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1دورية أكاديمية
المؤلفون: Yasmin Al‐Din, Carol Dryden, Gordon MacGregor, David Young, Cristina Coelho
المصدر: The Clinical Respiratory Journal, Vol 17, Iss 5, Pp 473-477 (2023)
مصطلحات موضوعية: cystic fibrosis, cystic fibrosis transmembrane conductance regulator, G551D mutation, ivacaftor, pulmonary, real world, Diseases of the respiratory system, RC705-779
وصف الملف: electronic resource
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2دورية أكاديمية
المؤلفون: Scott C. Bell, Jochen G. Mainz, Gordon MacGregor, Susan Madge, Julie Macey, Moshe Fridman, Ellison D. Suthoff, Siva Narayanan, Nils Kinnman
المصدر: BMC Pulmonary Medicine, Vol 19, Iss 1, Pp 1-9 (2019)
مصطلحات موضوعية: Patient-reported outcomes, Work productivity, Ivacaftor, Cystic fibrosis, G551D-CFTR, Diseases of the respiratory system, RC705-779
وصف الملف: electronic resource
العلاقة: http://link.springer.com/article/10.1186/s12890-019-0887-6Test; https://doaj.org/toc/1471-2466Test
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3دورية أكاديمية
المؤلفون: Silke van Koningsbruggen-Rietschel, Jane C. Davies, Tacjana Pressler, Rainald Fischer, Gordon MacGregor, Scott H. Donaldson, Knut Smerud, Nils Meland, Jann Mortensen, Marie Ø. Fosbøl, Damian G. Downey, Astrid H. Myrset, Hugo Flaten, Philip D. Rye, The following investigators and their teams (in alphabetical order) conducted this study., Mary Carroll, Jane Davies, Carsten Schwarz, Nico Derichs, Damian Downey, Olaf Eickmeier, Pal Leyell Finstad, Marie Øbro Fossbøl, Marita Gilljam, Lena Hjelte, Alan Knox, Susanne Nährig, Joachim Riethmüller, Felix C. Ringshausen, AS AlgiPharma, Laura Gow, Joy Conway, William Bennett
المصدر: ERJ Open Research, Vol 6, Iss 4 (2020)
مصطلحات موضوعية: Medicine
وصف الملف: electronic resource
العلاقة: http://openres.ersjournals.com/content/6/4/00132-2020.fullTest; https://doaj.org/toc/2312-0541Test
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4دورية أكاديمية
المؤلفون: Graham Devereux, Danielle Wrolstad, Stephen J Bourke, Cori L Daines, Simon Doe, Ryan Dougherty, Rose Franco, Alastair Innes, Benjamin T Kopp, Jorge Lascano, Daniel Layish, Gordon MacGregor, Lorna Murray, Daniel Peckham, Vincenzina Lucidi, Emma Lovie, Jennifer Robertson, Douglas J Fraser-Pitt, Deborah A O'Neil
المصدر: PLoS ONE, Vol 15, Iss 12, p e0242945 (2020)
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/1932-6203Test
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5دورية أكاديمية
المؤلفون: Hannah K Bayes, Stephen Bicknell, Gordon MacGregor, Tom J Evans
المصدر: PLoS ONE, Vol 9, Iss 2, p e90263 (2014)
وصف الملف: electronic resource
العلاقة: http://europepmc.org/articles/PMC3937364?pdf=renderTest; https://doaj.org/toc/1932-6203Test
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6
المؤلفون: Ahmet Z Uluer, Gordon MacGregor, Pilar Azevedo, Veronica Indihar, Claire Keating, Marcus A Mall, Edward F McKone, Bonnie W Ramsey, Steven M Rowe, Ronald C Rubenstein, Jennifer L Taylor-Cousar, Elizabeth Tullis, Lael M Yonker, Chenghao Chu, Anna P Lam, Nitin Nair, Patrick R Sosnay, Simon Tian, Fredrick Van Goor, Lakshmi Viswanathan, David Waltz, Linda T Wang, Yingmei Xi, Joanne Billings, Alexander Horsley, Edward F. Nash, Marleen Bakker, Renske van der Meer, Petrus Merkus, Christof Majoor, Karen McCoy, Krishna Pancham, James Tolle, Bryon Quick, Ahmet Uluer, Emily DiMango, Adupa Rao, Santiago Reyes, Ross Klingsberg, Celeste Barreto, Victor Ortega, Donna Willey-Courand, Carsten Schwarz, Sivagurunathan Sutharsan, Rainald Fischer, Jane Davies, Jamie Duckers, Simon Doe, Harry Heijerman, George M. Solomon, Christian Merlo, Jennifer Griffonnet, Joseph Pilewski, Jordan Dunitz, Saba Sheikh, Ronald C. Rubenstein, Daniel B. Rosenbluth, Theodore Liou, Maria Indihar, Lael Yonker, Samya Nasr, Cynthia D. Brown, Gregory S. Sawicki, Jennifer Ruddy, Bryan Garcia, Andrew Braun, Alex H. Gifford, Nighat Mehdi, Maria Tupayachi Ortiz, Raksha Jain, Francisco J. Calimano, Jimmy Johannes, Cori L. Daines, Jason Fullmer, Joel Mermis, Christopher Barrios, Ngoc Ly, Brian P. Casserly, Stephan Eisenmann, Helge Hebestreit, Alexander Kiefer, Daniel Peckham, Martin Ledson, Eva Van Braeckel, Noel Gerard McElvaney, Edward McKone, Barry Plant, Lucy Burr, Daniel J. Smith, Peter Middleton, John Wilson
المساهمون: VU University medical center
المصدر: The Lancet Respiratory Medicine, 11(6), 550-562. Elsevier Limited
VX18-121-101 & VX18-561-101 Study Groups 2023, ' Safety and efficacy of vanzacaftor–tezacaftor–deutivacaftor in adults with cystic fibrosis : randomised, double-blind, controlled, phase 2 trials ', The Lancet Respiratory Medicine, vol. 11, no. 6, pp. 550-562 . https://doi.org/10.1016/S2213-2600Test(22)00504-5
LANCET RESPIRATORY MEDICINEمصطلحات موضوعية: Pulmonary and Respiratory Medicine, Medicine and Health Sciences
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::72b19fd4ef9823a3f92122d18b15dec4Test
https://research.vumc.nl/en/publications/0a8b171c-28b7-4da9-8e4a-5749733cacf9Test -
7رسالة جامعية
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8
المؤلفون: David Cooper, William D Laidig, Alexandra Sappington, Gordon MacGregor
المصدر: Cureus.
مصطلحات موضوعية: General Engineering
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::5c41959b3f3121afd1301314c21aa029Test
https://doi.org/10.7759/cureus.35109Test -
9
المصدر: Journal of Cystic Fibrosis.
مصطلحات موضوعية: Pulmonary and Respiratory Medicine, Pediatrics, Perinatology and Child Health
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::619cf5f1d000a1c980ad8852d7f50d53Test
https://doi.org/10.1016/j.jcf.2023.02.004Test -
10
المؤلفون: Sivagurunathan Sutharsan, Edward F McKone, Damian G Downey, Jamie Duckers, Gordon MacGregor, Elizabeth Tullis, Eva Van Braeckel, Claire E Wainwright, Danie Watson, Neil Ahluwalia, Bote G Bruinsma, Christopher Harris, Anna P Lam, Yiyue Lou, Samuel M Moskowitz, Simon Tian, Jason Yuan, David Waltz, Marcus A Mall, Paul Aurora, Stijn Verhulst, Michael Lorenz, Jobst Roehmel, Wolfgang Gleiber, Susanne Naehrig, Florian Stehling, Silke van Koningsbruggen-Rietschel, Rainald Fischer, Damian Downey, Charles Haworth, Julian Legg, Peter Barry, Rebecca Thursfield, Simon James Doe, Tom Hilliard, Edward F Nash, Nicholas John Withers, Daniel Peckham, Helen Louise Barr, Timothy Lee, Robert Gray, Francois Vermeulen, Eef Vanderhelst, Philip J Robinson, Daniel J Smith, Siobhain A Mulrennan, Barry S Clements, Peter Wark
المساهمون: Aurora, Paul (Beitragende*r), Verhulst, Stijn (Beitragende*r), Lorenz, Michael (Beitragende*r), Roehmel, Jobst (Beitragende*r), Gleiber, Wolfgang (Beitragende*r), Naehrig, Susanne (Beitragende*r), Stehling, Florian (Beitragende*r), van Koningsbruggen-Rietschel, Silke (Beitragende*r), Fischer, Rainald (Beitragende*r), Haworth, Charles (Beitragende*r), Legg, Julian (Beitragende*r), Barry, Peter (Beitragende*r), Thursfield, Rebecca (Beitragende*r), Doe, Simon James (Beitragende*r), Hilliard, Tom (Beitragende*r), Nash, Edward F (Beitragende*r), Withers, Nicholas John (Beitragende*r), Peckham, Daniel (Beitragende*r), Barr, Helen Louise (Beitragende*r), Lee, Timothy (Beitragende*r), Gray, Robert (Beitragende*r), Vermeulen, Francois (Beitragende*r), Vanderhelst, Eef (Beitragende*r), Robinson, Philip J (Beitragende*r), Smith, Daniel J (Beitragende*r), Mulrennan, Siobhain A (Beitragende*r), Clements, Barry S (Beitragende*r), Wark, Peter (Beitragende*r), Physiotherapy, Human Physiology and Anatomy, Clinical sciences, Pneumology
المصدر: VX18-445-109 study group 2021, ' Efficacy and safety of elexacaftor plus tezacaftor plus ivacaftor versus tezacaftor plus ivacaftor in people with cystic fibrosis homozygous for F508del-CFTR: a 24-week, multicentre, randomised, double-blind, active-controlled, phase 3b trial ', The Lancet. Respiratory medicine . https://doi.org/10.1016/S2213-2600Test(21)00454-9
مصطلحات موضوعية: Pulmonary and Respiratory Medicine, Indoles, Pyrrolidines, F508del-CFTR allele, Cystic Fibrosis, aged 12 years or older, Pyridines, Medizin, Cystic Fibrosis Transmembrane Conductance Regulator, Quinolones, Aminophenols, Double-Blind Method, Mutation, Quality of Life, Humans, Pyrazoles, cystic fibrosis transmembrane conductance regulator (CFTR), Benzodioxoles, Child, Chloride Channel Agonists
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::75c34a7aa3d2d4d1a01b05a402f021fcTest
https://www.scopus.com/inward/record.url?partnerID=HzOxMe3b&origin=inward&scp=85124502293Test