/item/2q73t715Test
-
3دورية أكاديمية
المؤلفون: Viney, Nicholas J, Guo, Shuling, Tai, Li‐Jung, Baker, Brenda F, Aghajan, Mariam, Jung, Shiangtung W, Yu, Rosie Z, Booten, Sheri, Murray, Heather, Machemer, Todd, Burel, Sebastien, Murray, Sue, Buchele, Gustavo, Tsimikas, Sotirios, Schneider, Eugene, Geary, Richard S, Benson, Merrill D, Monia, Brett P
المصدر: ESC Heart Failure. 8(1)
مصطلحات موضوعية: Pharmacology and Pharmaceutical Sciences, Biomedical and Clinical Sciences, Clinical Sciences, Cancer, Clinical Trials and Supportive Activities, Clinical Research, Liver Disease, Rare Diseases, Biotechnology, Orphan Drug, Digestive Diseases, Evaluation of treatments and therapeutic interventions, 6.1 Pharmaceuticals, Amyloid Neuropathies, Familial, Animals, Ligands, Mice, Oligonucleotides, Antisense, Prealbumin, Transthyretin, Amyloidosis, Cardiomyopathy, Polyneuropathy, Antisense, Ligand-conjugated, Cardiorespiratory Medicine and Haematology, Cardiovascular medicine and haematology
وصف الملف: application/pdf
الوصول الحر: https://escholarship.org/uc/item/41n576q7Test
-
4دورية أكاديمية
المؤلفون: Coelho, Teresa, Marques, Wilson, Dasgupta, Noel R, Chao, Chi-Chao, Parman, Yesim, França, Marcondes Cavalcante, Guo, Yuh-Cherng, Wixner, Jonas, Ro, Long-Sun, Calandra, Cristian R, Kowacs, Pedro A, Berk, John L, Obici, Laura, Barroso, Fabio A, Weiler, Markus, Conceição, Isabel, Jung, Shiangtung W, Buchele, Gustavo, Brambatti, Michela, Chen, Jersey, Hughes, Steven G, Schneider, Eugene, Viney, Nicholas J, Masri, Ahmad, Gertz, Morie R, Ando, Yukio, Gillmore, Julian D, Khella, Sami, Dyck, P James B, Waddington Cruz, Márcia, NEURO-TTRansform Investigators
المصدر: JAMA: Journal of the American Medical Association , 330 (15) pp. 1448-1458. (2023)
مصطلحات موضوعية: Science & Technology, Life Sciences & Biomedicine, Medicine, General & Internal, General & Internal Medicine, DIFLUNISAL, TAFAMIDIS
وصف الملف: text
العلاقة: https://discovery.ucl.ac.uk/id/eprint/10186076/3/Gillmore_Coelho%202023%20JAMA.pdfTest; https://discovery.ucl.ac.uk/id/eprint/10186076/4/Gillmore_Coelho%202023%20JAMA%20Suppl%20Appendix%202.pdfTest; https://discovery.ucl.ac.uk/id/eprint/10186076Test/
-
5دورية أكاديمية
المؤلفون: Coelho, Teresa, Waddington Cruz, Márcia, Chao, Chi-Chao, Parman, Yeşim, Wixner, Jonas, Weiler, Markus, Barroso, Fabio A, Dasgupta, Noel R, Jung, Shiangtung W, Schneider, Eugene, Viney, Nicholas J, Dyck, P James B, Ando, Yukio, Gillmore, Julian D, Khella, Sami, Gertz, Morie A, Obici, Laura, Berk, John L
المصدر: Neurology and Therapy (2022) (In press).
مصطلحات موضوعية: ATTR, Amyloid, Cardiomyopathy, Eplontersen, Polyneuropathy, Transthyretin amyloidosis
وصف الملف: text
العلاقة: https://discovery.ucl.ac.uk/id/eprint/10162396/1/s40120-022-00414-z.pdfTest; https://discovery.ucl.ac.uk/id/eprint/10162396Test/
-
6دورية أكاديمية
المؤلفون: Walsh, Michael, Bethune, Claudette, Smyth, Andrew, Tyrwhitt, Jessica, Jung, Shiangtung W., Yu, Rosie Z., Wang, Yanfeng, Geary, Richard S., Weitz, Jeffrey, Bhanot, Sanjay
المصدر: Kidney International Reports ; volume 7, issue 2, page 200-209 ; ISSN 2468-0249
الإتاحة: https://doi.org/10.1016/j.ekir.2021.11.011Test
https://api.elsevier.com/content/article/PII:S2468024921015175?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S2468024921015175?httpAccept=text/plainTest -
7دورية أكاديمية
المؤلفون: Willmann, Stefan, Marostica, Eleonora, Snelder, Nelleke, Solms, Alexander, Jensen, Markus, Lobmeyer, Maximilian, Lensing, Anthonie W. A., Bethune, Claudette, Morgan, Erin, Yu, Rosie Z., Wang, Yanfeng, Jung, Shiangtung W., Geary, Richard, Bhanot, Sanjay
المصدر: CPT: Pharmacometrics & Systems Pharmacology ; volume 10, issue 8, page 890-901 ; ISSN 2163-8306 2163-8306
-
8دورية أكاديمية
المؤلفون: Dyck, P. James B., Coelho, Teresa, Waddington Cruz, Marcia, Brannagan, Thomas H., Khella, Sami, Karam, Chafic, Berk, John L., Polydefkis, Michael J., Kincaid, John C., Wiesman, Janice F., Litchy, William J., Mauermann, Michelle L., Ackermann, Elizabeth J., Baker, Brenda F., Jung, Shiangtung W., Guthrie, Spencer, Pollock, Michael, Dyck, Peter J.
مصطلحات موضوعية: Neuropathy Symptoms and Change, amyloidosis, hATTR, inotersen, transthyretin
العلاقة: Dyck PJB, Coelho T, Waddington Cruz M, et al. Neuropathy symptom and change: Inotersen treatment of hereditary transthyretin amyloidosis. Muscle Nerve. 2020;62(4):509-515. doi:10.1002/mus.27023; http://hdl.handle.net/10400.16/2682Test
-
9دورية أكاديمية
المؤلفون: Viney, Nicholas J., Guo, Shuling, Tai, Li‐Jung, Baker, Brenda F., Aghajan, Mariam, Jung, Shiangtung W., Yu, Rosie Z., Booten, Sheri, Murray, Heather, Machemer, Todd, Burel, Sebastien, Murray, Sue, Buchele, Gustavo, Tsimikas, Sotirios, Schneider, Eugene, Geary, Richard S., Benson, Merrill D., Monia, Brett P.
المصدر: ESC Heart Failure ; volume 8, issue 1, page 652-661 ; ISSN 2055-5822 2055-5822
-
10دورية أكاديمية
المؤلفون: Dyck, P. James B., Kincaid, John C., Wiesman, Janice F., Polydefkis, Michael, Litchy, William J., Mauermann, Michelle L., Ackermann, Elizabeth J., Guthrie, Spencer, Pollock, Michael, Jung, Shiangtung W., Baker, Brenda F., Dyck, Peter J.
المصدر: Muscle & Nerve ; volume 62, issue 4, page 502-508 ; ISSN 0148-639X 1097-4598