التفاصيل البيبلوغرافية
| العنوان: |
Safety, tolerability and pharmacokinetics of eteplirsen in young boys aged 6–48 months with Duchenne muscular dystrophy amenable to exon 51 skipping |
| المؤلفون: |
E. Mercuri, A.M. Seferian, L. Servais, N. Deconinck, H. Stevenson, X. Ni, W. Zhang, L. East, S. Yonren, F. Muntoni, Nicolas Deconinck, Rudy Van Coster, Arnaud Vanlander, Andreea Seferian, Silvana De Lucia, Teresa Gidaro, Laura Vanden Brande, Laurent Servais, Janbernd Kirschner, Sabine Borell, Eugenio Mercuri, Claudia Brogna, Marika Pane, Lavinia Fanelli, Giulia Norcia, Francesco Muntoni, Chiara Brusa, Mary Chesshyre, Kate Maresh, Jaqueline Pitchforth, Lucia Schottlaender, Mariacristina Scoto, Arpana Silwal, Fedrica Trucco |
| المصدر: |
Neuromuscular Disorders. 33:476-483 |
| بيانات النشر: |
Elsevier BV, 2023. |
| سنة النشر: |
2023 |
| مصطلحات موضوعية: |
Neurology, Pediatrics, Perinatology and Child Health, Neurology (clinical), Genetics (clinical) |
| تدمد: |
0960-8966 |
| الوصول الحر: |
https://explore.openaire.eu/search/publication?articleId=doi_________::010c398abc3705355c31db1d1dedc9efTest
https://doi.org/10.1016/j.nmd.2023.03.008Test |
| حقوق: |
OPEN |
| رقم الانضمام: |
edsair.doi...........010c398abc3705355c31db1d1dedc9ef |
| قاعدة البيانات: |
OpenAIRE |
