S852 IN VIVO SELECTION FOR CORRECTED BETA-GLOBIN ALLELES AFTER CRISPR/CAS9 EDITING IN HUMAN SICKLE HEMATOPOIETIC STEM CELLS ENHANCES THERAPEUTIC POTENTIAL
التفاصيل البيبلوغرافية
العنوان:
S852 IN VIVO SELECTION FOR CORRECTED BETA-GLOBIN ALLELES AFTER CRISPR/CAS9 EDITING IN HUMAN SICKLE HEMATOPOIETIC STEM CELLS ENHANCES THERAPEUTIC POTENTIAL