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1دورية أكاديمية
المؤلفون: Xiaoyi Cheng, Radwa Barakat, Giulia Pavani, Masuma Khatun Usha, Rodolfo Calderon, Elizabeth Snella, Abigail Gorden, Yudi Zhang, Paul Gadue, Deborah L. French, Karin S. Dorman, Antonella Fidanza, Clyde A. Campbell, Raquel Espin-Palazon
المصدر: Nature Communications, Vol 14, Iss 1, Pp 1-19 (2023)
مصطلحات موضوعية: Science
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/2041-1723Test
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2دورية أكاديمية
المؤلفون: Marine Laurent, Marine Geoffroy, Giulia Pavani, Simon Guiraud
المصدر: Cells, Vol 13, Iss 10, p 800 (2024)
مصطلحات موضوعية: CRISPR/Cas9, gene editing, blood disorders, neuromuscular disorders, β-hemoglobinopathies, Duchenne muscular dystrophy, Cytology, QH573-671
وصف الملف: electronic resource
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3دورية أكاديمية
المؤلفون: Giulia Pavani, Marine Laurent, Anna Fabiano, Erika Cantelli, Aboud Sakkal, Guillaume Corre, Peter J. Lenting, Jean-Paul Concordet, Magali Toueille, Annarita Miccio, Mario Amendola
المصدر: Nature Communications, Vol 11, Iss 1, Pp 1-13 (2020)
مصطلحات موضوعية: Science
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/2041-1723Test
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4دورية أكاديمية
المؤلفون: Giulia Pavani, Mario Amendola
المصدر: Frontiers in Genome Editing, Vol 3 (2021)
مصطلحات موضوعية: genome editing, gene therapy, nuclease, CRISPR, targeted integration (TI), knock-in, Biotechnology, TP248.13-248.65, Genetics, QH426-470
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fgeed.2021.682171/fullTest; https://doaj.org/toc/2673-3439Test
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5دورية أكاديمية
المؤلفون: Giulia Pavani, Mario Amendola
المصدر: Frontiers in Genome Editing, Vol 2 (2021)
مصطلحات موضوعية: genome editing, gene therapy, nuclease, CRISPR, targeted integration (TI), knock-in, Biotechnology, TP248.13-248.65, Genetics, QH426-470
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fgeed.2020.609650/fullTest; https://doaj.org/toc/2673-3439Test
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6دورية أكاديمية
المؤلفون: Giulia Pavani, Marine Laurent, Anna Fabiano, Erika Cantelli, Aboud Sakkal, Guillaume Corre, Peter J. Lenting, Jean-Paul Concordet, Magali Toueille, Annarita Miccio, Mario Amendola
المصدر: Nature Communications, Vol 11, Iss 1, Pp 1-1 (2020)
مصطلحات موضوعية: Science
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/2041-1723Test
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7
المؤلفون: Hyun Hyung An, Alyssa L. Gagne, Jean Ann Maguire, Giulia Pavani, Osheiza Abdulmalik, Paul Gadue, Deborah L. French, Connie M. Westhoff, Stella T. Chou
المصدر: Blood. 140(15)
مصطلحات موضوعية: Pluripotent Stem Cells, Rh-Hr Blood-Group System, Transfusion Medicine, Immunology, Blood Group Antigens, Humans, Cell Biology, Hematology, Biochemistry, Alleles
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::9855d693c99972244759e31bfab5cf59Test
https://pubmed.ncbi.nlm.nih.gov/36227750Test -
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المؤلفون: Catriana C. Nations, Paul Gadue, Giulia Pavani, Deborah L. French
المصدر: Curr Opin Hematol
مصطلحات موضوعية: Blood Platelets, Pluripotent Stem Cells, Models, Genetic, Platelet disorder, Genetic Diseases, Inborn, Cell Differentiation, Hematology, Disease, Biology, Embryonic stem cell, Article, Hematopoiesis, Haematopoiesis, medicine.anatomical_structure, Megakaryocyte, medicine, Animals, Humans, Blood Platelet Disorders, Progenitor cell, Induced pluripotent stem cell, Megakaryocytes, Neuroscience, Reprogramming
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::3b68c0743c226675aad526418122c3e5Test
https://doi.org/10.1097/moh.0000000000000671Test -
9
المؤلفون: Michael W. Drazer, Joshua G. Klein, Mortimer Poncz, Catriana C. Nations, Lucy A. Godley, Giulia Pavani, Deborah L. French, Rodney M. Camire, Jean Ann Maguire, Paul Gadue, Sara Borst
المصدر: Stem Cell Reports
مصطلحات موضوعية: 0301 basic medicine, Induced Pluripotent Stem Cells, iPSCs, Biology, Biochemistry, Models, Biological, Germline, megakaryocyte, 03 medical and health sciences, chemistry.chemical_compound, 0302 clinical medicine, Germline mutation, Megakaryocyte, Runx1, Report, Genetics, medicine, Humans, Genetic Predisposition to Disease, Induced pluripotent stem cell, Cells, Cultured, Proto-Oncogene Proteins c-ets, Cell Biology, ETV6, embryonic stem cells, Embryonic stem cell, Phenotype, Thrombocytopenia, hematopoiesis, Repressor Proteins, Haematopoiesis, 030104 developmental biology, medicine.anatomical_structure, RUNX1, chemistry, Core Binding Factor Alpha 2 Subunit, Mutation, Cancer research, Megakaryocytes, 030217 neurology & neurosurgery, Developmental Biology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::c28e11f4d1e0c0bf088d925b278e387cTest
http://europepmc.org/articles/PMC8190596Test -
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المؤلفون: Giulia, Pavani, Joshua G, Klein, Deborah L, French, Paul, Gadue
المصدر: Methods in molecular biology (Clifton, N.J.). 2520
مصطلحات موضوعية: Cytosine, Genome, Human, Adenine, Induced Pluripotent Stem Cells, Humans, CRISPR-Cas Systems
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=pmid________::e44c9ce678356c7d0132fc2219992e08Test
https://pubmed.ncbi.nlm.nih.gov/35579838Test