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1دورية أكاديمية
المؤلفون: Chiesa, Robert, Georgiadis, Christos, Syed, Farhatullah, Zhan, Hong, Etuk, Annie, Gkazi, Soragia Athina, Preece, Roland, Ottaviano, Giorgio, Braybrook, Toni, Chu, Jan, Kubat, Agnieszka, Adams, Stuart, Thomas, Rebecca, Gilmour, Kimberly, O'Connor, David, Vora, Ajay, Qasim, Waseem, Base-Edited, CAR T Group
المصدر: New England Journal of Medicine , 389 pp. 899-910. (2023)
وصف الملف: text
العلاقة: https://discovery.ucl.ac.uk/id/eprint/10176251/3/Etuk_Base-Edited%20CAR7%20T%20Cells%20for%20Relapsed%20T-Cell%20Acute%20Lymphoblastic%20Leukemia_AOP.pdfTest; https://discovery.ucl.ac.uk/id/eprint/10176251Test/
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2دورية أكاديمية
المؤلفون: Naso, Gaetano, Gkazi, Soragia Athina, Georgiadis, Christos, Jayarajan, Vignesh, Jacków, Joanna, Fleck, Roland, Allison, Leanne, Ogunbiyi, Olumide Kayode, McGrath, John Alexander, Ilic, Dusko, Di, Wei-Li, Petrova, Anastasia, Qasim, Waseem
المصدر: JID Innovations ; volume 3, issue 3, page 100191 ; ISSN 2667-0267
مصطلحات موضوعية: General Engineering
الإتاحة: https://doi.org/10.1016/j.xjidi.2023.100191Test
https://api.elsevier.com/content/article/PII:S2667026723000139?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S2667026723000139?httpAccept=text/plainTest -
3دورية أكاديمية
المؤلفون: Gkazi, Soragia Athina, Gravett, Emma, Bautista, Carla, Bartram, Jack, Ghorashian, Sara, Adams, Stuart Paul
المصدر: International Journal of Molecular Sciences , 23 (14) , Article 7573. (2022)
مصطلحات موضوعية: ddPCR, tisagenlecleucel, 4-1BB CD19, copy number variant
وصف الملف: text
العلاقة: https://discovery.ucl.ac.uk/id/eprint/10179397/1/Clinically%20Applicable%20Assessment%20of%20Tisagenlecleucel%20CAR%20T%20Cell%20Treatment%20by%20Digital%20Droplet%20PCR%20for%20Copy%20Number%20Variant%20Ass.pdfTest; https://discovery.ucl.ac.uk/id/eprint/10179397Test/
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4دورية أكاديمية
المؤلفون: Ottaviano, Giorgio, Georgiadis, Christos, Gkazi, Soragia Athina, Syed, Farhatullah, Zhan, Hong, Etuk, Annie, Preece, Roland, Chu, Jan, Kubat, Agnieszka, Adams, Stuart, Veys, Paul, Vora, Ajay, Rao, Kanchan, Qasim, Waseem, TT52 CRISPR-CAR, group
المصدر: Science Translational Medicine , 14 (668) , Article eabq3010. (2022)
مصطلحات موضوعية: TT52 CRISPR-CAR group
وصف الملف: text
العلاقة: https://discovery.ucl.ac.uk/id/eprint/10159117/2/Ottaviano_Phase%201%20clinical%20trial%20of%20CRISPR-engineered%20CAR19%20universal%20T%20cells%20for%20treatment%20of%20children%20with%20refractory%20B%20cell%20leukemia_AAM.pdfTest; https://discovery.ucl.ac.uk/id/eprint/10159117Test/
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5دورية أكاديمية
المؤلفون: Georgiadis, Christos, Rasaiyaah, Jane, Gkazi, Soragia Athina, Preece, Roland, Etuk, Aniekan, Christi, Abraham, Qasim, Waseem
المساهمون: Wellcome Trust, CHILDREN with CANCER UK, Bloodwise, DH | National Institute for Health Research
المصدر: Leukemia ; volume 35, issue 12, page 3466-3481 ; ISSN 0887-6924 1476-5551
مصطلحات موضوعية: Oncology, Cancer Research, Hematology
الإتاحة: https://doi.org/10.1038/s41375-021-01282-6Test
https://www.nature.com/articles/s41375-021-01282-6.pdfTest
https://www.nature.com/articles/s41375-021-01282-6Test -
6دورية أكاديمية
المؤلفون: Preece, Roland, Pavesi, Andrea, Gkazi, Soragia Athina, Stegmann, Kerstin A., Georgiadis, Christos, Tan, Zhi Ming, Aw, Jia Ying Joey, Maini, Mala K., Bertoletti, Antonio, Qasim, Waseem
المساهمون: NIHR Blood and Transplant Research Units, Great Ormond Street Biomedical Research Centre, Wellcome Trust, National Research Foundation Singapore
المصدر: Molecular Therapy - Methods & Clinical Development ; volume 19, page 149-161 ; ISSN 2329-0501
مصطلحات موضوعية: Genetics, Molecular Biology, Molecular Medicine
الإتاحة: https://doi.org/10.1016/j.omtm.2020.09.002Test
https://api.elsevier.com/content/article/PII:S232905012030187X?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S232905012030187X?httpAccept=text/plainTest -
7دورية أكاديمية
المؤلفون: Gkazi, Soragia Athina, Troakes, Claire, Topp, Simon, Miller, Jack W., Vance, Caroline A., Sreedharan, Jemeen, Al-Chalabi, Ammar, Kirby, Janine, Shaw, Pamela J., Al-Sarraj, Safa, King, Andrew, Smith, Bradley N., Shaw, Christopher E.
المصدر: Gkazi , S A , Troakes , C , Topp , S , Miller , J W , Vance , C A , Sreedharan , J , Al-Chalabi , A , Kirby , J , Shaw , P J , Al-Sarraj , S , King , A , Smith , B N & Shaw , C E 2019 , ' Striking phenotypic variation in a family with the P506S UBQLN2 mutation including amyotrophic lateral sclerosis, spastic paraplegia and frontotemporal dementia ' , Neurobiology of Aging , vol. 73 , pp. 229.e5-229.e9 . https://doi.org/10.1016/j.neurobiolaging.2018.08.015Test
مصطلحات موضوعية: Familial amyotrophic lateral sclerosis (FALS), Frontotemporal dementia (FTD), Spastic paraplegia (SP), UBQLN2
وصف الملف: application/pdf
الإتاحة: https://doi.org/10.1016/j.neurobiolaging.2018.08.015Test
https://kclpure.kcl.ac.uk/portal/en/publications/d64da4de-91b5-4a81-9c55-cae1aa958f87Test
https://kclpure.kcl.ac.uk/ws/files/101006225/Striking_phenotypic_variation_in_GKAZI_Firstonline24August2018_GREEN_AAM_CC_BY_NC_ND_.pdfTest
http://www.scopus.com/inward/record.url?scp=85055047566&partnerID=8YFLogxKTest -
8دورية أكاديمية
المؤلفون: Preece, Roland, Georgiadis, Christos, Gkazi, Soragia Athina, Etuk, Aniekan, Christi, Abraham, Qasim, Waseem
المساهمون: DH | National Institute for Health Research, Great Ormond Street Hospital for Children
المصدر: Gene Therapy ; volume 27, issue 9, page 451-458 ; ISSN 0969-7128 1476-5462
مصطلحات موضوعية: Genetics, Molecular Biology, Molecular Medicine
الإتاحة: https://doi.org/10.1038/s41434-020-0142-zTest
http://www.nature.com/articles/s41434-020-0142-z.pdfTest
http://www.nature.com/articles/s41434-020-0142-zTest -
9دورية أكاديمية
المؤلفون: Gkazi, Soragia Athina
المساهمون: Qasim, Waseem
المصدر: Emerging Topics in Life Sciences ; volume 3, issue 3, page 327-334 ; ISSN 2397-8554 2397-8562
الإتاحة: https://doi.org/10.1042/etls20180146Test
https://portlandpress.com/emergtoplifesci/article-pdf/3/3/327/851037/etls-2018-0146c.pdfTest -
10دورية
المؤلفون: Adams, Stuart, Hancock, Jeremy, Kaplinsky, Joe, Sosinsky, Alona, Wright, Gary, Gkazi, Soragia Athina, Kricke, Susanne, Thomas, Rebecca, Kent, Natalie, Hodder, Angus, Bartram, Jack
المصدر: Blood; November 2023, Vol. 142 Issue: 1, Number 1 Supplement 1 p4351-4351, 1p