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1دورية أكاديمية
المؤلفون: Giulia Bortolussi, Alessandra Iaconcig, Giulia Canarutto, Fabiola Porro, Filippo Ferrucci, Claudia Galletta, Cristian Díaz-Muñoz, Vipin Rawat, Alessia De Caneva, Olayemi Joseph Olajide, Lorena Zentilin, Silvano Piazza, Luka Bočkor, Andrés Fernando Muro
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 31, Iss , Pp 101161- (2023)
مصطلحات موضوعية: gene editing, neonatal mice, liver-directed gene editing, adeno-associated viral vector, AAV, bilirubin, CRISPR-SaCas9, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050123002000Test; https://doaj.org/toc/2329-0501Test
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2دورية أكاديمية
المؤلفون: Michela Lisjak, Alessia De Caneva, Thibaut Marais, Elena Barbon, Maria Grazia Biferi, Fabiola Porro, Adi Barzel, Lorena Zentilin, Mark A. Kay, Federico Mingozzi, Andrés F. Muro
المصدر: Frontiers in Genome Editing, Vol 4 (2022)
مصطلحات موضوعية: GeneRide, albumin gene targeting, mouse model, coagulation factor IX, tail clip test, CRISPR/SaCas9, Biotechnology, TP248.13-248.65, Genetics, QH426-470
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fgeed.2022.785698/fullTest; https://doaj.org/toc/2673-3439Test
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3دورية أكاديمية
المؤلفون: Fabiola Porro, Luka Bockor, Alessia De Caneva, Giulia Bortolussi, Andrés F Muro
المصدر: PLoS ONE, Vol 9, Iss 8, p e104816 (2014)
وصف الملف: electronic resource
العلاقة: http://europepmc.org/articles/PMC4132024?pdf=renderTest; https://doaj.org/toc/1932-6203Test
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4دورية أكاديمية
المؤلفون: Luisa Costessi, Fabiola Porro, Alessandra Iaconcig, Mirjana Nedeljkovic, Andrés Fernando Muro
المصدر: PLoS ONE, Vol 8, Iss 3, p e58879 (2013)
وصف الملف: electronic resource
العلاقة: https://www.ncbi.nlm.nih.gov/pmc/articles/pmid/23554949/pdf/?tool=EBITest; https://doaj.org/toc/1932-6203Test
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5صورة
المؤلفون: Michela Lisjak, Alessia De Caneva, Thibaut Marais, Elena Barbon, Maria Grazia Biferi, Fabiola Porro, Adi Barzel, Lorena Zentilin, Mark A. Kay, Federico Mingozzi, Andrés F. Muro
مصطلحات موضوعية: Genetics, Molecular Biology, Genetic Engineering, Molecular Medicine, Gene and Molecular Therapy, GeneRide, albumin gene targeting, mouse model, coagulation factor IX, tail clip test, CRISPR/SaCas9
الإتاحة: https://doi.org/10.3389/fgeed.2022.785698.s001Test
https://figshare.com/articles/figure/Image1_Promoterless_Gene_Targeting_Approach_Combined_to_CRISPR_Cas9_Efficiently_Corrects_Hemophilia_B_Phenotype_in_Neonatal_Mice_tiff/19343618Test -
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المؤلفون: Michela Lisjak, Alessia De Caneva, Thibaut Marais, Elena Barbon, Maria Grazia Biferi, Fabiola Porro, Adi Barzel, Lorena Zentilin, Mark A. Kay, Federico Mingozzi, Andrés F. Muro
مصطلحات موضوعية: Genetics, Molecular Biology, Genetic Engineering, Molecular Medicine, Gene and Molecular Therapy, GeneRide, albumin gene targeting, mouse model, coagulation factor IX, tail clip test, CRISPR/SaCas9
الإتاحة: https://doi.org/10.3389/fgeed.2022.785698.s006Test
https://figshare.com/articles/dataset/Table1_Promoterless_Gene_Targeting_Approach_Combined_to_CRISPR_Cas9_Efficiently_Corrects_Hemophilia_B_Phenotype_in_Neonatal_Mice_pdf/19343648Test -
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المؤلفون: Dimitar G. Efremov, Silvano Piazza, Supriya Chakraborty, Tiziana Vaisitti, Alice Bonato, Marija Dimishkovska, Silvia Deaglio, Rosa Fazio, Fabiola Porro, Idanna Innocenti, Ilaria Fortunati, Aleksandar Dimovski, Luca Laurenti, Alberto Zamò, Claudio Martines, Brijesh Singh Yadav
المصدر: Blood. 138(12)
مصطلحات موضوعية: Chronic lymphocytic leukemia, Immunology, Receptors, Antigen, B-Cell, Biology, Biochemistry, Mice, Downregulation and upregulation, hemic and lymphatic diseases, Cell Line, Tumor, medicine, Animals, Humans, Receptor, neoplasms, Cyclin-Dependent Kinase Inhibitor p16, Cyclin-Dependent Kinase Inhibitor p15, Kinase, Cell growth, Cyclin-dependent kinase 4, breakpoint cluster region, Cell Biology, Hematology, Cell cycle, medicine.disease, Leukemia, Lymphocytic, Chronic, B-Cell, Settore MED/15 - MALATTIE DEL SANGUE, Cell Transformation, Neoplastic, Cancer research, biology.protein, Tumor Suppressor Protein p53, chronic lymphocytic leukaemia, Signal Transduction
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::caca9ab929952b6383ceaa1769c35d20Test
https://pubmed.ncbi.nlm.nih.gov/34554222Test -
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المؤلفون: Ilaria Fortunati, Idanna Innocenti, Silvia Deaglio, Alberto Zamò, Aleksandar Dimovski, Rosa Fazio, Dimitar G. Efremov, Brijesh Singh Yadav, Marija Dimishkovska, Supriya Chakraborty, Tizianna Vaisitti, Luca Laurenti, Alice Bonato, Fabiola Porro, Claudio Martines
مصطلحات موضوعية: Richter syndrome, Immunology, B-cell receptor, Cell Biology, Hematology, Biology, Biochemistry, Signal, Settore MED/15 - MALATTIE DEL SANGUE, CDKN2A, hemic and lymphatic diseases, CDKN2B, Cancer research, neoplasms, Richter Syndrome
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::366b33d84002704d943fe86c2ca158d8Test
http://hdl.handle.net/10807/184877Test -
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المؤلفون: Claudio Martines, Malgorzata Bobrowicz, Sven Turkalj, Beata Pyrzynska, Joanna Stachura, Binu K. Sasi, Engin Bojnik, Francesco Bertoni, Dimitar G. Efremov, Magdalena Winiarska, Richard Rosenquist, Elena Xerxa, Hilal Kalkan, Larry Mansouri, Valdemar Priebe, Fabiola Porro, Rosa Fazio, Abdessamad Zerrouqi
المصدر: Leukemia. 33(10)
مصطلحات موضوعية: 0301 basic medicine, Cancer Research, B-cell receptor, Syk, Antineoplastic Agents, Apoptosis, Mice, SCID, 03 medical and health sciences, chemistry.chemical_compound, Mice, Phosphatidylinositol 3-Kinases, 0302 clinical medicine, immune system diseases, Mice, Inbred NOD, hemic and lymphatic diseases, Cell Line, Tumor, medicine, Agammaglobulinaemia Tyrosine Kinase, Bruton's tyrosine kinase, Animals, Humans, Syk Kinase, MCL1, PI3K/AKT/mTOR pathway, Cell Proliferation, Sulfonamides, biology, Venetoclax, Protein Tyrosine Phosphatase, Non-Receptor Type 6, breakpoint cluster region, Hematology, medicine.disease, Bridged Bicyclo Compounds, Heterocyclic, Xenograft Model Antitumor Assays, 3. Good health, 030104 developmental biology, Oncology, chemistry, Proto-Oncogene Proteins c-bcl-2, 030220 oncology & carcinogenesis, Cancer research, biology.protein, Female, Lymphoma, Large B-Cell, Diffuse, Diffuse large B-cell lymphoma, Signal Transduction
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::c8ee0c29e9fa452d48dd21bf19da2a2dTest
https://pubmed.ncbi.nlm.nih.gov/30872780Test -
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المؤلفون: Luisa Costessi, Alessandra Iaconcig, Fabiola Porro, Andrés F. Muro
المصدر: RNA Biology. 11:1280-1290
مصطلحات موضوعية: Polyadenylation, RNA Stability, Blotting, Western, Electrophoretic Mobility Shift Assay, RNA-binding protein, Biology, Real-Time Polymerase Chain Reaction, Mice, mental disorders, Gene expression, RNA Precursors, Animals, Humans, RNA, Messenger, Molecular Biology, mRNA Cleavage and Polyadenylation Factors, Regulation of gene expression, Messenger RNA, Synapse assembly, Reverse Transcriptase Polymerase Chain Reaction, Three prime untranslated region, RNA-Binding Proteins, nutritional and metabolic diseases, Cell Biology, Blotting, Northern, Research Papers, Molecular biology, nervous system diseases, DNA-Binding Proteins, Cytoskeletal Proteins, HEK293 Cells, Gene Expression Regulation, RNA splicing, HeLa Cells
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::e66e5abf1a40b412614581915292c5aeTest
https://doi.org/10.1080/15476286.2014.996081Test