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1دورية أكاديمية
المؤلفون: Mudde, Anne CA, Kuo, Caroline Y, Kohn, Donald B, Booth, Claire
المصدر: The Journal of Allergy and Clinical Immunology In Practice. 12(5)
مصطلحات موضوعية: Medical Biotechnology, Biomedical and Clinical Sciences, Pediatric, Genetics, Stem Cell Research, Biotechnology, Regenerative Medicine, Gene Therapy, Development of treatments and therapeutic interventions, 5.2 Cellular and gene therapies, Inflammatory and immune system, Humans, Gene Editing, Genetic Therapy, Animals, CRISPR-Cas Systems, Agammaglobulinemia, Severe Combined Immunodeficiency, Hematopoietic Stem Cell Transplantation, Gene editing, Inborn errors of immunity, CRISPR/Cas, Prime editing, Base editing, Immunology
وصف الملف: application/pdf
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2دورية أكاديمية
المؤلفون: Hołubowicz, Rafał, Palczewski, Krzysztof
المصدر: Trends in Molecular Medicine. 29(7)
مصطلحات موضوعية: CRISPR-Cas, base editing, genome editing, prime editing, retinal degeneration, Animals, Mice, Humans, Gene Editing, CRISPR-Cas Systems, Mutation
وصف الملف: application/pdf
الوصول الحر: https://escholarship.org/uc/item/43s897c5Test
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3دورية أكاديمية
المؤلفون: Yan, Alexander, Du, Samuel, Palczewski, Krzysztof
مصطلحات موضوعية: Base editing, Genome editing, Leber congenital amaurosis, Prime editing, Retina physiology, Retinal degeneration, Retinopathies, Humans, Gene Editing, CRISPR-Cas Systems, Genetic Therapy, Retinal Diseases, Retina
وصف الملف: application/pdf
الوصول الحر: https://escholarship.org/uc/item/55d0f9c2Test
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4دورية أكاديمية
المؤلفون: Ranzau, Brodie L, Rallapalli, Kartik L, Evanoff, Mallory, Paesani, Francesco, Komor, Alexis C
المصدر: ChemBioChem. 24(16)
مصطلحات موضوعية: Genetics, Generic health relevance, adenosine deamination chemistry, base editing, directed evolution, nucleic acids, genome editing, Adenosine Deaminase, Gene Editing, RNA, Transfer, DNA, Mutation, CRISPR-Cas Systems, Medicinal and Biomolecular Chemistry, Biochemistry and Cell Biology, Organic Chemistry
وصف الملف: application/pdf
الوصول الحر: https://escholarship.org/uc/item/8wx3v2q6Test
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5دورية أكاديمية
المؤلفون: McAuley, Grace E, Yiu, Gloria, Chang, Patrick C, Newby, Gregory A, Campo-Fernandez, Beatriz, Fitz-Gibbon, Sorel T, Wu, Xiaomeng, Kang, Sung-Hae L, Garibay, Amber, Butler, Jeffrey, Christian, Valentina, Wong, Ryan L, Everette, Kelcee A, Azzun, Anthony, Gelfer, Hila, Seet, Christopher S, Narendran, Aru, Murguia-Favela, Luis, Romero, Zulema, Wright, Nicola, Liu, David R, Crooks, Gay M, Kohn, Donald B
المصدر: Cell. 186(7)
مصطلحات موضوعية: Biomedical and Clinical Sciences, Cardiovascular Medicine and Haematology, Clinical Research, Rare Diseases, Genetics, Stem Cell Research, Biotechnology, Stem Cell Research - Nonembryonic - Human, Regenerative Medicine, Transplantation, Development of treatments and therapeutic interventions, 5.2 Cellular and gene therapies, Humans, Animals, Mice, T-Lymphocytes, Severe Combined Immunodeficiency, Gene Editing, Mice, SCID, CD3 Complex, Receptors, Antigen, T-Cell, CD3D severe combined immune deficiency, CITE-seq, artificial thymic organoid, base editing, hematopoietic stem and progenitor cells, Biological Sciences, Medical and Health Sciences, Developmental Biology, Biological sciences, Biomedical and clinical sciences
وصف الملف: application/pdf
الوصول الحر: https://escholarship.org/uc/item/4z6394j3Test
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6دورية أكاديمية
المؤلفون: Doo Eun Choi, Jun Wan Shin, Sophia Zeng, Eun Pyo Hong, Jae-Hyun Jang, Jacob M Loupe, Vanessa C Wheeler, Hannah E Stutzman, Ben Kleinstiver, Jong-Min Lee
المصدر: eLife, Vol 12 (2024)
مصطلحات موضوعية: Huntington's disease, duplicated interruption, uninterrupted repeat, base editing, CAG-to-CAA conversion, CAG repeat instability, Medicine, Science, Biology (General), QH301-705.5
وصف الملف: electronic resource
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7دورية أكاديمية
المؤلفون: Evan W. Kleinboehl, Kanut Laoharawee, Walker S. Lahr, Jacob D. Jensen, Joseph J. Peterson, Jason B. Bell, Beau R. Webber, Branden S. Moriarity
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 2, Pp 101253- (2024)
مصطلحات موضوعية: CRISPR, genome modification, cas9, base editing, prime editing, reporter plasmid, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S232905012400069XTest; https://doaj.org/toc/2329-0501Test
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8دورية أكاديمية
المؤلفون: Citra N.Z. Mattar, Wei Leong Chew, Poh San Lai
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 2, Pp 101229- (2024)
مصطلحات موضوعية: embryo, fetus, base editing, CRISPR-Cas9, viral vectors, lipid nanoparticles, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050124000457Test; https://doaj.org/toc/2329-0501Test
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9دورية أكاديمية
المؤلفون: Alessandro Nicolia, Nunzia Scotti, Nunzio D’Agostino, Giovanna Festa, Lorenza Sannino, Gaetano Aufiero, Shin-ichi Arimura, Teodoro Cardi
المصدر: Plant Methods, Vol 20, Iss 1, Pp 1-12 (2024)
مصطلحات موضوعية: Mitochondrial DNA editing, MitoTALEN, MitoTALECD, Genome editing, Base editing, Chondriome, Plant culture, SB1-1110, Biology (General), QH301-705.5
وصف الملف: electronic resource
العلاقة: https://doaj.org/toc/1746-4811Test
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10دورية أكاديمية
المؤلفون: Gongchen Zhang, Chenyu Zhu, Xiaohan Chen, Jifang Yan, Dongyu Xue, Zixuan Wei, Guohui Chuai, Qi Liu
المصدر: Genomics, Proteomics & Bioinformatics, Vol 21, Iss 6, Pp 1237-1245 (2023)
مصطلحات موضوعية: Gene editing, Base editing, Pleiotropy, CRISPR/Cas9, gRNA design, Biology (General), QH301-705.5
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S1672022922000821Test; https://doaj.org/toc/1672-0229Test