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1دورية أكاديمية
المؤلفون: Francesco Muntoni, Barry J. Byrne, Hugh J. McMillan, Monique M. Ryan, Brenda L. Wong, Juergen Dukart, Amita Bansal, Valerie Cosson, Roxana Dreghici, Maitea Guridi, Michael Rabbia, Hannah Staunton, Giridhar S. Tirucherai, Karl Yen, Xiling Yuan, Kathryn R. Wagner, the Taldefgrobep Alfa Study Group
المصدر: Neurology and Therapy, Vol 13, Iss 1, Pp 183-219 (2024)
مصطلحات موضوعية: Clinical trial, Duchenne muscular dystrophy, Taldefgrobep alfa, Neuromuscular disorder, Myostatin, Neurology. Diseases of the nervous system, RC346-429
وصف الملف: electronic resource
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2دورية أكاديمية
المؤلفون: Brenda L. Wong, Suzanne Summer, Paul S. Horn, Meilan M. Rutter, Irina Rybalsky, Cuixia Tian, Karen C. Shellenbarger, Heidi J. Kalkwarf
المصدر: Journal of Cachexia, Sarcopenia and Muscle, Vol 14, Iss 6, Pp 2804-2812 (2023)
مصطلحات موضوعية: Appendicular lean mass (ALM), Appendicular lean mass index (ALMI), Becker muscular dystrophy (BMD), Dual energy‐X‐ray absorptiometry (DXA), Duchenne muscular dystrophy (DMD), Genotype, Diseases of the musculoskeletal system, RC925-935, Human anatomy, QM1-695
وصف الملف: electronic resource
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3دورية أكاديمية
المؤلفون: Craig M McDonald, Jessica R Marden, Perry B Shieh, Brenda L Wong, Henry Lane, Adina Zhang, Ha Nguyen, Molly Frean, Panayiota Trifillis, Karyn Koladicz, James Signorovitch
المصدر: Journal of Comparative Effectiveness Research, Vol 12, Iss 4 (2023)
مصطلحات موضوعية: clinical outcomes, deflazacort, disease milestones, duchenne muscular dystrophy, efficacy, prednisone/prednisolon, Public aspects of medicine, RA1-1270
العلاقة: https://doaj.org/toc/2042-6313Test; https://doaj.org/article/be4dafdf0eb54cbb8bfe4f65177fb28dTest
الإتاحة: https://doi.org/10.57264/cer-2022-0190Test
https://doaj.org/article/be4dafdf0eb54cbb8bfe4f65177fb28dTest -
4دورية أكاديمية
المؤلفون: Eugenio Mercuri, C. McDonald, Shannon Marraffino, Sarah P. Sherlock, Jean K. Mah, C. Tian, Russell J. Butterfield, Vivek S. Purohit, Kathryn R. Wagner, Michela Guglieri, Hoda Abdel-Hamid, Enrico Bertini, J. Statland, Peter I. Karachunski, Michael Binks, Craig Campbell, Alesia Sadosky, Lawrence Charnas, Brenda L. Wong, Jeffrey P. Palmer, Yasuhiro Takeshima, Chiara Fiorillo, Anna Kostera-Pruszczyk, Francesco Muntoni
مصطلحات موضوعية: Genetics (clinical), Neurology (clinical), Neurology, Pediatrics, Perinatology and Child Health
العلاقة: url:https://www.openaccessrepository.it/communities/itmirrorTest; https://www.openaccessrepository.it/record/86759Test
الإتاحة: https://doi.org/10.1016/j.nmd.2021.01.001Test
https://www.openaccessrepository.it/record/86759Test -
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المؤلفون: Brenda L, Wong, Tiffany, Cook, Hawken, Miller
المصدر: Journal of Comparative Effectiveness Research. 11:779-786
مصطلحات موضوعية: Inflammation, Male, Muscular Dystrophy, Duchenne, Scoliosis, Pregnenediones, Health Policy, Humans, Prednisone, Child, Language
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::f74c17c055360ddc91e3f95951c2b93eTest
https://doi.org/10.2217/cer-2022-0055Test -
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المؤلفون: Alexander M. Zygmunt, Brenda L. Wong, Paul S. Horn, Joshua Lambert, Jean E. Bange, Irina Rybalsky, Wendy Chouteau, Cuixia Tian
المصدر: MusclenerveREFERENCES.
مصطلحات موضوعية: Cellular and Molecular Neuroscience, Physiology, Physiology (medical), Neurology (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::29592413ba64477c191ee162071d1a08Test
https://pubmed.ncbi.nlm.nih.gov/36444146Test -
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المؤلفون: Meilan M. Rutter, Cuixia Tian, Paul M. Hochwalt, Joshua Cole Tilden, Lindsey Hornung, Nat Nasomyont, Brenda L. Wong, Jane C. Khoury
المصدر: Muscle & Nerve. 64:710-716
مصطلحات موضوعية: medicine.medical_specialty, Physiology, Radiography, Duchenne muscular dystrophy, medicine.medical_treatment, Population, Osteoporosis, Thoracic Vertebrae, Cellular and Molecular Neuroscience, Bone Density, Physiology (medical), medicine, Humans, In patient, Child, education, Glucocorticoids, Lumbar Vertebral Fracture, education.field_of_study, Diphosphonates, business.industry, Bisphosphonate, medicine.disease, Surgery, Muscular Dystrophy, Duchenne, Neurology (clinical), business, Glucocorticoid, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::7968d29d1615901bf64d5d90ed677ba9Test
https://doi.org/10.1002/mus.27416Test -
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المؤلفون: Brenda L. Wong, May Ling Mah, Joe N. Kornegay, Jamie L. Jackson, Dongsheng Duan, Kathi Kinnett, Linda H. Cripe, Susan D. Apkon, Mena Scavina, Vamshi Rao, Stanley F. Nelson, Kevin M. Flanigan
المصدر: Journal of Neuromuscular Diseases. 8:315-322
مصطلحات موضوعية: Pediatrics, medicine.medical_specialty, Neurology, business.industry, medicine, Neurology (clinical), Muscular dystrophy, medicine.disease, business
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::65a9c31b31ece3e68c478aabec918229Test
https://doi.org/10.3233/jnd-200555Test -
9دورية أكاديمية
المؤلفون: Zhi Yon Charles Toh, May Thandar Aung-Htut, Gavin Pinniger, Abbie M Adams, Sudarsan Krishnaswarmy, Brenda L Wong, Sue Fletcher, Steve D Wilton
المصدر: PLoS ONE, Vol 11, Iss 1, p e0145620 (2016)
وصف الملف: electronic resource
العلاقة: http://europepmc.org/articles/PMC4706350?pdf=renderTest; https://doaj.org/toc/1932-6203Test
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المؤلفون: Brenda L. Wong, Joshua Cole Tilden, Jane C. Khoury, Lindsey Hornung, P. Hochwalt, Nat Nasomyont, I. Rybalsky, Cuixia Tian, E. Jackson, C. Keefe, Meilan M. Rutter
المصدر: Osteoporosis International. 31:2449-2459
مصطلحات موضوعية: Adult, 0301 basic medicine, medicine.medical_specialty, Adolescent, Endocrinology, Diabetes and Metabolism, Duchenne muscular dystrophy, Osteoporosis, Long bone, Population, 030209 endocrinology & metabolism, Young Adult, 03 medical and health sciences, 0302 clinical medicine, Bone Density, Teriparatide, Internal medicine, medicine, Humans, education, Adverse effect, Bone mineral, education.field_of_study, Bone Density Conservation Agents, business.industry, medicine.disease, Rheumatology, Muscular Dystrophy, Duchenne, medicine.anatomical_structure, 030101 anatomy & morphology, business, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::c4423bafd467efec18c424b140b4a491Test
https://doi.org/10.1007/s00198-020-05549-zTest