دورية أكاديمية

Antisense oligonucleotide splicing modulation as a novel Cystic Fibrosis therapeutic approach for the W1282X nonsense mutation

التفاصيل البيبلوغرافية
العنوان: Antisense oligonucleotide splicing modulation as a novel Cystic Fibrosis therapeutic approach for the W1282X nonsense mutation
المؤلفون: Oren, Yifat S., Avizur-Barchad, Ofra, Ozeri-Galai, Efrat, Elgrabli, Renana, Schirelman, Meital R., Blinder, Tehilla, Stampfer, Chava D., Ordan, Merav, Laselva, Onofrio, Cohen-Cymberknoh, Malena, Kerem, Eitan, Bear, Christine E, Kerem, Batsheva
المصدر: Journal of Cystic Fibrosis ; volume 21, issue 4, page 630-636 ; ISSN 1569-1993
بيانات النشر: Elsevier BV
سنة النشر: 2022
المجموعة: ScienceDirect (Elsevier - Open Access Articles via Crossref)
مصطلحات موضوعية: Pulmonary and Respiratory Medicine, Pediatrics, Perinatology and Child Health
نوع الوثيقة: article in journal/newspaper
اللغة: English
DOI: 10.1016/j.jcf.2021.12.012
الإتاحة: https://doi.org/10.1016/j.jcf.2021.12.012Test
https://api.elsevier.com/content/article/PII:S156919932102172X?httpAccept=text/xmlTest
https://api.elsevier.com/content/article/PII:S156919932102172X?httpAccept=text/plainTest
حقوق: https://www.elsevier.com/tdm/userlicense/1.0Test/ ; http://creativecommons.org/licenses/by-nc-nd/4.0Test/
رقم الانضمام: edsbas.E8AB2E45
قاعدة البيانات: BASE