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1دورية أكاديمية
المؤلفون: Amy Bartlett, Stephen J. Kolb, Allison Kingsley, Kathryn J. Swoboda, Sandra P. Reyna, Ai Sakonju, Basil T. Darras, Richard Shell, Nancy Kuntz, Diana Castro, Susan T. Iannaccone, Julie Parsons, Anne M. Connolly, Claudia A. Chiriboga, Craig McDonald, W. Bryan Burnette, Klaus Werner, Mathula Thangarajh, Perry B. Shieh, Erika Finanger, Christopher S. Coffey, Jon W. Yankey, Merit E. Cudkowicz, Michelle M. McGovern, D. Elizabeth McNeil, W. David Arnold, John T. Kissel
المصدر: Contemporary Clinical Trials Communications, Vol 11, Iss , Pp 113-119 (2018)
مصطلحات موضوعية: Medicine (General), R5-920
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S2451865418300243Test; https://doaj.org/toc/2451-8654Test
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2دورية أكاديمية
المؤلفون: Michael J. Gale, Hope E. Titus, Gareth A. Harman, Talal Alabduljalil, Anna Dennis, Jenny L. Wilson, David M. Koeller, Erika Finanger, Peter A. Blasco, Pei-Wen Chiang, Daniel J. Karr, Paul Yang
المصدر: American Journal of Ophthalmology Case Reports, Vol 10, Iss , Pp 244-248 (2018)
مصطلحات موضوعية: Ophthalmology, RE1-994
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S2451993617302396Test; https://doaj.org/toc/2451-9936Test
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المؤلفون: Erin Neil Knierbein, Declan O'Rourke, Richard S. Finkel, Monique M. Ryan, Cuixia Tian, Craig M. McDonald, W. Bryan Burnette, Cam-Tu Emilie Nguyen, Han C. Phan, Erika Finanger, Katherine D. Mathews, H. Lee Sweeney, Jessica Nance, Hugh J. McMillan, Gary McCullagh, Jeffrey Statland, Kathryn R. Wagner, Michelle Eagle, Joanne M. Donovan, Jessika Johannsen, Warren Marks, James MacDougall, Maria Cecilia Mancini, Mar Tulinius, Kayal Vijayakumar, Wolfgang Müller-Felber
المصدر: Journal of Neuromuscular Diseases
مصطلحات موضوعية: 0301 basic medicine, Research Report, Duchenne muscular dystrophy, Male, medicine.medical_specialty, edasalonexent, Phases of clinical research, Administration, Oral, Subgroup analysis, Arachidonic Acids, Placebo, NF-κB, 03 medical and health sciences, 0302 clinical medicine, Double-Blind Method, Statistical significance, Internal medicine, NSAA - Total, Salicylamides, medicine, Humans, Adverse effect, Child, CAT-1004, business.industry, NF-kappa B, medicine.disease, Muscular Dystrophy, Duchenne, 030104 developmental biology, Neurology, Child, Preschool, Ambulatory, age effects, Neurology (clinical), business, 030217 neurology & neurosurgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::4ef0de36feced883ff8135df9c9185fcTest
http://europepmc.org/articles/PMC8543277Test -
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المؤلفون: Gihan Tennekoon, Maria Cecilia Mancini, Richard S. Finkel, Sabrina W. Yum, Sean C. Forbes, A. Nichols, Joanne M. Donovan, H. Lee Sweeney, Glenn A. Walter, Angelika Fretzen, William T. Triplett, Krista Vandenborne, James MacDougall, Erika Finanger, P. Bista, Rebecca J. Willcocks, Perry B. Shieh, William D. Rooney
المصدر: Neuromuscular Disorders. 31:385-396
مصطلحات موضوعية: Male, 0301 basic medicine, medicine.drug_class, Duchenne muscular dystrophy, Arachidonic Acids, Disease, Pharmacology, Proof of Concept Study, Anti-inflammatory, Dystrophin, 03 medical and health sciences, chemistry.chemical_compound, 0302 clinical medicine, Double-Blind Method, Salicylamides, Humans, Medicine, Child, Muscle, Skeletal, Genetics (clinical), business.industry, NF-kappa B, NF-κB, medicine.disease, Small molecule, Muscular Dystrophy, Duchenne, 030104 developmental biology, Neurology, chemistry, Docosahexaenoic acid, Child, Preschool, Pediatrics, Perinatology and Child Health, Disease Progression, Neurology (clinical), Open label, business, 030217 neurology & neurosurgery, Salicylic acid
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::e2fa34a107912e09b9d437a015defaf4Test
https://doi.org/10.1016/j.nmd.2021.02.001Test -
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المؤلفون: Perry B Shieh, Gary Elfring, Panayiota Trifillis, Claudio Santos, Stuart W Peltz, Julie A Parsons, Susan Apkon, Basil T Darras, Craig Campbell, Craig M McDonald, Richard J Barohn, Enrico Bertini, Kate Bushby, Brigitte Chabrol, Emma Ciafaloni, Jaume Columer, Giacomi Pietro Comi, Anne Connolly, Richard S Finkel, Kevin M Flanigan, Nathalie Goemans, Michela Guglieri, Susan T Iannaccone, Kristi J Jones, Petra Kaufmann, Janbernd Kirschner, Jean K Mah, Katherine Mathews, Eugenio Mercuri, Francesco Muntoni, Yoram Nevo, Andrés Nascimento Osorio, Yann Péréon, Rosaline Quinlivan, J. Ben Renfroe, Barry Russman, Monique Ryan, Jacinda Sampson, Ulrike Schara, Kathryn Selby, Thomas Sejersen, Douglas M Sproule, H. Lee Sweeney, Már Tulinius, Juan J Vilchez, Giuseppe Vita, Thomas Voit, Stephanie Burns-Wechsler, Brenda Wong, Ted Abresch, Erik K Henricson, Kim Coleman, Michelle Eagle, Julaine Florence, Ed Gappmaier, Craig McDonald, Hoda Z Abdel-Hamid, Clemens Bloetzer, Russell J Butterfield, Jong-Hee Chae, Jahannaz Dastgir, Isabelle Desguerre, Raul G Escobar, Erika Finanger, Peter Heydemann, Imelda Hughes, Anna Kaminska, Peter Karachunski, Martin Kudr, Timothy Lotze, Alexandra Prufer de Queiroz Campos Araujo, Maria Bernadete Dutra de Resende, Gihan Tennekoon, Haluk Topaloglu, Ricardo Erazo Torricelli, Lindsay N Alfano, Meredith K James, Linda Lowes, Anna Mayhew, Elena S Mazzone, Leslie Nelson, Kristy J Rose
المصدر: Paediatrics Publications
مصطلحات موضوعية: Duchenne muscular dystrophy, medicine.medical_specialty, nonsense mutation Duchenne muscular dystrophy, Prednisolone, Population, Nonsense mutation, Placebo, chemistry.chemical_compound, Pregnenediones, Prednisone, Internal medicine, medicine, Humans, education, deflazacort, Retrospective Studies, education.field_of_study, business.industry, Health Policy, prednisolone, medicine.disease, Ataluren, Muscular Dystrophy, Duchenne, Deflazacort, meta-analysis, chemistry, Codon, Nonsense, prednisone, business, medicine.drug
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::1e773db882a9b68ac18148646fe6a8d7Test
https://ir.lib.uwo.ca/context/paedpub/article/3206/viewcontent/843.pdfTest -
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المؤلفون: Ann T. Harrington, John F. Brandsema, Glenn A. Walter, Rebecca J. Willcocks, Harneet Arora, Michael J. Daniels, William T. Triplett, Gihan Tennekoon, Krista Vandenborne, Claudia R. Senesac, Erika Finanger, H. Lee Sweeney, Alison M. Barnard, Donovan J. Lott, William D. Rooney, Sean C. Forbes, Dah Jyuu Wang, Umar Alabasi
المصدر: Radiology
مصطلحات موضوعية: Male, In vivo magnetic resonance spectroscopy, Adolescent, Proton Magnetic Resonance Spectroscopy, Duchenne muscular dystrophy, Deltoid curve, Thigh, Biceps, 030218 nuclear medicine & medical imaging, Cohort Studies, 03 medical and health sciences, 0302 clinical medicine, Forearm, Outcome Assessment, Health Care, medicine, Humans, Radiology, Nuclear Medicine and imaging, Prospective Studies, Muscular dystrophy, Child, Muscle, Skeletal, Prospective cohort study, Original Research, Leg, business.industry, medicine.disease, Magnetic Resonance Imaging, Muscular Dystrophy, Duchenne, Cross-Sectional Studies, medicine.anatomical_structure, Case-Control Studies, 030220 oncology & carcinogenesis, Arm, Disease Progression, Feasibility Studies, business, Nuclear medicine
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::f308dc946b30fa57f404285eb7254d08Test
https://doi.org/10.1148/radiol.2020192210Test -
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المؤلفون: William T. Triplett, Sean C. Forbes, Barry S. Russman, Claudia R. Senesac, G. Tennekoon, Harneet Arora, Rebecca J. Willcocks, Erika Finanger, Michael J. Daniels, Dah Jyuu Wang, Richard S. Finkel, William D. Rooney, Yosef A. Berlow, Elliott O'Brien, Donovan J. Lott, Saptarshi Chakraborty, Brendan Moloney, Alison M. Barnard, Krista Vandenborne, H. Lee Sweeney, Ishu Arpan, Glenn A. Walter
المصدر: Neurology
مصطلحات موضوعية: Male, 0301 basic medicine, medicine.medical_specialty, Magnetic Resonance Spectroscopy, Adolescent, Duchenne muscular dystrophy, Population, Corticosteroid treatment, Walking, Article, 03 medical and health sciences, 0302 clinical medicine, Adrenal Cortex Hormones, Internal medicine, medicine, Humans, Muscular dystrophy, Child, Muscle, Skeletal, education, Leg, education.field_of_study, medicine.diagnostic_test, Disease trajectory, business.industry, Disease progression, Therapeutic effect, Magnetic resonance imaging, medicine.disease, Magnetic Resonance Imaging, Muscular Dystrophy, Duchenne, 030104 developmental biology, Child, Preschool, Disease Progression, Cardiology, Female, Neurology (clinical), business, Biomarkers, 030217 neurology & neurosurgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::3801c2c1126305e4799fbcff5f53a6acTest
https://doi.org/10.1212/wnl.0000000000009244Test -
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المؤلفون: Gihan Tennekoon, A. Nichols, Sabrina W. Yum, Hanlan Liu, P. Bista, Angelika Fretzen, Erika Finanger, H. Lee Sweeney, Richard S. Finkel, Krista Vandenborne, Joanne M. Donovan, Maria Cecilia Mancini
المصدر: Journal of Neuromuscular Diseases
مصطلحات موضوعية: 0301 basic medicine, Research Report, Duchenne muscular dystrophy, Male, medicine.medical_specialty, edasalonexent, Administration, Oral, Arachidonic Acids, Gastroenterology, NF-κB, 03 medical and health sciences, 0302 clinical medicine, Pharmacokinetics, Oral administration, Internal medicine, Salicylamides, medicine, Humans, Dosing, Adverse effect, Child, CAT-1004, business.industry, NF-kappa B, medicine.disease, Blood proteins, Muscular Dystrophy, Duchenne, 030104 developmental biology, Neurology, Tolerability, Neuromuscular Agents, Pharmacodynamics, Child, Preschool, Neurology (clinical), business, 030217 neurology & neurosurgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::4ee4e21dacc995b6e3885ef5352cbd6fTest
http://europepmc.org/articles/PMC6398836Test -
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المؤلفون: Ai Sakonju, Erika Finanger, Nancy L. Kuntz, Diana Castro, Allison Kingsley, Kathryn J. Swoboda, Mathula Thangarajh, W. David Arnold, John T. Kissel, Sandra P. Reyna, D. Elizabeth McNeil, Klaus Werner, Richard Shell, Michelle McGovern, Perry B. Shieh, Basil T. Darras, Susan T. Iannaccone, Craig M. McDonald, Anne M. Connolly, Christopher S. Coffey, Amy Bartlett, Jon W. Yankey, Stephen J. Kolb, Claudia A. Chiriboga, W. Bryan Burnette, Merit Cudkowicz, Julie A. Parsons
المصدر: Contemporary Clinical Trials Communications, Vol 11, Iss, Pp 113-119 (2018)
Contemporary Clinical Trials Communicationsمصطلحات موضوعية: medicine.medical_specialty, Poor prognosis, Population, Network, Article, Clinical study, Social media, 03 medical and health sciences, 0302 clinical medicine, medicine, 030212 general & internal medicine, education, Healthy controls, Pharmacology, education.field_of_study, lcsh:R5-920, business.industry, Spinal muscle atrophy, General Medicine, SMA, Altruism, Natural history, Clinical trial, Family medicine, Biomarker (medicine), business, lcsh:Medicine (General), 030217 neurology & neurosurgery, Natural history study
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::1b2d218639a32eae9ed8ff77ff7b9e2cTest
http://www.sciencedirect.com/science/article/pii/S2451865418300243Test -
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المؤلفون: Krista Vandenborne, Gihan Tennekoon, William D. Rooney, Hilary Cunkle, Erika Finanger, Tanja Taivassalo, Ann M. Harrington, Claudia R. Senesac, Catherine Powers, Rebecca J. Willcocks, Kirsten L. Zilke, Donovan J. Lott
المصدر: Muscle Nerve
مصطلحات موضوعية: 0301 basic medicine, Male, medicine.medical_specialty, Physiology, Duchenne muscular dystrophy, Walking, 030105 genetics & heredity, Article, Cohort Studies, 03 medical and health sciences, Cellular and Molecular Neuroscience, Activity monitoring, 0302 clinical medicine, Physical medicine and rehabilitation, Physiology (medical), Accelerometry, Activities of Daily Living, medicine, Humans, Functional ability, Mobility Limitation, Child, Exercise, Glucocorticoids, business.industry, Ambulatory Status, Walking (activity), medicine.disease, Large cohort, Clinical trial, Muscular Dystrophy, Duchenne, Functional Status, Case-Control Studies, Child, Preschool, Ambulatory, Disease Progression, Neurology (clinical), business, 030217 neurology & neurosurgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::4ac3bed17efc67a48d2754bec968b174Test
https://europepmc.org/articles/PMC8314165Test/