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1دورية أكاديمية
المؤلفون: Scala, Serena, Ferrua, Francesca, Basso-Ricci, Luca, Dionisio, Francesca, Omrani, Maryam, Quaranta, Pamela, Jofra Hernandez, Raisa, Del Core, Luca, Benedicenti, Fabrizio, Monti, Ilaria, Giannelli, Stefania, Fraschetta, Federico, Darin, Silvia, Albertazzi, Elena, Galimberti, Stefania, Montini, Eugenio, Calabria, Andrea, Cicalese, Maria Pia, Aiuti, Alessandro
المساهمون: Scala, S, Ferrua, F, Basso-Ricci, L, Dionisio, F, Omrani, M, Quaranta, P, Jofra Hernandez, R, Del Core, L, Benedicenti, F, Monti, I, Giannelli, S, Fraschetta, F, Darin, S, Albertazzi, E, Galimberti, S, Montini, E, Calabria, A, Cicalese, M, Aiuti, A
مصطلحات موضوعية: gene therapy
وصف الملف: ELETTRONICO
العلاقة: info:eu-repo/semantics/altIdentifier/pmid/37244942; info:eu-repo/semantics/altIdentifier/wos/WOS:000996589500016; volume:14; issue:1; journal:NATURE COMMUNICATIONS; https://hdl.handle.net/10281/419198Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85160243442
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2دورية أكاديمية
المؤلفون: Quaranta, Pamela, Basso-Ricci, Luca, Jofra Hernandez, Raisa, Maria Naldini, Matteo, Barcella, Matteo, Pacini, Guido, Pietrasanta, Carlo, Pugni, Lorenza, Pais, Giulia, Benedicenti, Fabrizio, Giannelli, Stefania, Monti, Ilaria, Darin, Silvia, Barera, Graziano, Tucci, Francesca, Ferrua, Francesca, Calbi, Valeria, Gentner, Bernhard, DI Micco, Raffaella, Montini, Eugenio, Calabria, Andrea, Merelli, Ivan, Mosca, Fabio, Ester Bernardo, Maria, Pia Cicalese, Maria, Aiuti, Alessandro, Serena, Scala
المصدر: HemaSphere ; volume 7, issue S3, page e78878d6 ; ISSN 2572-9241
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3دورية أكاديميةMesenchymal stromal cells improve the transplantation outcome of CRISPR-Cas9 gene-edited human HSPCs
المؤلفون: Crippa, Stefania, Conti, Anastasia, Vavassori, Valentina, Ferrari, Samuele, Beretta, Stefano, Rivis, Silvia, Bosotti, Roberto, Scala, Serena, Pirroni, Stefania, Jofra-Hernandez, Raisa, Santi, Ludovica, Basso-Ricci, Luca, Merelli, Ivan, Genovese, Pietro, Aiuti, Alessandro, Naldini, Luigi, Di Micco, Raffaella, Bernardo, Maria Ester
المساهمون: Lady Tata Memorial Trust, Fondation Louis-Jeantet, Fondazione Telethon
المصدر: Molecular Therapy ; volume 31, issue 1, page 230-248 ; ISSN 1525-0016
مصطلحات موضوعية: Drug Discovery, Pharmacology, Genetics, Molecular Biology, Molecular Medicine
الإتاحة: https://doi.org/10.1016/j.ymthe.2022.08.011Test
https://api.elsevier.com/content/article/PII:S1525001622004993?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S1525001622004993?httpAccept=text/plainTest -
4دوريةCirculating hematopoietic stem/progenitor cell subsets contribute to human hematopoietic homeostasis
المؤلفون: Quaranta, Pamela, Basso-Ricci, Luca, Jofra Hernandez, Raisa, Pacini, Guido, Naldini, Matteo Maria, Barcella, Matteo, Seffin, Luca, Pais, Giulia, Spinozzi, Giulio, Benedicenti, Fabrizio, Pietrasanta, Carlo, Cheong, Jin Gyu, Ronchi, Andrea, Pugni, Lorenza, Dionisio, Francesca, Monti, Ilaria, Giannelli, Stefania, Darin, Silvia, Fraschetta, Federico, Barera, Graziano, Ferrua, Francesca, Calbi, Valeria, Ometti, Marco, Di Micco, Raffaella, Mosca, Fabio, Josefowicz, Steven Zvi, Montini, Eugenio, Calabria, Andrea, Bernardo, Maria Ester, Cicalese, Maria Pia, Gentner, Bernhard, Merelli, Ivan, Aiuti, Alessandro, Scala, Serena
المصدر: Blood; May 2024, Vol. 143 Issue: 19 p1937-1952, 16p
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5دورية أكاديميةMesenchymal stromal cells improve the transplantation outcome of CRISPR-Cas9 gene-edited human HSPCs
المؤلفون: Crippa, Stefania, Conti, Anastasia, Vavassori, Valentina, Ferrari, Samuele, Beretta, Stefano, Rivis, Silvia, Bosotti, Roberto, Scala, Serena, Pirroni, Stefania, Jofra-Hernandez, Raisa, Santi, Ludovica, Basso-Ricci, Luca, Merelli, Ivan, Genovese, Pietro, Aiuti, Alessandro, Naldini, Luigi, Di Micco, Raffaella, Bernardo, Maria Ester
المصدر: Molecular Therapy ; volume 30, issue 10, page 3333 ; ISSN 1525-0016
مصطلحات موضوعية: Drug Discovery, Pharmacology, Genetics, Molecular Biology, Molecular Medicine
الإتاحة: https://doi.org/10.1016/j.ymthe.2022.09.005Test
https://api.elsevier.com/content/article/PII:S1525001622005597?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S1525001622005597?httpAccept=text/plainTest -
6دورية أكاديمية
المؤلفون: Zoccolillo Matteo, Brigida Immacolata, Barzaghi Federica, Scala Serena, Jofra Hernandez Raisa, Basso-Ricci Luca, Colantuoni Mariasilvia, Pettinato Emanuela, Sergi Sergi Lucia, Milardi Giulia, Capasso Paola, Lombardo Angelo, Gregori Silvia, Sanvito Francesca, Schena Francesca, Cesaro Simone, Conti Francesca, Pession Andrea, Benedetti Fabio, Gattorno Marco, Lee Pui Y, Naldini Luigi, Cicalese Maria Pia, Aiuti Alessandro, Mortellaro Alessandra
مصطلحات موضوعية: adenosine deaminase 2, gene therapy, lentiviral vectors, macrophages, inflammation
العلاقة: info:eu-repo/grantAgreement/EC/H2020/841780/; https://zenodo.org/record/5513518Test; https://doi.org/10.1182/bloodadvances.2020003811Test; oai:zenodo.org:5513518
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7دورية أكاديمية
المؤلفون: Jofra Hernández, Raisa, Calabria, Andrea, Sanvito, Francesca, De Mattia, Fabiola, Farinelli, Giada, Scala, Serena, Visigalli, Ilaria, Carriglio, Nicola, De Simone, Maura, Vezzoli, Michela, Cecere, Francesca, Migliavacca, Maddalena, Basso-Ricci, Luca, Omrani, Maryam, Benedicenti, Fabrizio, Norata, Rossana, Rancoita, Paola Maria Vittoria, Di Serio, Clelia, Albertini, Paola, Cristofori, Patrizia, Naldini, Luigi, Gentner, Bernhard, Montini, Eugenio, Aiuti, Alessandro, Mortellaro, Alessandra
المساهمون: European Commission, Fondazione Telethon, Italian Ministry of Health
المصدر: Molecular Therapy ; volume 29, issue 1, page 86-102 ; ISSN 1525-0016
مصطلحات موضوعية: Drug Discovery, Pharmacology, Genetics, Molecular Biology, Molecular Medicine
الإتاحة: https://doi.org/10.1016/j.ymthe.2020.09.030Test
https://api.elsevier.com/content/article/PII:S1525001620304871?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S1525001620304871?httpAccept=text/plainTest -
8دورية أكاديمية
المؤلفون: Colantuoni, Mariasilvia, Jofra Hernandez, Raisa, Pettinato, Emanuela, Basso-Ricci, Luca, Magnani, Laura, Andolfi, Grazia, Rigamonti, Chiara, Finardi, Annamaria, Romeo, Valentina, Soldi, Monica, Sergi Sergi, Lucia, Rocchi, Martina, Scala, Serena, Hoffman, Hal M., Gregori, Silvia, Kajaste-Rudnitski, Anna, Sanvito, Francesca, Muzio, Luca, Naldini, Luigi, Aiuti, Alessandro, Mortellaro, Alessandra
المصدر: Science Translational Medicine ; volume 15, issue 698 ; ISSN 1946-6234 1946-6242
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9دورية أكاديمية
المؤلفون: Chanut, Franck J. A., Sanvito, Francesca, Ferrari, Giuliana, Visigalli, Ilaria, Carriglio, Nicola, Jofra Hernandez, Raisa, Norata, Rossana, Doglioni, Claudio, Naldini, Luigi, Cristofori, Patrizia
المساهمون: Chanut, Franck J. A., Sanvito, Francesca, Ferrari, Giuliana, Visigalli, Ilaria, Carriglio, Nicola, Jofra Hernandez, Raisa, Norata, Rossana, Doglioni, Claudio, Naldini, Luigi, Cristofori, Patrizia
العلاقة: info:eu-repo/semantics/altIdentifier/wos/WOS:000581176300001; journal:HUMAN GENE THERAPY; http://hdl.handle.net/20.500.11768/107448Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85099739931
الإتاحة: https://doi.org/20.500.11768/107448Test
https://doi.org/10.1089/hum.2020.135Test
https://hdl.handle.net/20.500.11768/107448Test -
10دورية أكاديمية
المؤلفون: Farinelli, Giada, Jofra Hernandez, Raisa, Rossi, Alice, Ranucci, Serena, Sanvito, Francesca, Migliavacca, Maddalena, Brombin, Chiara, Pramov, Aleksandar, Di Serio, Clelia, Bovolenta, Chiara, Gentner, Bernhard, Bragonzi, Alessandra, Aiuti, Alessandro
المصدر: Molecular Therapy ; volume 24, issue 10, page 1873-1880 ; ISSN 1525-0016
مصطلحات موضوعية: Drug Discovery, Pharmacology, Genetics, Molecular Biology, Molecular Medicine
الإتاحة: https://doi.org/10.1038/mt.2016.150Test
https://api.elsevier.com/content/article/PII:S1525001616454146?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S1525001616454146?httpAccept=text/plainTest