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1دورية أكاديمية
المؤلفون: E. V. Melnikova, V. A. Merkulov, O. V. Merkulova
المصدر: Ведомости Научного центра экспертизы средств медицинского применения, Vol 14, Iss 1, Pp 29-41 (2024)
مصطلحات موضوعية: gene and cell therapy, unregistered medicinal products, hospital exemption, expanded access, compassionate use, medical technologies, biomedical cell product for individual medical use, Medicine (General), R5-920
وصف الملف: electronic resource
العلاقة: https://www.vedomostincesmp.ru/jour/article/view/615Test; https://doaj.org/toc/1991-2919Test; https://doaj.org/toc/2619-1172Test
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2دورية أكاديمية
المؤلفون: Theo Leitner, Cyrus Khandanpour, Knut Wendelin, Fuat Oduncu, Christoph Kimmich, Ralph Naumann, Miriam Kull, Hartmut Goldschmidt, Martin Ehmer, Claudia Kiewitz, Hans Salwender
المصدر: Frontiers in Hematology, Vol 3 (2024)
مصطلحات موضوعية: isatuximab, multiple myeloma, relapsed/refractory, real-world, compassionate use, Neoplasms. Tumors. Oncology. Including cancer and carcinogens, RC254-282
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/frhem.2024.1335161/fullTest; https://doaj.org/toc/2813-3935Test
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3دورية أكاديمية
المؤلفون: Enver Aydilek, Gerald Wulf, Friedrich Schwarz, Ulrike Bacher, Mathias Rummel, Olga Stiefel, Andrea Kerkhoff, Markus Maulhardt, Thomas Melchardt, Thomas Pabst, Georg Lenz, Evgenii Shumilov
المصدر: Cancer Medicine, Vol 13, Iss 10, Pp n/a-n/a (2024)
مصطلحات موضوعية: compassionate use program, mantle cell lymphoma, outcomes, pirtobrutinib, Neoplasms. Tumors. Oncology. Including cancer and carcinogens, RC254-282
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/2045-7634Test
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4دورية أكاديمية
المصدر: Global & Regional Health Technology Assessment, Vol 11, Iss 1 (2024)
مصطلحات موضوعية: Compassionate use program, Economic impact, Italy, Medical technology, R855-855.5
وصف الملف: electronic resource
العلاقة: https://journals.aboutscience.eu/index.php/grhta/article/view/2735Test; https://doaj.org/toc/2284-2403Test; https://doaj.org/toc/2283-5733Test
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5دورية أكاديمية
المصدر: Orphanet Journal of Rare Diseases, Vol 18, Iss 1, Pp 1-14 (2023)
مصطلحات موضوعية: Compassionate use, Rare disease, Orphan drug, Case reports, Expanded access, Medicine
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/1750-1172Test
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6دورية أكاديمية
المؤلفون: Hui-Ying Liu, Xiao-Fei Bi, Ya-Jun Wang, Feng-Jie Xie, Hong Zhang, Yu-Cheng Zhu, Yan Zhang, Zhi-Hui Wang, Di Wu, Huan Meng, Yi-Lu Lin, Lin-Qiong Liu, Shu-Xiao Qiu, Yan Gao, Kai Kang, Yang Gao
المصدر: Frontiers in Pediatrics, Vol 12 (2024)
مصطلحات موضوعية: Contezolid, Compassionate use, Toddler, Community-acquired pneumonia, Staphylococcus aureus, Gram-positive bacterial infection, Pediatrics, RJ1-570
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fped.2024.1321447/fullTest; https://doaj.org/toc/2296-2360Test
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7دورية أكاديمية
المؤلفون: Sandra Fontanals, Anna Esteve, Andrea González, Cristina Ibáñez, Javier Martínez, Ricard Mesía, Ana Clopés
المصدر: Cancer Medicine, Vol 12, Iss 16, Pp 17112-17125 (2023)
مصطلحات موضوعية: cancer, compassionate use, off‐label use, survival, treatment outcomes, Neoplasms. Tumors. Oncology. Including cancer and carcinogens, RC254-282
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/2045-7634Test
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8دورية أكاديمية
المؤلفون: Shee, Kevin, Ahn, Justin, Hamouche, Fadl, Mena, Jorge, Chi, Thomas, Stoller, Marshall L
مصطلحات موضوعية: Biomedical and Clinical Sciences, Clinical Sciences, Transplantation, Rare Diseases, Urologic Diseases, Kidney Disease, Digestive Diseases, Organ Transplantation, Liver Disease, Renal and urogenital, Adolescent, Female, Humans, Compassionate Use Trials, Hyperoxaluria, Oxalates, Renal Dialysis, Treatment Outcome, Urology & Nephrology, Clinical sciences
وصف الملف: application/pdf
الوصول الحر: https://escholarship.org/uc/item/5vn5f6p4Test
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9دورية أكاديمية
المؤلفون: Andrés Tittarelli, Cristian Pereda, María A. Gleisner, Mercedes N. López, Iván Flores, Fabián Tempio, Alvaro Lladser, Adnane Achour, Fermín E. González, Claudia Durán-Aniotz, Juan P. Miranda, Milton Larrondo, Flavio Salazar-Onfray
المصدر: Vaccines, Vol 12, Iss 4, p 357 (2024)
مصطلحات موضوعية: immunotherapy, vaccine, melanoma, dendritic cell, clinical trials, compassionate use, Medicine
وصف الملف: electronic resource
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10
المؤلفون: Raposo, Vera Lúcia
المساهمون: NOVA School of Law|Faculdade de Direito (NSL|FD), RUN
مصطلحات موضوعية: gene therapy medicinal products, genetic tourism, compassionate use, advanced therapy medicinal products, named patient use, hospital use, SDG 16 - Peace, Justice and Strong Institutions
وصف الملف: application/pdf
العلاقة: PURE: 62705954