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1دورية أكاديمية
المؤلفون: Eve Fouarge, Arnaud Monseur, Bruno Boulanger, Mélanie Annoussamy, Andreea M. Seferian, Silvana De Lucia, Charlotte Lilien, Leen Thielemans, Khazal Paradis, Belinda S. Cowling, Chris Freitag, Bradley P. Carlin, Laurent Servais, the NatHis-MTM Study Group
المصدر: Orphanet Journal of Rare Diseases, Vol 16, Iss 1, Pp 1-11 (2021)
مصطلحات موضوعية: Bayesian analysis, Centronuclear myopathy, Complex innovative clinical trial design, Disease progression model, Natural history data, Medicine
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/1750-1172Test
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2دورية أكاديمية
المؤلفون: Fouarge, Eve, Monseur, Arnaud, Boulanger, Bruno, Annoussamy, Mélanie, Seferian, Andreea M., De Lucia, Silvana, Lilien, Charlotte, Thielemans, Leen, Paradis, Khazal, Cowling, Belinda S., Freitag, Chris, Carlin, Bradley P., Servais, Laurent
المصدر: Orphanet Journal of Rare Diseases, 16 (1), 3 (2021-01)
مصطلحات موضوعية: Bayesian analysis, Centronuclear myopathy, Complex innovative clinical trial design, Disease progression model, Natural history data, Human health sciences, Neurology, Pediatrics, Sciences de la santé humaine, Neurologie, Pédiatrie
العلاقة: urn:issn:1750-1172; https://orbi.uliege.be/handle/2268/268493Test; info:hdl:2268/268493; scopus-id:2-s2.0-85098948662; info:pmid:33407688
الإتاحة: https://doi.org/10.1186/s13023-020-01663-7Test
https://orbi.uliege.be/handle/2268/268493Test