-
1دورية أكاديمية
المؤلفون: Yu, Y., Dunaway, S., Champer, J., Kim, J., Alikhan, A.
المصدر: British Journal of Dermatology ; volume 182, issue 1, page e28-e28 ; ISSN 0007-0963
-
2دورية أكاديمية
المؤلفون: Yu, Y., Dunaway, S., Champer, J., Kim, J., Alikhan, A.
المصدر: British Journal of Dermatology ; volume 182, issue 1, page e45-e45 ; ISSN 0007-0963
مصطلحات موضوعية: Dermatology
-
3دورية أكاديمية
المؤلفون: Riddler, S.A., Zheng, L., Durand, C.M., Ritz, J., Koup, R.A., Ledgerwood, J., Bailer, R.T., Koletar, S.L., Eron, J.J., Keefer, M.C., Macatangay, B.J.C., Cyktor, J.C., Mellors, J.W., Hite, M., Clark, J., Currin, D., Tipton, M., Weinman, R., Onesi, S., Hurley, C., Bunce, C.A., Storey, S., Dunaway, S., Lambert, N., Berzins, B., Gottesman, J., Leonard, M., Ray, G., Kittelson, P., Benson, C., Muttera, L., Flynn, T., Sbrolla, A., Wiggins, I., Howard, J., Arduino, R.C., Villamil, A.E., Kessels, L., Spitz, T., Campbell, D., Kudumu, M., Sise, T., Nair, A., Baer, J., Epperson, K., Perelson, A., Jennings, C., Tressler, R., Acosta, Ed., Casazza, J., Benns, A., AIDS Clinical Trials Group A5342 Protocol Team
المصدر: Open Forum Infectious Diseases, 5(10)
مصطلحات موضوعية: VRC01, HIV-1 cure, Clinical trial, BnMAb, HIV-1 persistence
العلاقة: https://doi.org/10.17615/p8th-zw41Test; https://cdr.lib.unc.edu/downloads/sb397f65r?file=thumbnailTest; https://cdr.lib.unc.edu/downloads/sb397f65rTest
الإتاحة: https://doi.org/10.17615/p8th-zw41Test
https://cdr.lib.unc.edu/downloads/sb397f65r?file=thumbnailTest
https://cdr.lib.unc.edu/downloads/sb397f65rTest -
4دورية أكاديمية
المؤلفون: Pera, MC, Coratti, G, Forcina, N, Mazzone, ES, Scoto, M, Montes, J, Pasternak, A, Mayhew, A, Messina, S, Sframeli, M, Main, M, Lofra, RM, Duong, T, Ramsey, D, Dunaway, S, Salazar, R, Fanelli, L, Civitello, M, de Sanctis, R, Antonaci, L, Lapenta, L, Lucibello, S, Pane, M, Day, J, Darras, BT, De Vivo, DC, Muntoni, F, Finkel, R, Mercuri, E
المصدر: BMC Neurology , 17 (1) , Article 39. (2017)
مصطلحات موضوعية: Carers, Clinical trials, Quality of life, Spinal muscular atrophy
وصف الملف: text
العلاقة: https://discovery.ucl.ac.uk/id/eprint/1544842/1/Muntoni_art%25253A10.1186%25252Fs12883-017-0790-9.pdfTest; https://discovery.ucl.ac.uk/id/eprint/1544842Test/
-
5دورية أكاديمية
المؤلفون: Finkel, RS, Mercuri, E, Darras, BT, Connolly, AM, Kuntz, NL, Kirschner, J, Chiriboga, CA, Saito, K, Servais, L, Tizzano, E, Topaloglu, H, Tulinius, M, Montes, J, Glanzman, AM, Bishop, K, Zhong, ZJ, Gheuens, S, Bennett, CF, Schneider, E, Farwell, W, De Vivo, DC, Bradley, WG, Schroth, MK, Bodensteriner, JB, Davis, CS, Shell, R, Hen, J, Austin, ED, Aziz-Zaman, S, Cappell, J, Constantinescu, A, Cruz, R, Dastgir, J, Dunaway, S, Engelstad, K, Gormley, M, Holuba La Marca, N, Khandji, A, Kramer, S, Marra, J, Ortiz-Miller, C, Popolizio, M, Salazar, R, Sanabria, L, Weimer, L, Anand, P, Gadeken, R, Golumbek, PT, Siener, C, Zaidman, CM, Al-Ghamdi, F, Berde, C, Ghosh, P, Graham, R, Harrington, T, Koka, A, Laine, R, Liew, W, Mirek, E, Ordonez, G, Pasternak, A, Quigley, J, Sethna, N, Souris, M, Szelag, H, Wand, L, Day, JW, D'Souza, G, Duong, TT, Gee, R, Kitsuwa-Lowe, J, McFall, D, Patnaik, S, Paulose, S, Perez, J, Proud, C, Purse, B, Ramamurthi, RJ, Sakamuri, S, Sampson, J, Sanjanwala, B, Tesi Rocha, AC, Watson, K, Welsh, L, Pena, LDM, Case, L, Coates, J, DeArmey, S, Homi, MM, Milleson, C, Nelson, N, Ross, A, Smith, E, Taicher, B, Wootton, J, Finanger, E, Benjamin, D, Frank, A, Roberts, C, Russman, B, Farrar, Michelle, Kandula, Tejaswi
المصدر: urn:ISSN:0028-4793 ; urn:ISSN:1533-4406 ; New England Journal of Medicine, 377, 18, 1723-1732
مصطلحات موضوعية: Brain Disorders, Pediatric, Clinical Research, Neurosciences, Genetics, Clinical Trials and Supportive Activities, Orphan Drug, Spinal Muscular Atrophy, Neurodegenerative, Patient Safety, Rare Diseases, Neurological, 3 Good Health and Well Being, Age of Onset, Disease-Free Survival, Double-Blind Method, Female, Humans, Infant, Injections, Spinal, Male, Motor Skills, Oligonucleotides, Antisense, RNA, Messenger, Respiration, Artificial, Spinal Muscular Atrophies of Childhood
وصف الملف: application/pdf
العلاقة: http://hdl.handle.net/1959.4/unsworks_49227Test; https://unsworks.unsw.edu.au/bitstreams/8464c3c3-9df7-43a0-be50-b5125661ad27/downloadTest; https://doi.org/10.1056/NEJMoa1702752Test
الإتاحة: https://doi.org/10.1056/NEJMoa1702752Test
http://hdl.handle.net/1959.4/unsworks_49227Test
https://unsworks.unsw.edu.au/bitstreams/8464c3c3-9df7-43a0-be50-b5125661ad27/downloadTest -
6دورية أكاديمية
المؤلفون: Mercuri, E., Darras, B. T., Chiriboga, C. A., Day, J. W., Campbell, C., Connolly, A. M., Iannaccone, S. T., Kirschner, J., Kuntz, N. L., Saito, K., Shieh, P. B., Tulinius, M., Mazzone, E. S., Montes, J., Bishop, K. M., Yang, Q., Foster, R., Gheuens, S., Bennett, C. F., Farwell, W., Schneider, E., De Vivo, D. C., Finkel, R. S., Bradley WG, Kaufmann P, Dickson PI, Reingold SC, Davis CS, Arredondo K, Castro D, Cowie M, Farrow-Gillespie A, Hebert A, Kauk M, Miller N, Nelson L, Spain T Jr, Cappell J, Constantinescu A, Cruz R, Dastgir J, Dunaway S, Engelstad K, Khandji AG, Kramer S, Marra J, Popolizio M, Salazar R, Weimer LH, Aziz-Zaman S, LaMarca N, Ghosh P, Al-Ghamdi F, Liew W, Graham R, Berde C, Sethna N, Koka A, Wang L, Laine R, Souris M, Ordonez G, Harrington T, Szelag H, Pasternak A, Mirek E, Quigley J, Berry D, Civitello M, Endsley JD, Eden C, Leon W, O'Reardon K, Sigurdardottir L, Johnson C, Turner J, Vega M, Weber-Guzman F, Zinn M, Tesi Rocha AC, Watson K, D'Souza G, Ramamurthi RJ, Gee R, Kitsuwa-Lowe J, Hagerman K, Crasta S, Welsh L, Paulose S, McFall D, Perez J, Patnaik S, Sanjanwala B, Sakamuri S, Proud C, Purse BP, Duong TT, Sampson J, Tennekoon G, Brandsema J, Glanzman A, Flickinger J, Toms M, Adang L, Stanford D, Mayer O, Zigmont J, Chadehumbe M, Kichula E, Finanger E, Russman B, Roberts C, Frank A, Benjamin D, Zilke K, Golumbek PT, Zaidman CM, Anand P, Gadeken R, Siener C, Epstein L, Krueger J, Goldman S, Krosschell K, Blomgren C, Choi HW, Kurz J, Parsons J, Janas J, Yang M, Ballard A, Carry T, Shea S, Bielsky A, Booker K, Camuto A, Lord-Halvorson S, Gibbons M, Zimmerman C, Allen V, Fuhr P, Kelley C, Johnson H, Tran V, VanderVeen G, Fowler E, Parziale N, Rao L, Skura C, Shu F, Oskoui M, Zielinski D, Poulin C, Ingelmo PM, Desilets ST, Dinunzio P, Rivera G, Srour M, Arpin S, Goobie S, Gibson P, Scholtes C, McDonald W, Zapata E, Nguyen CE, Servais L, Gargaun E, Le Moing AG, Gidaro T, Vialle R, Guye ML, Lilien C, Olliver G, Gilabert S, Borell S, Wider S, Stein S, Vogt S, Krüger M, Pechmann A, Rippberger B, Eckenweiler M, Schara U, Koelbel H, Andres B, Rupprich K, Gangfuss A, Jachertz P, Della Marina A, Sponemann N, Pane M, Palermo C, Piastra M, Fanelli L, De Sanctis R, Genovese O, Antonaci L, Pera MC, Lamendola P, Messina S, Vita G, Di Bella V, Sframeli M, La Rosa M, Barcellona C, Distefano MG, Cavallaro F, Versaci A, De Luca F, Nacimento Osorio A, Tizzano E, Ortez Gonzalez CI, Ortigoza Escobar JD, Colomer Oferil J, Medina Cantillo J, Rotger AF, Vigo Morancho M, Eldblom J, Darin N, Kroksmark AK, Lindstedt A, Michael E, Kimber E, Wahlgren L, Chan SH, Chim S, Chiu J, Ho ACC, Ip JKJ, Lam WWM, Ng MC, Wan C, Wong VCN, Yue Y, Arakawa R, Yamauchi A, Nagata S, Ito Y, Nakatsukasa H, Takeshita A, Hirasawa K, Ikai T, Eto K, Otamni Y, Takeshima Y, Fukuda N, Tanaka Y, Shimomura H, Lee T, Shibano T, Tachikawa T, Chae JH, Lim BC, Shin HI, Kim SY, Choi SA, Son WS, Jo H, Chun SM, Kim H.
المساهمون: Mercuri, E., Darras, B. T., Chiriboga, C. A., Day, J. W., Campbell, C., Connolly, A. M., Iannaccone, S. T., Kirschner, J., Kuntz, N. L., Saito, K., Shieh, P. B., Tulinius, M., Mazzone, E. S., Montes, J., Bishop, K. M., Yang, Q., Foster, R., Gheuens, S., Bennett, C. F., Farwell, W., Schneider, E., De Vivo, D. C., Finkel, R. S., Bradley, Wg, Kaufmann, P, Dickson, Pi, Reingold, Sc, Davis, C, Arredondo, K, Castro, D, Cowie, M, Farrow-Gillespie, A, Hebert, A, Kauk, M, Miller, N, Nelson, L, Spain, T Jr, Cappell, J, Constantinescu, A, Cruz, R, Dastgir, J, Dunaway, S, Engelstad, K, Khandji, Ag, Kramer, S, Marra, J, Popolizio, M, Salazar, R, Weimer, Lh, Aziz-Zaman, S, Lamarca, N, Ghosh, P, Al-Ghamdi, F, Liew, W, Graham, R, Berde, C, Sethna, N, Koka, A, Wang, L, Laine, R, Souris, M, Ordonez, G, Harrington, T, Szelag, H, Pasternak, A, Mirek, E, Quigley, J, Berry, D, Civitello, M, Endsley, Jd, Eden, C, Leon, W, O'Reardon, K, Sigurdardottir, L, Johnson, C, Turner, J, Vega, M, Weber-Guzman, F, Zinn, M, Tesi Rocha, Ac, Watson, K, D'Souza, G, Ramamurthi, Rj, Gee, R, Kitsuwa-Lowe, J, Hagerman, K, Crasta, S, Welsh, L, Paulose, S, Mcfall, D, Perez, J, Patnaik, S, Sanjanwala, B, Sakamuri, S, Proud, C, Purse, Bp, Duong, Tt, Sampson, J, Tennekoon, G, Brandsema, J
مصطلحات موضوعية: Age of Onset, Child, Preschool, Double-Blind Method, Female, Human, Infant, Injections, Spinal, Least-Squares Analysi, Male, Motor Skill, Oligonucleotide, Oligonucleotides, Antisense, Spinal Muscular Atrophies of Childhood, Medicine (all)
وصف الملف: STAMPA
العلاقة: info:eu-repo/semantics/altIdentifier/pmid/29443664; info:eu-repo/semantics/altIdentifier/wos/WOS:000425000000008; volume:378; issue:7; firstpage:625; lastpage:635; numberofpages:11; journal:NEW ENGLAND JOURNAL OF MEDICINE; http://hdl.handle.net/11570/3127475Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85042194277; http://www.nejm.org/medical-indexTest
الإتاحة: https://doi.org/10.1056/NEJMoa1710504Test
http://hdl.handle.net/11570/3127475Test
http://www.nejm.org/medical-indexTest -
7دورية أكاديمية
المؤلفون: Yu, Y., Dunaway, S., Champer, J., Kim, J., Alikhan, A.
المصدر: British Journal of Dermatology ; ISSN 0007-0963 1365-2133
-
8
المؤلفون: Hurley, C., AIDS Clinical Trials Group A5342 Protocol Team, Ritz, J., Storey, S., Gottesman, J., Sbrolla, A., Macatangay, B.J.C., Kessels, L., Arduino, R.C., Acosta, Ed., Perelson, A., Ray, G., Eron, J.J., Ledgerwood, J., Baer, J., Zheng, L., Lambert, N., Kudumu, M., Koup, R.A., Campbell, D., Tipton, M., Bunce, C.A., Epperson, K., Villamil, A.E., Sise, T., Casazza, J., Jennings, C., Dunaway, S., Tressler, R., Nair, A., Leonard, M., Cyktor, J.C., Bailer, R.T., Hite, M., Howard, J., Muttera, L., Clark, J., Weinman, R., Mellors, J.W., Durand, C.M., Koletar, S.L., Flynn, T., Benns, A., Keefer, M.C., Berzins, B., Currin, D., Riddler, S.A., Benson, C., Kittelson, P., Spitz, T., Wiggins, I., Onesi, S.
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::b93056666a9b7c3b36000d63201c3c0eTest
-
9دورية أكاديمية
المؤلفون: Mercuri, E, Finkel, R, Montes, J, Mazzone, Es, SORMANI, MARIA PIA, Main, M, Ramsey, D, Mayhew, A, Glanzman, Am, Dunaway, S, Salazar, R, Pasternak, A, Quigley, J, Pane, M, Pera, Mc, Scoto, M, Messina, S, Sframeli, M, Vita, Gl, D'Amico, A, van den Hauwe, M, Sivo, S, Goemans, N, Kaufmann, P, Darras, Bt, Bertini, E, Muntoni, F, De Vivo, D.c.3.
المساهمون: Mercuri, E, Finkel, R, Montes, J, Mazzone, E, Sormani, MARIA PIA, Main, M, Ramsey, D, Mayhew, A, Glanzman, Am, Dunaway, S, Salazar, R, Pasternak, A, Quigley, J, Pane, M, Pera, Mc, Scoto, M, Messina, S, Sframeli, M, Vita, Gl, D'Amico, A, van den Hauwe, M, Sivo, S, Goemans, N, Kaufmann, P, Darras, Bt, Bertini, E, Muntoni, F, De Vivo, D. c. 3.
وصف الملف: ELETTRONICO
العلاقة: info:eu-repo/semantics/altIdentifier/pmid/26776503; info:eu-repo/semantics/altIdentifier/wos/WOS:000371652100002; volume:26; firstpage:126; lastpage:131; numberofpages:6; journal:NEUROMUSCULAR DISORDERS; http://hdl.handle.net/11567/859005Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-84956949641
-
10دورية أكاديمية
المؤلفون: Ramsey, D., Scoto, M., Mayhew, A., Main, M., Mazzone, E., Montes, J., Dunaway, S., Salazar, R., Glanzman, A., Pasternak, A., Duong, T., Gee, R., Civitello, M., Bushby, K., Day, J., Darras, B., De Vivo, D., Finkel, R., Mercuri, E., Muntoni, F.
المصدر: Neuromuscular Disorders ; volume 26, page S104 ; ISSN 0960-8966
مصطلحات موضوعية: Genetics (clinical), Neurology (clinical), Neurology, Pediatrics, Perinatology and Child Health
الإتاحة: https://doi.org/10.1016/j.nmd.2016.06.071Test
https://api.elsevier.com/content/article/PII:S0960896616303649?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S0960896616303649?httpAccept=text/plainTest