المؤلفون: Nazma F. Ilahibaks, Thomas A. Kluiver, Olivier G. deJong, Saskia C. A. deJager, Raymond M. Schiffelers, Pieter Vader, Weng Chuan Peng, Zhiyong Lei, Joost P. G. Sluijter

المصدر: Journal of Extracellular Vesicles, Vol 13, Iss 1, Pp n/a-n/a (2024)

مصطلحات موضوعية: cholesterol‐lowering therapy, CRISPR/Cas9 delivery, exosomes, extracellular vesicles, gene therapy, increased LDL‐C uptake, Cytology, QH573-671

وصف الملف: electronic resource

العلاقة: https://doaj.org/toc/2001-3078Test

الوصول الحر: https://doaj.org/article/83cebf0ddaa745919861e6dd47a10bfcTest

المؤلفون: Ilahibaks, Nazma F, Kluiver, Thomas A, de Jong, Olivier G, de Jager, Saskia C A, Schiffelers, Raymond M, Vader, Pieter, Peng, Weng Chuan, Lei, Zhiyong, Sluijter, Joost P G

المساهمون: Experimentele Afd. Cardiologie 2, CDL Nanomedicine, Circulatory Health, Infection & Immunity, Centraal Diagnostisch Laboratorium, Cancer, CDL Cluster Onderzoek en Onderwijs, Regenerative Medicine and Stem Cells, Onderzoek Cardiovasculair Reg. Med.

مصطلحات موضوعية: Animals, CRISPR-Cas Systems, Cholesterol, LDL, Extracellular Vesicles, Hepatocytes, Mice, Proprotein Convertase 9/genetics, Sirolimus, Subtilisins, Tacrolimus Binding Protein 1A, LDLR recycling, increased LDL-C uptake, gene therapy, cholesterol-lowering therapy, exosomes, CRISPR/Cas9 delivery, Pcsk9 inactivation, Cell Biology, Histology, Journal Article

وصف الملف: application/pdf

العلاقة: https://dspace.library.uu.nl/handle/1874/451159Test

الإتاحة: https://dspace.library.uu.nl/handle/1874/451159Test

المؤلفون: Ali, Jahanzaib, Aslam, Husnain, Yousuf , Abida

المصدر: BIOEDUSCIENCE; Vol. 7 No. 3 (2023): BIOEDUSCIENCE; 339-349 ; BIOEDUSCIENCE; Vol 7 No 3 (2023): BIOEDUSCIENCE; 339-349 ; 2614-1558 ; 2614-154X ; 10.22236/jbes/7.3

مصطلحات موضوعية: hepatitis B virus, CRISPR/Cas9 delivery, AAV vectors, in vovo gene editing, Virus hepatitis B, CRISPR/Cas9, In Vivo, Vektor AAV

وصف الملف: application/pdf

العلاقة: https://journal.uhamka.ac.id/index.php/bioeduscience/article/view/12693/4165Test; https://journal.uhamka.ac.id/index.php/bioeduscience/article/view/12693Test

الإتاحة: https://doi.org/10.22236/jbes/12693Test
https://doi.org/10.22236/jbes/7.3Test
https://journal.uhamka.ac.id/index.php/bioeduscience/article/view/12693Test

المؤلفون: Xabier Osteikoetxea, Andreia Silva, Elisa Lázaro‐Ibáñez, Nikki Salmond, Olga Shatnyeva, Josia Stein, Jan Schick, Stephen Wren, Julia Lindgren, Mike Firth, Alexandra Madsen, Lorenz M. Mayr, Ross Overman, Rick Davies, Niek Dekker

المصدر: Journal of Extracellular Vesicles, Vol 11, Iss 5, Pp n/a-n/a (2022)

مصطلحات موضوعية: CRISPR/Cas9 delivery, exosomes, extracellular vesicles, gene editing, optogenetics, Cytology, QH573-671

وصف الملف: electronic resource

العلاقة: https://doaj.org/toc/2001-3078Test

الوصول الحر: https://doaj.org/article/4a8bdd5ba4bc4514895ce03bd1082822Test

المؤلفون: Kelly Godbout, Jacques P. Tremblay

المصدر: Pharmaceutics; Volume 14; Issue 10; Pages: 2129

مصطلحات موضوعية: lipid nanoparticles, gene therapy, mRNA delivery, CRISPR/Cas9 delivery, specific organ delivery

وصف الملف: application/pdf

العلاقة: Drug Delivery and Controlled Release; https://dx.doi.org/10.3390/pharmaceutics14102129Test

الإتاحة: https://doi.org/10.3390/pharmaceutics14102129Test

المؤلفون: Muhammad Naeem, Mubasher Zahir Hoque, Muhammad Ovais, Chanbasha Basheer, Irshad Ahmad

المصدر: International Journal of Molecular Sciences; Volume 22; Issue 20; Pages: 11300

مصطلحات موضوعية: smart nanoparticles, CRISPR/Cas9 delivery, therapeutic genome editing, stimulus CRISPR delivery

جغرافية الموضوع: agris

وصف الملف: application/pdf

العلاقة: Molecular Biology; https://dx.doi.org/10.3390/ijms222011300Test

الإتاحة: https://doi.org/10.3390/ijms222011300Test

المؤلفون: Hryhorowicz, Magdalena, Grześkowiak, Bartosz, Lipiński, Daniel, Olejnik, Przemysław, Zeyland, Joanna

المساهمون: Gmerek, Krzysztof

مصطلحات موضوعية: Chemistry, Medicine, Health and Life Sciences, magnetic nanoparticles, CRISPR/Cas9 delivery, magnetofection, genome editing, transfection

العلاقة: https://doi.org/10.18150/FNTBD7Test

الإتاحة: https://doi.org/10.18150/FNTBD7Test

المؤلفون: Zhen, Shuai, Takahashi, Y., Narita, S., Yang, Yi-Chen, Li, Xu

مصطلحات موضوعية: CRISPR/Cas9 delivery, aptamer-liposome chimera, prostate cancer, prostate-specific membrane antigen (PSMA), polo-like kinase 1 (PLK1)

وصف الملف: application/pdf

العلاقة: http://hdl.handle.net/2433/218755Test; Oncotarget

الإتاحة: http://hdl.handle.net/2433/218755Test

المؤلفون: Cécile Masson, Mario Amendola, Annarita Miccio, Annalisa Lattanzi, Ciaran M. Lee, Chiara Antoniani, Sophie Ramadier, Gang Bao, Olivier Alibeu, Vasco Meneghini, Tristan Felix, Matthew H. Porteus, Giulia Pavani, Fulvio Mavilio, Fatima Amor

المساهمون: Approches génétiques intégrées et nouvelles thérapies pour les maladies rares (INTEGRARE), Université d'Évry-Val-d'Essonne (UEVE)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Généthon-École pratique des hautes études (EPHE), Université Paris sciences et lettres (PSL)-Université Paris sciences et lettres (PSL), Généthon, Chromatin and gene regulation during development (Equipe Inserm U1163), Imagine - Institut des maladies génétiques (IHU) (Imagine - U1163), Institut National de la Santé et de la Recherche Médicale (INSERM)-Université de Paris (UP)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Université de Paris (UP), Plateforme Bioinformatique [SFR Necker] (BIP-D), Structure Fédérative de Recherche Necker (SFR Necker - UMS 3633 / US24), Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Centre National de la Recherche Scientifique (CNRS)-Université de Paris (UP)-Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Centre National de la Recherche Scientifique (CNRS)-Université de Paris (UP), Institut National de la Santé et de la Recherche Médicale (INSERM)-Université de Paris (UP), Rice University [Houston], Stanford University, Università degli Studi di Modena e Reggio Emilia (UNIMORE), École pratique des hautes études (EPHE), Université Paris sciences et lettres (PSL)-Université Paris sciences et lettres (PSL)-Université d'Évry-Val-d'Essonne (UEVE)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Généthon, Institut National de la Santé et de la Recherche Médicale (INSERM)-Université Paris Cité (UPCité)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Université Paris Cité (UPCité), Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Centre National de la Recherche Scientifique (CNRS)-Université Paris Cité (UPCité)-Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Centre National de la Recherche Scientifique (CNRS)-Université Paris Cité (UPCité), Institut National de la Santé et de la Recherche Médicale (INSERM)-Université Paris Cité (UPCité), Università degli Studi di Modena e Reggio Emilia = University of Modena and Reggio Emilia (UNIMORE), CCSD, Accord Elsevier, École Pratique des Hautes Études (EPHE), Chromatin and gene regulation during development, ANR-16-CE18-0004,GETH,L'Édition Génomique comme outil Thérapeutique contre les ß-Hémoglobinopathies(2016)

المصدر: Molecular Therapy
Molecular Therapy, Cell Press, 2019, 27, pp.137-150. ⟨10.1016/j.ymthe.2018.10.008⟩
Molecular Therapy, 2019, 27, pp.137-150. ⟨10.1016/j.ymthe.2018.10.008⟩

مصطلحات موضوعية: [SDV]Life Sciences [q-bio], Genetic enhancement, Anemia, Sickle Cell, Biology, Heterogeneous-Nuclear Ribonucleoproteins, Viral vector, 03 medical and health sciences, 0302 clinical medicine, Genome editing, CRISPR-Associated Protein 9, hemic and lymphatic diseases, Drug Discovery, Genetics, Humans, CRISPR, Progenitor cell, Molecular Biology, 030304 developmental biology, Gene Editing, Pharmacology, 0303 health sciences, Cas9, beta-Thalassemia, Genetic Therapy, Hematopoietic Stem Cells, 3. Good health, Cell biology, Hemoglobinopathies, [SDV] Life Sciences [q-bio], Haematopoiesis, 030220 oncology & carcinogenesis, Molecular Medicine, Original Article, CRISPR-Cas Systems, Stem cell, Plasmids, RNA, Guide, Kinetoplastida, CRISPR/Cas9 delivery, genome editing, β-hemoglobinopathies, Drug Discovery3003 Pharmaceutical Science

وصف الملف: application/pdf

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::5877ed9da54aab838a3dc0587cdf6277Test
https://doi.org/10.1016/j.ymthe.2018.10.008Test

المؤلفون: Lattanzi, Annalisa, Meneghini, Vasco, Pavani, Giulia, Amor, Fatima, Ramadier, Sophie, Felix, Tristan, Antoniani, Chiara, Masson, Cecile, Alibeu, Olivier, Lee, Ciaran, Porteus, Matthew H., Bao, Gang, Amendola, Mario, Mavilio, Fulvio, Miccio, Annarita

المساهمون: Lattanzi, Annalisa, Meneghini, Vasco, Pavani, Giulia, Amor, Fatima, Ramadier, Sophie, Felix, Tristan, Antoniani, Chiara, Masson, Cecile, Alibeu, Olivier, Lee, Ciaran, Porteus, Matthew H., Bao, Gang, Amendola, Mario, Mavilio, Fulvio, Miccio, Annarita

مصطلحات موضوعية: CRISPR/Cas9 delivery, genome editing, β-hemoglobinopathie, Molecular Medicine, Molecular Biology, Genetic, Pharmacology, Drug Discovery3003 Pharmaceutical Science

العلاقة: info:eu-repo/semantics/altIdentifier/pmid/30424953; info:eu-repo/semantics/altIdentifier/wos/WOS:000454708300015; volume:27; issue:1; firstpage:137; lastpage:150; numberofpages:14; journal:MOLECULAR THERAPY; http://hdl.handle.net/11380/1172498Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85056268645; https://www.journals.elsevier.com/molecular-therapyTest

الإتاحة: https://doi.org/10.1016/j.ymthe.2018.10.008Test
http://hdl.handle.net/11380/1172498Test
https://www.journals.elsevier.com/molecular-therapyTest