المؤلفون: Leslie Weber, Valentina Poletti, Elisa Magrin, Chiara Antoniani, Samia Martin, Charles Bayard, Hanem Sadek, Tristan Felix, Vasco Meneghini, Michael N. Antoniou, Wassim El-Nemer, Fulvio Mavilio, Marina Cavazzana, Isabelle Andre-Schmutz, Annarita Miccio

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 10, Iss , Pp 268-280 (2018)

مصطلحات موضوعية: Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050118300767Test; https://doaj.org/toc/2329-0501Test

الوصول الحر: https://doaj.org/article/86a442d8230844db8aa5394698431fd8Test

المؤلفون: Oriana Romano, Luca Petiti, Tristan Felix, Vasco Meneghini, Michel Portafax, Chiara Antoniani, Mario Amendola, Silvio Bicciato, Clelia Peano, Annarita Miccio

المصدر: iScience, Vol 23, Iss 4, Pp - (2020)

مصطلحات موضوعية: Science

وصف الملف: electronic resource

العلاقة: http://www.sciencedirect.com/science/article/pii/S2589004220302029Test; https://doaj.org/toc/2589-0042Test

الوصول الحر: https://doaj.org/article/df69b62e79414ae38bc26bd15a8b4d02Test

المؤلفون: Cécile Masson, Mario Amendola, Annarita Miccio, Annalisa Lattanzi, Ciaran M. Lee, Chiara Antoniani, Sophie Ramadier, Gang Bao, Olivier Alibeu, Vasco Meneghini, Tristan Felix, Matthew H. Porteus, Giulia Pavani, Fulvio Mavilio, Fatima Amor

المساهمون: Approches génétiques intégrées et nouvelles thérapies pour les maladies rares (INTEGRARE), Université d'Évry-Val-d'Essonne (UEVE)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Généthon-École pratique des hautes études (EPHE), Université Paris sciences et lettres (PSL)-Université Paris sciences et lettres (PSL), Généthon, Chromatin and gene regulation during development (Equipe Inserm U1163), Imagine - Institut des maladies génétiques (IHU) (Imagine - U1163), Institut National de la Santé et de la Recherche Médicale (INSERM)-Université de Paris (UP)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Université de Paris (UP), Plateforme Bioinformatique [SFR Necker] (BIP-D), Structure Fédérative de Recherche Necker (SFR Necker - UMS 3633 / US24), Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Centre National de la Recherche Scientifique (CNRS)-Université de Paris (UP)-Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Centre National de la Recherche Scientifique (CNRS)-Université de Paris (UP), Institut National de la Santé et de la Recherche Médicale (INSERM)-Université de Paris (UP), Rice University [Houston], Stanford University, Università degli Studi di Modena e Reggio Emilia (UNIMORE), École pratique des hautes études (EPHE), Université Paris sciences et lettres (PSL)-Université Paris sciences et lettres (PSL)-Université d'Évry-Val-d'Essonne (UEVE)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Généthon, Institut National de la Santé et de la Recherche Médicale (INSERM)-Université Paris Cité (UPCité)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Université Paris Cité (UPCité), Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Centre National de la Recherche Scientifique (CNRS)-Université Paris Cité (UPCité)-Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Centre National de la Recherche Scientifique (CNRS)-Université Paris Cité (UPCité), Institut National de la Santé et de la Recherche Médicale (INSERM)-Université Paris Cité (UPCité), Università degli Studi di Modena e Reggio Emilia = University of Modena and Reggio Emilia (UNIMORE), CCSD, Accord Elsevier, École Pratique des Hautes Études (EPHE), Chromatin and gene regulation during development, ANR-16-CE18-0004,GETH,L'Édition Génomique comme outil Thérapeutique contre les ß-Hémoglobinopathies(2016)

المصدر: Molecular Therapy
Molecular Therapy, Cell Press, 2019, 27, pp.137-150. ⟨10.1016/j.ymthe.2018.10.008⟩
Molecular Therapy, 2019, 27, pp.137-150. ⟨10.1016/j.ymthe.2018.10.008⟩

مصطلحات موضوعية: [SDV]Life Sciences [q-bio], Genetic enhancement, Anemia, Sickle Cell, Biology, Heterogeneous-Nuclear Ribonucleoproteins, Viral vector, 03 medical and health sciences, 0302 clinical medicine, Genome editing, CRISPR-Associated Protein 9, hemic and lymphatic diseases, Drug Discovery, Genetics, Humans, CRISPR, Progenitor cell, Molecular Biology, 030304 developmental biology, Gene Editing, Pharmacology, 0303 health sciences, Cas9, beta-Thalassemia, Genetic Therapy, Hematopoietic Stem Cells, 3. Good health, Cell biology, Hemoglobinopathies, [SDV] Life Sciences [q-bio], Haematopoiesis, 030220 oncology & carcinogenesis, Molecular Medicine, Original Article, CRISPR-Cas Systems, Stem cell, Plasmids, RNA, Guide, Kinetoplastida, CRISPR/Cas9 delivery, genome editing, β-hemoglobinopathies, Drug Discovery3003 Pharmaceutical Science

وصف الملف: application/pdf

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::5877ed9da54aab838a3dc0587cdf6277Test
https://doi.org/10.1016/j.ymthe.2018.10.008Test

المؤلفون: Giulia Pavani, Wassim El Nemer, Oriana Romano, Chiara Antoniani, Ante Sven Lundberg, Yukio Nakamura, Vasco Meneghini, Sara El Hoss, Fulvio Mavilio, Annarita Miccio, Annalisa Lattanzi, Thomas J. Cradick, Mario Amendola, Marina Cavazzana, Ryo Kurita, Tristan Felix, Matthew H. Porteus, Elisa Magrin, Leslie Weber

المساهمون: Approches génétiques intégrées et nouvelles thérapies pour les maladies rares (INTEGRARE), Université d'Évry-Val-d'Essonne (UEVE)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Généthon-École pratique des hautes études (EPHE), Université Paris sciences et lettres (PSL)-Université Paris sciences et lettres (PSL), Human Lymphohematopoiesis Laboratory (Equipe Inserm U1163), Imagine - Institut des maladies génétiques (IHU) (Imagine - U1163), Institut National de la Santé et de la Recherche Médicale (INSERM)-Université de Paris (UP)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Université de Paris (UP), Site de Recherche Intégrée en Cancérologie (SIRIC-ONCOLille), Université de Lille, Sciences et Technologies-Université de Lille, Sciences Humaines et Sociales-Centre Régional de Lutte contre le Cancer Oscar Lambret [Lille] (UNICANCER/Lille), Université Lille Nord de France (COMUE)-UNICANCER-Université Lille Nord de France (COMUE)-UNICANCER-Cancéropole Nord-Ouest-Université de Lille, Droit et Santé-Centre Hospitalier Régional Universitaire [Lille] (CHRU Lille), European Synchrotron Radiation Facility (ESRF), INSERM U665, affiliation inconnue, Généthon, École Pratique des Hautes Études (EPHE), Université Paris sciences et lettres (PSL)-Université Paris sciences et lettres (PSL)-Université d'Évry-Val-d'Essonne (UEVE)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Généthon, Institut National de la Santé et de la Recherche Médicale (INSERM)-Université Paris Cité (UPCité)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Université Paris Cité (UPCité), Université de Lille-UNICANCER-Université de Lille-UNICANCER-Cancéropole Nord-Ouest-Université de Lille, Droit et Santé-Centre Hospitalier Régional Universitaire [Lille] (CHRU Lille), ANR-16-CE18-0004,GETH,L'Édition Génomique comme outil Thérapeutique contre les ß-Hémoglobinopathies(2016)

المصدر: Blood
Blood, American Society of Hematology, 2018, 131, pp.1960-1973. ⟨10.1182/blood-2017-10-811505⟩
Blood, 2018, 131, pp.1960-1973. ⟨10.1182/blood-2017-10-811505⟩

مصطلحات موضوعية: 0301 basic medicine, Cell Line, Hematopoietic Stem Cells, Humans, beta-Globins, Anemia, Sickle Cell, CRISPR-Cas Systems, Fetal Hemoglobin, Gene Editing, Genetic Loci, congenital, hereditary, and neonatal diseases and abnormalities, Hereditary persistence of fetal hemoglobin, [SDV]Life Sciences [q-bio], Immunology, Biology, Biochemistry, 03 medical and health sciences, Human β-globin locus, hemic and lymphatic diseases, Fetal hemoglobin, medicine, CRISPR, Globin, Epigenetics, Genetics, Cas9, Anemia, Cell Biology, Hematology, medicine.disease, Chromatin, Sickle Cell, 030104 developmental biology, BLOOD Commentary

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::b4b03950f429c7272d83511e6c369566Test
https://hal.archives-ouvertes.fr/hal-02880783Test

المؤلفون: Oriana Romano, Annarita Miccio, Chiara Antoniani

المصدر: Stem Cells Translational Medicine

مصطلحات موضوعية: 0301 basic medicine, Anemia, Epigenetics, Hematopoiesis, Transcriptional regulation, Computational biology, Biology, Epigenesis, Genetic, 03 medical and health sciences, Translational Research Articles and Reviews, Animals, Humans, Progenitor cell, Enhancer, Gene, Transcription factor, Genetics, Enabling Technologies for Cell‐Based Clinical Translation, Gene Expression Regulation, Developmental, Cell Biology, General Medicine, Genetic Therapy, Phenotype, 030104 developmental biology, Hematopoietic Disorders, Hematopoietic Stem/Progenitor Cells, Stem cell, Developmental Biology

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::8fbfb5d005187d590e1a47198030495dTest
https://pubmed.ncbi.nlm.nih.gov/29080249Test

المؤلفون: Pietro Andreone, Paolo Caraceni, Rossella Manfredini, Licia Foscoli, Tiziana Montemurro, Rosaria Giordano, Elisa Bianchi, Ferdinando Giannone, Antonia D'Errico, Valeria Giudice, Antonio Curti, Maurizio Baldassarre, Marilena Ciciarello, Daria Sollazzo, Chiara Antoniani, Lucia Catani, Roberto M. Lemoli, Elisa Montelatici

المساهمون: Catani, Lucia, Sollazzo, Daria, Bianchi, Elisa, Ciciarello, Marilena, Antoniani, Chiara, Foscoli, Licia, Caraceni, Paolo, Giannone, Ferdinando Antonino, Baldassarre, Maurizio, Giordano, Rosaria, Montemurro, Tiziana, Montelatici, Elisa, D'Errico, Antonia, Andreone, Pietro, Giudice, Valeria, Curti, Antonio, Manfredini, Rossella, Lemoli, Roberto Massimo

مصطلحات موضوعية: 0301 basic medicine, Pathology, medicine.medical_specialty, Cancer Research, end-stage liver disease, Immunology, Biology, CD133+stem/progenitor cells, cell therapy, liver microenvironment, Immunology and Allergy, Oncology, Genetics (clinical), Cell Biology, Transplantation, Cell therapy, CD133+ stem/progenitor cells, End Stage Liver Disease, 03 medical and health sciences, 0302 clinical medicine, Granulocyte Colony-Stimulating Factor, medicine, Hepatic Stellate Cells, Humans, AC133 Antigen, Progenitor cell, Physiologic, Neovascularization, Cell Proliferation, Stem Cells, CD133+stem/progenitor cell, Coculture Techniques, Endothelial stem cell, Haematopoiesis, 030104 developmental biology, medicine.anatomical_structure, Liver, Hepatic stellate cell, 030211 gastroenterology & hepatology, Liver function, Bone marrow, Neovascularization, Physiologic, Stem Cell Transplantation, Stromal Cells, Stem cell

وصف الملف: STAMPA

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::362cf6b5a8deac4978e44754ecc2b1e9Test
https://hdl.handle.net/11380/1174072Test

المؤلفون: Lucia, Catani, Daria, Sollazzo, Elisa, Bianchi, Marilena, Ciciarello, Chiara, Antoniani, Licia, Foscoli, Paolo, Caraceni, Ferdinando Antonino, Giannone, Maurizio, Baldassarre, Rosaria, Giordano, Tiziana, Montemurro, Elisa, Montelatici, Antonia, D'Errico, Pietro, Andreone, Valeria, Giudice, Antonio, Curti, Rossella, Manfredini, Roberto Massimo, Lemoli

المصدر: Cytotherapy. 19(12)

مصطلحات موضوعية: End Stage Liver Disease, Liver, Stem Cells, Granulocyte Colony-Stimulating Factor, Hepatic Stellate Cells, Humans, Neovascularization, Physiologic, AC133 Antigen, Stromal Cells, Coculture Techniques, Cell Proliferation, Stem Cell Transplantation

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=pmid________::df4dcbbf183c311604e63c25be662bdcTest
https://pubmed.ncbi.nlm.nih.gov/28917627Test

المؤلفون: Giulia Pavani, Fulvio Mavilio, Leslie Weber, Elisa Magrin, Matthew H. Porteus, Chiara Antoniani, Annalisa Lattanzi, Annarita Miccio, Marina Cavazzana, Vasco Meneghini

المصدر: Molecular Therapy. 24:S223-S224

مصطلحات موضوعية: Pharmacology, Hereditary persistence of fetal hemoglobin, GATA1, Biology, medicine.disease, Cell morphology, Molecular biology, Haematopoiesis, hemic and lymphatic diseases, Drug Discovery, Fetal hemoglobin, Genetics, medicine, Molecular Medicine, Autologous transplantation, Progenitor cell, Stem cell, Molecular Biology

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::7abf26d0076d8b42d75e9e258116b35eTest
https://doi.org/10.1016/s1525-0016Test(16)33367-6

المؤلفون: Chiara Antoniani, Fatima Amor, Elisa Magrin, Vasco Meneghini, Leslie Weber, Fulvio Mavilio, Thomas J. Cradick, Mario Amendola, Matthew H. Porteus, Annalisa Lattanzi, Tristan Felix, Marina Cavazzana, Ante Sven Lundberg, Giulia Pavani, Oriana Romano, Annarita Miccio

المصدر: Blood. 128:321-321

مصطلحات موضوعية: Genetics, Hereditary persistence of fetal hemoglobin, Cas9, Immunology, GATA1, Cell Biology, Hematology, Biology, medicine.disease, Cell morphology, Biochemistry, Molecular biology, hemic and lymphatic diseases, Fetal hemoglobin, medicine, CRISPR, Globin, Gene

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::9f960da5c19fbeae87437dfa90fa4f5bTest
https://doi.org/10.1182/blood.v128.22.321.321Test

المؤلفون: Annalisa Lattanzi, Fulvio Mavilio, Chiara Antoniani, Mario Amendola, Giulia Pavani, Fatima Amor, Annarita Miccio

المصدر: Molecular Therapy. 24:S55

مصطلحات موضوعية: Pharmacology, Genetics, Promoter, Biology, Genome, Cell biology, Transduction (genetics), genomic DNA, Genome editing, Drug Discovery, Gene cluster, Molecular Medicine, Guide RNA, Indel, Molecular Biology

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::627ff984a3cfc58d23ee0120f9acfb6bTest
https://doi.org/10.1016/s1525-0016Test(16)32944-6