المؤلفون: Schiffmann, R, Goker-Alpan, O, Holida, M, Giraldo, P, Barisoni, L, Colvin, RB, Jennette, CJ, Maegawa, G, Boyadjiev, SA, Gonzalez, D, Nicholls, K, Tuffaha, A, Atta, MG, Rup, B, Charney, MR, Paz, A, Szlaifer, M, Alon, S, Brill-Almon, E, Chertkoff, R, Hughes, D

المصدر: Journal of Inherited Metabolic Disease , 42 (3) pp. 534-544. (2019)

مصطلحات موضوعية: antidrug antibodies, enzyme replacement therapy, Fabry disease, immunogenicity, pegunigalsidase alfa, pharmacokinetics

وصف الملف: text

العلاقة: https://discovery.ucl.ac.uk/id/eprint/10072975/1/Schiffmann_et_al-2019-Journal_of_Inherited_Metabolic_Disease.pdfTest; https://discovery.ucl.ac.uk/id/eprint/10072975Test/

الإتاحة: https://discovery.ucl.ac.uk/id/eprint/10072975/1/Schiffmann_et_al-2019-Journal_of_Inherited_Metabolic_Disease.pdfTest
https://discovery.ucl.ac.uk/id/eprint/10072975Test/

المؤلفون: Germain, DP, Giugliani, R, Hughes, DA, Mehta, A, Nicholls, K, Barisoni, L, Jennette, CJ, Bragat, A, Castelli, J, Sitaraman, S, Lockhart, DJ, Boudes, PF

العلاقة: pii: 1750-1172-7-91; Germain, D. P., Giugliani, R., Hughes, D. A., Mehta, A., Nicholls, K., Barisoni, L., Jennette, C. J., Bragat, A., Castelli, J., Sitaraman, S., Lockhart, D. J. & Boudes, P. F. (2012). Safety and pharmacodynamic effects of a pharmacological chaperone on alpha-galactosidase A activity and globotriaosylceramide clearance in Fabry disease: report from two phase 2 clinical studies. ORPHANET JOURNAL OF RARE DISEASES, 7 (1), https://doi.org/10.1186/1750-1172-7-91Test.; http://hdl.handle.net/11343/261889Test

الإتاحة: https://doi.org/10.1186/1750-1172-7-91Test
http://hdl.handle.net/11343/261889Test