المؤلفون: Crow, Rebecca A., Hart, Kimberly A., McDermott, Michael P., Tawil, Rabi, Martens, William B., Herr, Barbara E., McColl, Elaine, Wilkinson, Jennifer, Kirschner, Janbernd, King, Wendy M., Eagle, Michele, Brown, Mary W., Hirtz, Deborah, Lochmuller, Hanns, Straub, Volker, Ciafaloni, Emma, Shieh, Perry B., Spinty, Stefan, Childs, Anne-Marie, Manzur, Adnan Y., Morandi, Lucia, Butterfield, Russell J., Horrocks, Iain, Roper, Helen, Flanigan, Kevin M., Kuntz, Nancy L., Mah, Jean K., Morrison, Leslie, Darras, Basil T., von der Hagen, Maja, Schara, Ulrike, Wilichowski, Ekkehard, Mongini, Tiziana, McDonald, Craig M., Vita, Giuseppe, Barohn, Richard J., Finkel, Richard S., Wicklund, Matthew, McMillan, Hugh J., Hughes, Imelda, Pegoraro, Elena, Bryan Burnette, W., Howard, James F., Thangarajh, Mathula, Campbell, Craig, Griggs, Robert C., Bushby, Kate, Guglieri, Michela

المساهمون: Crow, Rebecca A., Hart, Kimberly A., Mcdermott, Michael P., Tawil, Rabi, Martens, William B., Herr, Barbara E., Mccoll, Elaine, Wilkinson, Jennifer, Kirschner, Janbernd, King, Wendy M., Eagle, Michele, Brown, Mary W., Hirtz, Deborah, Lochmuller, Hann, Straub, Volker, Ciafaloni, Emma, Shieh, Perry B., Spinty, Stefan, Childs, Anne-Marie, Manzur, Adnan Y., Morandi, Lucia, Butterfield, Russell J., Horrocks, Iain, Roper, Helen, Flanigan, Kevin M., Kuntz, Nancy L., Mah, Jean K., Morrison, Leslie, Darras, Basil T., von der Hagen, Maja, Schara, Ulrike, Wilichowski, Ekkehard, Mongini, Tiziana, Mcdonald, Craig M., Vita, Giuseppe, Barohn, Richard J., Finkel, Richard S., Wicklund, Matthew, Mcmillan, Hugh J., Hughes, Imelda, Pegoraro, Elena, Bryan Burnette, W., Howard, James F., Thangarajh, Mathula, Campbell, Craig, Griggs, Robert C., Bushby, Kate, Guglieri, Michela

مصطلحات موضوعية: Academic-led clinical trial, Clinical trial, Clinical trial regulation, Duchenne muscular dystrophy, Rare disease, Budget, Clinical Trials as Topic, Contract, Human, International Cooperation, Multicenter Studies as Topic, Muscular Dystrophy, Duchenne, Patient Selection, Research Support as Topic, Steroid, Time Factor, Treatment Outcome, Checklist, Research Design, Medicine (miscellaneous), Pharmacology (medical)

وصف الملف: ELETTRONICO

العلاقة: info:eu-repo/semantics/altIdentifier/pmid/29793540; volume:19; issue:1; firstpage:291; numberofpages:9; journal:TRIALS; http://hdl.handle.net/11577/3294935Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85047553551; http://www.trialsjournal.com/homeTest/

الإتاحة: https://doi.org/10.1186/s13063-018-2645-0Test
http://hdl.handle.net/11577/3294935Test
http://www.trialsjournal.com/homeTest/

المؤلفون: Guglieri, Michela, Bushby, Kate, McDermott, Michael P, Hart, Kimberly A, Tawil, Rabi, Martens, William B, Herr, Barbara E, McColl, Elaine, Speed, Chris, Wilkinson, Jennifer, Kirschner, Janbernd, King, Wendy M, Eagle, Michelle, Brown, Mary W, Willis, Tracey, Griggs, Robert C, Straub, Volker, van Ruiten, Henriette, Childs, Anne-Marie, Ciafaloni, Emma, Shieh, Perry B, Spinty, Stefan, Maggi, Lorenzo, Baranello, Giovanni, Butterfield, Russell J, Horrocks, I A, Roper, Helen, Alhaswani, Zoya, Flanigan, Kevin M, Kuntz, Nancy L, Manzur, Adnan, Darras, Basil T, Kang, Peter B, Morrison, Leslie, Krzesniak-Swinarska, Monika, Mah, Jean K, Mongini, Tiziana E, Ricci, Federica, von der Hagen, Maja, Finkel, Richard S, O'Reardon, Kathleen, Wicklund, Matthew, Kumar, Ashutosh, McDonald, Craig M, Han, Jay J, Joyce, Nanette, Henricson, Erik K, Schara-Schmidt, Ulrike, Gangfuss, Andrea, Wilichowski, Ekkehard, Barohn, Richard J, Statland, Jeffrey M, Campbell, Craig, Vita, Giuseppe, Vita, Gian Luca, Howard, James F, Hughes, Imelda, McMillan, Hugh J, Pegoraro, Elena, Bello, Luca, Burnette, W Bryan, Thangarajh, Mathula, Chang, Taeun

المساهمون: Guglieri, Michela, Bushby, Kate, Mcdermott, Michael P, Hart, Kimberly A, Tawil, Rabi, Martens, William B, Herr, Barbara E, Mccoll, Elaine, Speed, Chri, Wilkinson, Jennifer, Kirschner, Janbernd, King, Wendy M, Eagle, Michelle, Brown, Mary W, Willis, Tracey, Griggs, Robert C, Straub, Volker, van Ruiten, Henriette, Childs, Anne-Marie, Ciafaloni, Emma, Shieh, Perry B, Spinty, Stefan, Maggi, Lorenzo, Baranello, Giovanni, Butterfield, Russell J, Horrocks, I A, Roper, Helen, Alhaswani, Zoya, Flanigan, Kevin M, Kuntz, Nancy L, Manzur, Adnan, Darras, Basil T, Kang, Peter B, Morrison, Leslie, Krzesniak-Swinarska, Monika, Mah, Jean K, Mongini, Tiziana E, Ricci, Federica, von der Hagen, Maja, Finkel, Richard S, O'Reardon, Kathleen, Wicklund, Matthew, Kumar, Ashutosh, Mcdonald, Craig M, Han, Jay J, Joyce, Nanette, Henricson, Erik K, Schara-Schmidt, Ulrike, Gangfuss, Andrea, Wilichowski, Ekkehard, Barohn, Richard J, Statland, Jeffrey M, Campbell, Craig, Vita, Giuseppe, Vita, Gian Luca, Howard, James F, Hughes, Imelda, Mcmillan, Hugh J, Pegoraro, Elena, Bello, Luca, Burnette, W Bryan, Thangarajh, Mathula, Chang, Taeun

مصطلحات موضوعية: Child, Preschool, Female, Human, Male, Pregnenedione, Glucocorticoid, Muscular Dystrophy, Duchenne, Prednisone

وصف الملف: STAMPA

العلاقة: info:eu-repo/semantics/altIdentifier/pmid/35381069; info:eu-repo/semantics/altIdentifier/wos/WOS:000779463300001; volume:327; issue:15; firstpage:1456; lastpage:1468; numberofpages:13; journal:JAMA; http://hdl.handle.net/11577/3443654Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85128799842

الإتاحة: https://doi.org/10.1001/jama.2022.4315Test
http://hdl.handle.net/11577/3443654Test

المؤلفون: Crow, Rebecca A, Hart, Kimberly A, McDermott, Michael P, Tawil, Rabi, Martens, William B, Herr, Barbara E, McColl, Elaine, Wilkinson, Jennifer, Kirschner, Janbernd, King, Wendy M, Eagle, Michele, Brown, Mary W, Hirtz, Deborah, Lochmuller, Hanns, Straub, Volker, Ciafaloni, Emma, Shieh, Perry B, Spinty, Stefan, Childs, Anne-Marie, Manzur, Adnan Y, Morandi, Lucia, Butterfield, Russell J, Horrocks, Iain, Roper, Helen, Flanigan, Kevin M, Kuntz, Nancy L, Mah, Jean K, Morrison, Leslie, Darras, Basil T, von der Hagen, Maja, Schara, Ulrike, Wilichowski, Ekkehard, Mongini, Tiziana, McDonald, Craig M, Vita, Giuseppe, Barohn, Richard J, Finkel, Richard S, Wicklund, Matthew, McMillan, Hugh J, Hughes, Imelda, Pegoraro, Elena, Bryan Burnette, W, Howard, James F, Thangarajh, Mathula, Campbell, Craig, Griggs, Robert C, Bushby, Kate, Guglieri, Michela

مصطلحات موضوعية: WE Musculoskeletal. Orthopaedics

وصف الملف: text

العلاقة: http://www.repository.uhblibrary.co.uk/id/eprint/1669/1/A%20checklist%20for%20clinical%20trials%20in%20rare%20disease.pdfTest; Crow, Rebecca A, Hart, Kimberly A, McDermott, Michael P, Tawil, Rabi, Martens, William B, Herr, Barbara E, McColl, Elaine, Wilkinson, Jennifer, Kirschner, Janbernd, King, Wendy M, Eagle, Michele, Brown, Mary W, Hirtz, Deborah, Lochmuller, Hanns, Straub, Volker, Ciafaloni, Emma, Shieh, Perry B, Spinty, Stefan, Childs, Anne-Marie, Manzur, Adnan Y, Morandi, Lucia, Butterfield, Russell J, Horrocks, Iain, Roper, Helen, Flanigan, Kevin M, Kuntz, Nancy L, Mah, Jean K, Morrison, Leslie, Darras, Basil T, von der Hagen, Maja, Schara, Ulrike, Wilichowski, Ekkehard, Mongini, Tiziana, McDonald, Craig M, Vita, Giuseppe, Barohn, Richard J, Finkel, Richard S, Wicklund, Matthew, McMillan, Hugh J, Hughes, Imelda, Pegoraro, Elena, Bryan Burnette, W, Howard, James F, Thangarajh, Mathula, Campbell, Craig, Griggs, Robert C, Bushby, Kate and Guglieri, Michela (2018) A checklist for clinical trials in rare disease: obstacles and anticipatory actions-lessons learned from the FOR-DMD trial. Trials, 19 (1). p. 291. ISSN 1745-6215. This article is available to all UHB staff and students login using a UHB Athens Account. Register for Athens here - https://openathens.nice.org.ukTest/

الإتاحة: http://www.repository.uhblibrary.co.uk/id/eprint/1669Test/
https://trialsjournal.biomedcentral.com/articles?query=A+checklist+for+clinical+trials+in+rare+disease%3A+obstacles+and+anticipatory+actions-lessons+learned+from+the+FOR-DMD+trial.&searchType=journalSearch&tab=keywordTest
http://www.repository.uhblibrary.co.uk/id/eprint/1669/1/A%20checklist%20for%20clinical%20trials%20in%20rare%20disease.pdfTest

المؤلفون: Herr, Barbara E., Hart, Kimberly A., McDermott, Michael, Griggs, Robert C., Herbelin, Laura, Barohn, Richard

المصدر: Neurotherapeutics ; volume 5, issue 3, page 490 ; ISSN 1878-7479

مصطلحات موضوعية: Pharmacology (medical), Neurology (clinical), Pharmacology

الإتاحة: https://doi.org/10.1016/j.nurt.2008.03.003Test
https://api.elsevier.com/content/article/PII:S1878747923004750?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S1878747923004750?httpAccept=text/plainTest

المؤلفون: Venance, Shannon L., Herr, Barbara E., Griggs, Robert C.

المصدر: Neurotherapeutics ; volume 4, issue 2, page 199-204 ; ISSN 1878-7479

مصطلحات موضوعية: Pharmacology (medical), Neurology (clinical), Pharmacology

الإتاحة: https://doi.org/10.1016/j.nurt.2007.01.004Test
https://api.elsevier.com/content/article/PII:S187874792300658X?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S187874792300658X?httpAccept=text/plainTest

المؤلفون: Herr, Barbara E., Richesson, Rachel, Griggs, Robert C.

المصدر: Neurotherapeutics ; volume 4, issue 4, page 728 ; ISSN 1878-7479

مصطلحات موضوعية: Pharmacology (medical), Neurology (clinical), Pharmacology

الإتاحة: https://doi.org/10.1016/j.nurt.2007.03.015Test
https://api.elsevier.com/content/article/PII:S1878747923006013?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S1878747923006013?httpAccept=text/plainTest

المؤلفون: Guglieri, Michela, Bushby, Kate, Mcdermott, Michael P., Hart, Kimberly A., Tawil, Rabi, Martens, William B., Herr, Barbara E., Mccoll, Elaine, Wilkinson, Jennifer, Kirschner, Janbernd, King, Wendy M., Eagle, Michele, Brown, Mary W., Willis, Tracey, Hirtz, Deborah, Shieh, Perry B., Straub, Volker, Childs, Anne Marie, Ciafaloni, Emma, Butterfield, Russell J., Horrocks, Iain, Spinty, Stefan, Flanigan, Kevin M., Kuntz, Nancy L., Baranello, Giovanni, Roper, Helen, Morrison, Leslie, Mah, Jean K., Manzur, Adnan Y., Mcdonald, Craig M., Schara, Ulrike, von der Hagen, Maja, Barohn, Richard J., Campbell, Craig, Darras, Basil T., Finkel, Richard S., Vita, Giuseppe, Hughes, Imelda, Mongini, Tiziana, PEGORARO, ELENA, Wicklund, Matthew, Wilichowski, Ekkehard, Bryan Burnette, W., Howard, James F., Mcmillan, Hugh J., Thangarajh, Mathula, Griggs, Robert C.

المساهمون: Guglieri, Michela, Bushby, Kate, Mcdermott, Michael P., Hart, Kimberly A., Tawil, Rabi, Martens, William B., Herr, Barbara E., Mccoll, Elaine, Wilkinson, Jennifer, Kirschner, Janbernd, King, Wendy M., Eagle, Michele, Brown, Mary W., Willis, Tracey, Hirtz, Deborah, Shieh, Perry B., Straub, Volker, Childs, Anne Marie, Ciafaloni, Emma, Butterfield, Russell J., Horrocks, Iain, Spinty, Stefan, Flanigan, Kevin M., Kuntz, Nancy L., Baranello, Giovanni, Roper, Helen, Morrison, Leslie, Mah, Jean K., Manzur, Adnan Y., Mcdonald, Craig M., Schara, Ulrike, von der Hagen, Maja, Barohn, Richard J., Campbell, Craig, Darras, Basil T., Finkel, Richard S., Vita, Giuseppe, Hughes, Imelda, Mongini, Tiziana, Pegoraro, Elena, Wicklund, Matthew, Wilichowski, Ekkehard, Bryan Burnette, W., Howard, James F., Mcmillan, Hugh J., Thangarajh, Mathula, Griggs, Robert C.

مصطلحات موضوعية: Deflazacort, Duchenne muscular dystrophy, Prednisolone, Randomized, Standards of care, Medicine (all), Pharmacology (medical)

وصف الملف: STAMPA

العلاقة: info:eu-repo/semantics/altIdentifier/pmid/28450193; info:eu-repo/semantics/altIdentifier/wos/WOS:000403860000004; volume:58; firstpage:34; lastpage:39; numberofpages:6; journal:CONTEMPORARY CLINICAL TRIALS; http://hdl.handle.net/11577/3232624Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85018333312; http://www.elsevier.com/wps/find/journaldescription.cws_home/704636/description#descriptionTest

الإتاحة: https://doi.org/10.1016/j.cct.2017.04.008Test
http://hdl.handle.net/11577/3232624Test
http://www.elsevier.com/wps/find/journaldescription.cws_home/704636/description#descriptionTest

المؤلفون: Griggs, Robert C., Herr, Barbara E., Reha, Allen, Elfring, Gary, Atkinson, Leone, Cwik, Valerie, Mccoll, Elaine, Tawil, Rabi, Pandya, Shree, McDermott, Michael P., Bushby, Kate

المصدر: Muscle & Nerve ; volume 48, issue 1, page 27-31 ; ISSN 0148-639X 1097-4598

الإتاحة: https://doi.org/10.1002/mus.23831Test

المؤلفون: Herr, Barbara E., Pelusio, Rita M.

المصدر: Controlled Clinical Trials ; volume 18, issue 3, page S180 ; ISSN 0197-2456

مصطلحات موضوعية: Pharmacology

الإتاحة: https://doi.org/10.1016/s0197-2456Test(97)91208-3
https://api.elsevier.com/content/article/PII:S0197245697912083?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S0197245697912083?httpAccept=text/plainTest

المؤلفون: Griggs, Robert C., Jozefowicz, Ralph, Kingston, William, Nair, K. Sreekumaran, Herr, Barbara E., Halliday, David

المصدر: Annals of Neurology ; volume 27, issue 5, page 505-512 ; ISSN 0364-5134 1531-8249

الإتاحة: https://doi.org/10.1002/ana.410270509Test