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1دورية أكاديمية
المؤلفون: Jian Qiu, Martha A. Bosch, Todd L. Stincic, Avery C. Hunker, Larry S. Zweifel, Oline K. Rønnekleiv, Martin J. Kelly
المصدر: Molecular Metabolism, Vol 66, Iss , Pp 101645- (2022)
مصطلحات موضوعية: CRISPR/SaCas9, POMC, STIM1, TRPC 5 channel, Glutamate, High fat diet, Internal medicine, RC31-1245
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S2212877822002149Test; https://doaj.org/toc/2212-8778Test
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2دورية أكاديمية
المؤلفون: Michela Lisjak, Alessia De Caneva, Thibaut Marais, Elena Barbon, Maria Grazia Biferi, Fabiola Porro, Adi Barzel, Lorena Zentilin, Mark A. Kay, Federico Mingozzi, Andrés F. Muro
المصدر: Frontiers in Genome Editing, Vol 4 (2022)
مصطلحات موضوعية: GeneRide, albumin gene targeting, mouse model, coagulation factor IX, tail clip test, CRISPR/SaCas9, Biotechnology, TP248.13-248.65, Genetics, QH426-470
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fgeed.2022.785698/fullTest; https://doaj.org/toc/2673-3439Test
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3دورية أكاديمية
المؤلفون: Kun Yan, Jiangpeng Feng, Xing Liu, Hongyun Wang, Qiaohong Li, Jiali Li, Tianmo Xu, Muhammad Sajid, Hafiz Ullah, Li Zhou, Limin Zhou, Yu Chen
المصدر: Frontiers in Microbiology, Vol 12 (2021)
مصطلحات موضوعية: hepatitis B virus, CRISPR/SaCas9, liver-specific promoter, adeno-associated virus, gene therapy, Microbiology, QR1-502
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fmicb.2021.665184/fullTest; https://doaj.org/toc/1664-302XTest
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4دورية أكاديمية
المؤلفون: Qiaoqiao Xiao, Shuliang Chen, Qiankun Wang, Zhepeng Liu, Shuai Liu, Huan Deng, Wei Hou, Dongcheng Wu, Yong Xiong, Jiafu Li, Deyin Guo
المصدر: Retrovirology, Vol 16, Iss 1, Pp 1-17 (2019)
مصطلحات موضوعية: CCR5, HIV-1, CRISPR/SaCas9, Primary CD4+ T cells, Human CD34+ hematopoietic stem/progenitor cells, Immunologic diseases. Allergy, RC581-607
وصف الملف: electronic resource
العلاقة: http://link.springer.com/article/10.1186/s12977-019-0477-yTest; https://doaj.org/toc/1742-4690Test
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5دورية أكاديمية
المؤلفون: Qiankun Wang, Shuliang Chen, Qiaoqiao Xiao, Zhepeng Liu, Shuai Liu, Panpan Hou, Li Zhou, Wei Hou, Wenzhe Ho, Chunmei Li, Li Wu, Deyin Guo
المصدر: Retrovirology, Vol 14, Iss 1, Pp 1-12 (2017)
مصطلحات موضوعية: CXCR4, HIV-1, Primary CD4+ T cells, Adeno-associated virus, CRISPR/SaCas9, Immunologic diseases. Allergy, RC581-607
وصف الملف: electronic resource
العلاقة: http://link.springer.com/article/10.1186/s12977-017-0375-0Test; https://doaj.org/toc/1742-4690Test
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6دورية أكاديمية
المؤلفون: Lisjak, Michela, de Caneva, Alessia, Marais, Thibaut, Barbon, Elena, Biferi, Maria Grazia, Porro, Fabiola, Barzel, Adi, Zentilin, Lorena, Kay, Mark, Mingozzi, Federico, Muro, Andrés
المساهمون: International Centre for Genetic Engineering and Biotechnology Trieste, Italy (ICGEB), Centre de recherche en Myologie – U974 SU-INSERM, Institut National de la Santé et de la Recherche Médicale (INSERM)-Sorbonne Université (SU), Institut de Myologie, Commissariat à l'énergie atomique et aux énergies alternatives (CEA)-Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Association française contre les myopathies (AFM-Téléthon)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Sorbonne Université (SU)-Centre National de la Recherche Scientifique (CNRS), Généthon, IRCCS Ospedale San Raffaele Milan, Italy, Tel Aviv University (TAU), Stanford University, Spark Therapeutics Philadelphia, PA, USA
المصدر: EISSN: 2673-3439 ; Frontiers in Genome Editing ; https://hal.science/hal-03862537Test ; Frontiers in Genome Editing, 2022, 4, ⟨10.3389/fgeed.2022.785698⟩
مصطلحات موضوعية: CRISPR/SaCas9, GeneRide, albumin gene targeting, coagulation factor IX, mouse model, tail clip test, [SDV]Life Sciences [q-bio]
العلاقة: info:eu-repo/semantics/altIdentifier/pmid/35359664; hal-03862537; https://hal.science/hal-03862537Test; PUBMED: 35359664; PUBMEDCENTRAL: PMC8962648
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7صورة
المؤلفون: Michela Lisjak, Alessia De Caneva, Thibaut Marais, Elena Barbon, Maria Grazia Biferi, Fabiola Porro, Adi Barzel, Lorena Zentilin, Mark A. Kay, Federico Mingozzi, Andrés F. Muro
مصطلحات موضوعية: Genetics, Molecular Biology, Genetic Engineering, Molecular Medicine, Gene and Molecular Therapy, GeneRide, albumin gene targeting, mouse model, coagulation factor IX, tail clip test, CRISPR/SaCas9
الإتاحة: https://doi.org/10.3389/fgeed.2022.785698.s001Test
https://figshare.com/articles/figure/Image1_Promoterless_Gene_Targeting_Approach_Combined_to_CRISPR_Cas9_Efficiently_Corrects_Hemophilia_B_Phenotype_in_Neonatal_Mice_tiff/19343618Test -
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المؤلفون: Michela Lisjak, Alessia De Caneva, Thibaut Marais, Elena Barbon, Maria Grazia Biferi, Fabiola Porro, Adi Barzel, Lorena Zentilin, Mark A. Kay, Federico Mingozzi, Andrés F. Muro
مصطلحات موضوعية: Genetics, Molecular Biology, Genetic Engineering, Molecular Medicine, Gene and Molecular Therapy, GeneRide, albumin gene targeting, mouse model, coagulation factor IX, tail clip test, CRISPR/SaCas9
الإتاحة: https://doi.org/10.3389/fgeed.2022.785698.s006Test
https://figshare.com/articles/dataset/Table1_Promoterless_Gene_Targeting_Approach_Combined_to_CRISPR_Cas9_Efficiently_Corrects_Hemophilia_B_Phenotype_in_Neonatal_Mice_pdf/19343648Test -
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المؤلفون: Wei Hou, Jiafu Li, Dongcheng Wu, Shuliang Chen, Shuai Liu, Zhepeng Liu, Huan Deng, Qiaoqiao Xiao, Deyin Guo, Qiankun Wang, Yong Xiong
المصدر: Retrovirology, Vol 16, Iss 1, Pp 1-17 (2019)
Retrovirologyمصطلحات موضوعية: lcsh:Immunologic diseases. Allergy, CRISPR/SaCas9, Human CD34+ hematopoietic stem/progenitor cells, medicine.disease_cause, 03 medical and health sciences, Plasmid, Virology, medicine, Progenitor cell, 030304 developmental biology, 0303 health sciences, biology, Cd4 t cell, 030306 microbiology, Cas9, Research, virus diseases, Haematopoiesis, Infectious Diseases, Hiv 1 resistance, Staphylococcus aureus, biology.protein, HIV-1, Primary CD4+ T cells, Antibody, lcsh:RC581-607, CCR5
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::b38c3096b537e94e646bd963c2b5b548Test
http://link.springer.com/article/10.1186/s12977-019-0477-yTest -
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المصدر: Dipòsit Digital de Documents de la UAB
Universitat Autònoma de Barcelonaمصطلحات موضوعية: nervous system, Mutation, Huntington's disease, CRISPR/SaCas9, Gene editing
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=dedup_wf_001::261ef40e41cf456a760abe9f2dbb9c5bTest
https://ddd.uab.cat/record/248696Test