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1دورية أكاديمية
المؤلفون: Shingo Suzuki, Keisuke Chosa, Cristina Barillà, Michael Yao, Orsetta Zuffardi, Hirofumi Kai, Tsuyoshi Shuto, Mary Ann Suico, Yuet W. Kan, R. Geoffrey Sargent, Dieter C. Gruenert
المصدر: Frontiers in Genome Editing, Vol 4 (2022)
مصطلحات موضوعية: cystic fibrosis, iPS cells, seamless gene correction, homology directed repair, non-homologous end joining, vector replacement event, Biotechnology, TP248.13-248.65, Genetics, QH426-470
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fgeed.2022.843885/fullTest; https://doaj.org/toc/2673-3439Test
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2دورية أكاديمية
المؤلفون: Shunsuke Kamei, Haruka Fujikawa, Hirofumi Nohara, Keiko Ueno-Shuto, Kasumi Maruta, Ryunosuke Nakashima, Taisei Kawakami, Chizuru Matsumoto, Yuki Sakaguchi, Tomomi Ono, Mary Ann Suico, Richard C. Boucher, Dieter C. Gruenert, Toru Takeo, Naomi Nakagata, Jian-Dong Li, Hirofumi Kai, Tsuyoshi Shuto
المصدر: EBioMedicine, Vol 27, Iss C, Pp 304-316 (2018)
مصطلحات موضوعية: ZIP2, CFTR, ENaC, Splicing isoform, Mucus hypersecretion, Cystic fibrosis, Medicine, Medicine (General), R5-920
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S2352396417305066Test; https://doaj.org/toc/2352-3964Test
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3دورية أكاديمية
المؤلفون: Shota Mizunoe, Tsuyoshi Shuto, Shingo Suzuki, Chizuru Matsumoto, Kenji Watanabe, Keiko Ueno-Shuto, Mary Ann Suico, Kouhei Onuki, Dieter C. Gruenert, Hirofumi Kai
المصدر: Journal of Pharmacological Sciences, Vol 118, Iss 4, Pp 512-520 (2012)
مصطلحات موضوعية: Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S1347861319305456Test; https://doaj.org/toc/1347-8613Test
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4دورية أكاديمية
المؤلفون: Chizuru Matsumoto, Dieter C. Gruenert, Hirofumi Kai, Keiko Ueno-Shuto, Kenji Watanabe, Kouhei Onuki, Mary Ann Suico, Shingo Suzuki, Shota Mizunoe, Tsuyoshi Shuto
المصدر: Journal of Pharmacological Sciences. 2012, 118(4):512
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5دورية أكاديمية
المؤلفون: Shingo Suzuki, R Geoffrey Sargent, Beate Illek, Horst Fischer, Alaleh Esmaeili-Shandiz, Michael J Yezzi, Albert Lee, Yanu Yang, Soya Kim, Peter Renz, Zhongxia Qi, Jingwei Yu, Marcus O Muench, Ashley I Beyer, Alessander O Guimarães, Lin Ye, Judy Chang, Eli J Fine, Thomas J Cradick, Gang Bao, Meghdad Rahdar, Matthew H Porteus, Tsuyoshi Shuto, Hirofumi Kai, Yuet W Kan, Dieter C Gruenert
المصدر: Molecular Therapy: Nucleic Acids, Vol 5, Iss C (2016)
مصطلحات موضوعية: cystic fibrosis iPS cells, iPSC directed differentiation, polynucleotide gene targeting/genome editing, sequence-specific chimeric endonucleases, SFHR, Therapeutics. Pharmacology, RM1-950
العلاقة: http://www.sciencedirect.com/science/article/pii/S2162253116300099Test; https://doaj.org/toc/2162-2531Test; https://doaj.org/article/aa7f6c58c90142c2a88dd3a6fd6f2d5fTest
الإتاحة: https://doi.org/10.1038/mtna.2015.43Test
https://doaj.org/article/aa7f6c58c90142c2a88dd3a6fd6f2d5fTest -
6
المؤلفون: Shingo Suzuki, Keisuke Chosa, Cristina Barillà, Michael Yao, Orsetta Zuffardi, Hirofumi Kai, Tsuyoshi Shuto, Mary Ann Suico, Yuet W. Kan, R. Geoffrey Sargent, Dieter C. Gruenert
مصطلحات موضوعية: Genetics, Molecular Biology, Genetic Engineering, Molecular Medicine, Gene and Molecular Therapy, cystic fibrosis, iPS cells, seamless gene correction, homology directed repair, non-homologous end joining, vector replacement event, vector insertion event, intrachromosomal homologous recombination
الإتاحة: https://doi.org/10.3389/fgeed.2022.843885.s001Test
https://figshare.com/articles/dataset/DataSheet1_Seamless_Gene_Correction_in_the_Human_Cystic_Fibrosis_Transmembrane_Conductance_Regulator_Locus_by_Vector_Replacement_and_Vector_Insertion_Events_pdf/19523218Test -
7دورية أكاديمية
المصدر: PLoS ONE, Vol 10, Iss 10, p e0141169 (2015)
العلاقة: http://europepmc.org/articles/PMC4612780?pdf=renderTest; https://doaj.org/toc/1932-6203Test; https://doaj.org/article/b88659b513e64bf6880afc0a97be084cTest
الإتاحة: https://doi.org/10.1371/journal.pone.0141169Test
https://doaj.org/article/b88659b513e64bf6880afc0a97be084cTest -
8دورية أكاديمية
المؤلفون: Dieter C Gruenert, R Geoffrey Sargent
المصدر: Molecular Therapy: Nucleic Acids, Vol 1, Iss C (2012)
مصطلحات موضوعية: Therapeutics. Pharmacology, RM1-950
العلاقة: http://www.sciencedirect.com/science/article/pii/S2162253116300646Test; https://doaj.org/toc/2162-2531Test; https://doaj.org/article/9448df6b1e5247ccb7a878e047fcc640Test
الإتاحة: https://doi.org/10.1038/mtna.2011.7Test
https://doaj.org/article/9448df6b1e5247ccb7a878e047fcc640Test -
9دورية أكاديمية
المؤلفون: Takashi Furuta, Tsuyoshi Shuto, Shogo Shimasaki, Yuko Ohira, Mary Ann Suico, Dieter C Gruenert, Hirofumi Kai
المساهمون: The Pennsylvania State University CiteSeerX Archives
المصدر: ftp://ftp.ncbi.nlm.nih.gov/pub/pmc/c5/41/BMC_Mol_Biol_2008_Apr_21_9_39.tar.gz
وصف الملف: application/zip
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10
المؤلفون: Kevin V. Morris, Sheena Saayman, Pad Chivukula, Amanda Ackley, Jon Burdach, Kiyoshi Tachikawa, Dieter C. Gruenert, Matthew Clemson, Marc S. Weinberg
المصدر: Molecular Therapy
مصطلحات موضوعية: 0301 basic medicine, congenital, hereditary, and neonatal diseases and abnormalities, Cystic Fibrosis, Cystic Fibrosis Transmembrane Conductance Regulator, Biology, Models, Biological, 03 medical and health sciences, Transcription (biology), Drug Discovery, Transcriptional regulation, Genetics, Humans, RNA, Antisense, Gene, Molecular Biology, Regulation of gene expression, Pharmacology, Intron, Molecular biology, Cystic fibrosis transmembrane conductance regulator, Chromatin, DNA-Binding Proteins, 030104 developmental biology, Sense strand, Gene Expression Regulation, Genetic Loci, biology.protein, Molecular Medicine, Original Article, RNA, Long Noncoding, Protein Binding
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::1000f1ab26ea38447e57a17e49b0562eTest