المؤلفون: Jeng, Jing-Yi, Carlton, Adam, Goodyear, Richard, Chinowsky, Colbie, Ceriani, Federico, Johnson, Stuart, Sung, Tsung-Chang, Dayn, Yelena, Richardson, Guy, Bowl, Michael, Brown, Steve, Marcotti, Walter, Manor, Uri

مصطلحات موضوعية: AAVs, Eps8, auditory, cochlea, deafness, development, exocytosis, gene therapy, mouse, stereocilia

وصف الملف: application/pdf

الوصول الحر: https://escholarship.org/uc/item/9492k279Test

المؤلفون: Santos, Miguel Barbosa Louro dos

المساهمون: Silva, Ricardo, RUN

مصطلحات موضوعية: AAVs, Gene Therapy, Downstream, Affinity Chromatography, Magnetic Fishing, Domínio/Área Científica::Engenharia e Tecnologia::Outras Engenharias e Tecnologias

وصف الملف: application/pdf

الإتاحة: http://hdl.handle.net/10362/146989Test

المؤلفون: Liliana Mendonça, Johannes Boltze, Clévio Nóbrega

المصدر: Frontiers in Medicine, Vol 10 (2023)

مصطلحات موضوعية: regulatory landscape for ATMPs, AAVs-mediated gene delivery, riboswitch-regulated AAVs, regulatory T cells production and regulation, AAV8-mediated gene therapy combined with chemotherapy, Medicine (General), R5-920

وصف الملف: electronic resource

العلاقة: https://www.frontiersin.org/articles/10.3389/fmed.2023.1154360/fullTest; https://doaj.org/toc/2296-858XTest

الوصول الحر: https://doaj.org/article/2a9d6205006148c7ae5aec910765a848Test

المؤلفون: Jing-Yi Jeng, Adam J. Carlton, Richard J. Goodyear, Colbie Chinowsky, Federico Ceriani, Stuart L. Johnson, Tsung-Chang Sung, Yelena Dayn, Guy P. Richardson, Michael R. Bowl, Steve D.M. Brown, Uri Manor, Walter Marcotti

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 26, Iss , Pp 355-370 (2022)

مصطلحات موضوعية: mouse, auditory, cochlea, deafness, AAVs, gene therapy, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050122001048Test; https://doaj.org/toc/2329-0501Test

الوصول الحر: https://doaj.org/article/5942f8bc16104f7a85b0dffab23f1f8bTest

المؤلفون: Rodrigo Holanda Mendonça, Edmar Zanoteli

المصدر: Arquivos de Neuro-Psiquiatria, Vol 80, Iss 5 suppl 1, Pp 249-256 (2022)

مصطلحات موضوعية: Genetic Therapy, Dependovirus or Adeno-Associated Virus (AAVs), Muscular Atrophy, Spinal, Survival of Motor Neuron 1 Protein, Genetic Vectors, Neurosciences. Biological psychiatry. Neuropsychiatry, RC321-571

وصف الملف: electronic resource

العلاقة: http://www.scielo.br/scielo.php?script=sci_arttext&pid=S0004-282X2022000700249&tlng=enTest; https://doaj.org/toc/1678-4227Test

الوصول الحر: https://doaj.org/article/71b95a13e8304350bf114811455d2a9bTest

المؤلفون: Mendonça, Liliana, Boltze, Johannes, Nóbrega, Clévio

مصطلحات موضوعية: regulatory landscape for ATMPs, AAVs-mediated gene delivery, riboswitch-regulated AAVs, regulatory T cells production and regulation, AAV8-mediated gene therapy combined with chemotherapy

العلاقة: https://hdl.handle.net/10316/114699Test

الإتاحة: https://doi.org/10.3389/fmed.2023.1154360Test
https://hdl.handle.net/10316/114699Test

المؤلفون: Kai Zhou, Jinming Han, Yafeng Wang, Yaodong Zhang, Changlian Zhu

المصدر: Frontiers in Molecular Neuroscience, Vol 15 (2022)

مصطلحات موضوعية: gene therapy, AAVs, serotypes, administration routes, intravenous administration, intraparenchymal injection, Neurosciences. Biological psychiatry. Neuropsychiatry, RC321-571

وصف الملف: electronic resource

العلاقة: https://www.frontiersin.org/articles/10.3389/fnmol.2022.988914/fullTest; https://doaj.org/toc/1662-5099Test

الوصول الحر: https://doaj.org/article/76aad89740c0445b80f6f507790088b1Test

المؤلفون: Monteiro, Susana Patrícia Silva

المساهمون: Plancha, Carlos, Henrique, Domingos, Repositório da Universidade de Lisboa

مصطلحات موضوعية: Terapia génica, Vectores virais, CRISPR/Cas, AAVs, Ensaios clínicos, Domínio/Área Científica::Ciências Médicas

وصف الملف: application/pdf

الإتاحة: http://hdl.handle.net/10451/54319Test

المؤلفون: Deven Dhurandhar, Niroj Kumar Sahoo, Indumathi Mariappan, Raja Narayanan

المصدر: Indian Journal of Ophthalmology, Vol 69, Iss 9, Pp 2257-2265 (2021)

مصطلحات موضوعية: adeno-associated viral vectors (aavs), age-related macular degeneration (amd), gene delivery systems, gene therapy, inherited retinal diseases, luxturna, non-inherited retinal diseases, visual cycle, voretigene neparvovec, Ophthalmology, RE1-994

وصف الملف: electronic resource

العلاقة: http://www.ijo.in/article.asp?issn=0301-4738;year=2021;volume=69;issue=9;spage=2257;epage=2265;aulast=DhurandharTest; https://doaj.org/toc/0301-4738Test; https://doaj.org/toc/1998-3689Test

الوصول الحر: https://doaj.org/article/e033f2f2796645c0af4195239c47bfdaTest

المؤلفون: Ail, Divya, Ren, Duohao, Brazhnikova, Elena, Nouvel-Jaillard, Céline, Bertin, Stephane, Mirashrafi, Seyed, Fisson, Sylvain, Dalkara, Deniz

المساهمون: Institut de la Vision, Institut National de la Santé et de la Recherche Médicale (INSERM)-Sorbonne Université (SU)-Centre National de la Recherche Scientifique (CNRS), Approches génétiques intégrées et nouvelles thérapies pour les maladies rares (INTEGRARE), Université d'Évry-Val-d'Essonne (UEVE)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Université Paris-Saclay-Généthon, Centre Hospitalier National d'Ophtalmologie des Quinze-Vingts (CHNO), Sorbonne Université (SU), University of Mazandaran (UMZ)

المصدر: EISSN: 2329-0501 ; Molecular Therapy - Methods and Clinical Development ; https://hal.sorbonne-universite.fr/hal-03602826Test ; Molecular Therapy - Methods and Clinical Development, 2022, 24, pp.306 - 316. ⟨10.1016/j.omtm.2022.01.011⟩

مصطلحات موضوعية: non-human primates, binding antibodies, neutralizing antibodies, adeno-associated viruses, AAVs, gene therapy, NABs, BABs, [SDV.IMM.IA]Life Sciences [q-bio]/Immunology/Adaptive immunology, [SDV.BIO]Life Sciences [q-bio]/Biotechnology

العلاقة: hal-03602826; https://hal.sorbonne-universite.fr/hal-03602826Test; https://hal.sorbonne-universite.fr/hal-03602826/documentTest; https://hal.sorbonne-universite.fr/hal-03602826/file/2022-Ail-Dalkara-MTMCD.pdfTest; PUBMEDCENTRAL: PMC8844404

الإتاحة: https://doi.org/10.1016/j.omtm.2022.01.011Test
https://hal.sorbonne-universite.fr/hal-03602826Test
https://hal.sorbonne-universite.fr/hal-03602826/documentTest
https://hal.sorbonne-universite.fr/hal-03602826/file/2022-Ail-Dalkara-MTMCD.pdfTest