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1دورية أكاديمية
المؤلفون: Karthik Lingineni, Varun Aggarwal, Juan Francisco Morales, Daniela J. Conrado, Diane Corey, Camille Vong, Jackson Burton, Jane Larkindale, Klaus Romero, Stephan Schmidt, Sarah Kim, the Cooperative International Neuromuscular Research Group investigators and Duchenne Regulatory Science Consortium members
المصدر: CPT: Pharmacometrics & Systems Pharmacology, Vol 11, Iss 3, Pp 318-332 (2022)
مصطلحات موضوعية: Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/2163-8306Test
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2دورية أكاديمية
المؤلفون: Ariana P. Mullin, Diane Corey, Emily C. Turner, Richard Liwski, Daniel Olson, Jackson Burton, Sudhir Sivakumaran, Lynn D. Hudson, Klaus Romero, Diane T. Stephenson, Jane Larkindale
المصدر: Clinical and Translational Science, Vol 14, Iss 1, Pp 214-221 (2021)
مصطلحات موضوعية: Therapeutics. Pharmacology, RM1-950, Public aspects of medicine, RA1-1270
وصف الملف: electronic resource
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3دورية أكاديمية
المؤلفون: Peter D. Creigh, Joan Mountain, Janet E. Sowden, Katy Eichinger, Bernard Ravina, Jane Larkindale, David N. Herrmann
المصدر: Annals of Clinical and Translational Neurology, Vol 6, Iss 9, Pp 1718-1727 (2019)
مصطلحات موضوعية: Neurosciences. Biological psychiatry. Neuropsychiatry, RC321-571, Neurology. Diseases of the nervous system, RC346-429
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/2328-9503Test
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4دورية أكاديمية
المؤلفون: Shelli Schomaker, David Potter, Roscoe Warner, Jane Larkindale, Nicholas King, Amy C Porter, Jane Owens, Lindsay Tomlinson, John-Michael Sauer, Kent Johnson, Jiri Aubrecht
المصدر: PLoS ONE, Vol 15, Iss 5, p e0229753 (2020)
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/1932-6203Test
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5دورية أكاديمية
المؤلفون: Susan Stein, Elizabeth Bogard, Nicole Boice, Vivian Fernandez, Tessa Field, Alan Gilstrap, Susan R. Kahn, Jane Larkindale, Toni Mathieson
المصدر: Orphanet Journal of Rare Diseases, Vol 13, Iss 1, Pp 1-10 (2018)
مصطلحات موضوعية: Best practices, Biopharmaceutical, Guidelines, Partnership, Patient advocacy, Rare disease, Medicine
وصف الملف: electronic resource
العلاقة: http://link.springer.com/article/10.1186/s13023-018-0761-2Test; https://doaj.org/toc/1750-1172Test
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6
المؤلفون: Jamison Seabury, Danae Alexandrou, Nuran Dilek, Brittany Cohen, John Heatwole, Jane Larkindale, David R. Lynch, Courtney Park, Spencer Rosero, Sub H. Subramony, Anika Varma, Ellen Wagner, Susan Walther, Jennifer Weinstein, McKenzie Wells, Christine Zizzi, Chad Heatwole
المصدر: Neurology
مصطلحات موضوعية: Neurology (clinical), Research Article
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::a0df1e01df7c43883e5c21de29decc1bTest
https://doi.org/10.1212/wnl.0000000000201598Test -
7تقرير
المؤلفون: Christina Olsen, Ritchie Head, Jane Knerova, Jane Larkindale, Susan Ward, Pietro Spitali, Hermien Kan
مصطلحات موضوعية: Duchenne muscular dystrophy, Vamorolone, Biomarkers
العلاقة: info:eu-repo/grantAgreement/EC/H2020/667078/; https://zenodo.org/communities/vision-dmd-h2020Test; https://zenodo.org/record/5668693Test; https://doi.org/10.5281/zenodo.5668693Test; oai:zenodo.org:5668693
الإتاحة: https://doi.org/10.5281/zenodo.5668693Test
https://doi.org/10.5281/zenodo.5668575Test
https://zenodo.org/record/5668693Test -
8
المؤلفون: Michelle Mellion, Jane Larkindale, Pallavi Lonkar, Jaya Goyal, Ashling Holland, Jeff Foy, Brijesh Garg, Shaoxia Yu, Anthony Frank, Chris Abbott, Niels Svenstrup, Jennifer Cormier, Sarah Vacca, James McArthur
المصدر: Sunday, April 23.
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::bd55720e8f0f2865337861f448edf214Test
https://doi.org/10.1212/wnl.0000000000203955Test -
9
المؤلفون: Michelle Mellion, Jane Larkindale, Jennifer Cormier, Holly Hand, Sarah Vacca, Pallavi Lonkar, Ashling Holland, Brijesh Garg, Jeff Foy, James McArthur
المصدر: Monday, April 24.
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::e4d8d1522af8af426f80c27a65b1c9e0Test
https://doi.org/10.1212/wnl.0000000000203993Test -
10
المؤلفون: Ashling Holland, Arnaud Klein, Caroline Godfrey, Niels Svenstrup, Jane Larkindale, Sonia Bracegirdle, Denis Furling, Jaya Goyal
المصدر: Thursday, April 27.
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::579875c2f7f6ba169307bc14b82718baTest
https://doi.org/10.1212/wnl.0000000000203804Test