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1دورية أكاديمية
المؤلفون: Sala D., Ornaghi F., Morena F., Argentati C., Valsecchi M., Alberizzi V., Di Guardo R., Bolino A., Aureli M., Martino S., Gritti A.
المساهمون: Sala, D., Ornaghi, F., Morena, F., Argentati, C., Valsecchi, M., Alberizzi, V., Di Guardo, R., Bolino, A., Aureli, M., Martino, S., Gritti, A.
مصطلحات موضوعية: Hex activity, cell therapy, CNS, gene therapy, GM2 gangliosidosis, hexosaminidase, lentiviral vectors, lysosomal storage disorders, Sandhoff disease
وصف الملف: STAMPA
العلاقة: info:eu-repo/semantics/altIdentifier/pmid/35434178; info:eu-repo/semantics/altIdentifier/wos/WOS:000787801500001; volume:25; firstpage:170; lastpage:189; numberofpages:20; journal:MOLECULAR THERAPY. METHODS & CLINICAL DEVELOPMENT; https://hdl.handle.net/11391/1516214Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85127260545
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المؤلفون: Davide Sala, Francesca Ornaghi, Francesco Morena, Chiara Argentati, Manuela Valsecchi, Valeria Alberizzi, Roberta Di Guardo, Alessandra Bolino, Massimo Aureli, Sabata Martino, Angela Gritti
مصطلحات موضوعية: CNS, GM2 gangliosidosis, Sandhoff disease, bone marrow transplantation, cell therapy, gene therapy, hexosaminidase, lentiviral vectors, lysosomal storage disorders, Settore BIO/10 - Biochimica, Genetics, Hex activity, Molecular Medicine, Molecular Biology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::b36b1605c05632177871f88568ac7db9Test
https://hdl.handle.net/11391/1516214Test -
3دورية أكاديمية
المساهمون: The Pennsylvania State University CiteSeerX Archives
مصطلحات موضوعية: hexosaminidase, HEX activity, cholesteatoma, normal retroauricular skin
وصف الملف: application/pdf