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1دورية أكاديمية
المؤلفون: Kate Mowrey, Hope Northrup, Peyton Rougeau, S. Shahrukh Hashmi, Darcy A. Krueger, Daniel Ebrahimi-Fakhari, Alexander J. Towbin, Andrew T. Trout, Jamie K. Capal, David Neal Franz, David Rodriguez-Buritica
المصدر: Frontiers in Neurology, Vol 12 (2021)
مصطلحات موضوعية: pancreatic neuroendocrine tumor, nonfunctional, tuberous sclerosis, surveillance, abdominal imaging, Neurology. Diseases of the nervous system, RC346-429
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fneur.2021.627672/fullTest; https://doaj.org/toc/1664-2295Test
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2دورية أكاديمية
المؤلفون: Daniel Ebrahimi-Fakhari, Ulrich Dillmann, Marina Flotats-Bastardas, Martin Poryo, Hashim Abdul-Khaliq, Mohammed Ghiath Shamdeen, Bernhard Mischo, Michael Zemlin, Sascha Meyer
المصدر: Frontiers in Pediatrics, Vol 7 (2019)
مصطلحات موضوعية: Translarna, Duchenne muscular dystrophy, DMD, non-ambulatory, nmDMD, stop codon read-through therapy, Pediatrics, RJ1-570
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/article/10.3389/fped.2019.00284/fullTest; https://doaj.org/toc/2296-2360Test
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3دورية أكاديمية
المؤلفون: Daniel Ebrahimi-Fakhari, Ulrich Dillmann, Marina Flotats-Bastardas, Martin Poryo, Hashim Abdul-Khaliq, Mohammed Ghiath Shamdeen, Bernhard Mischo, Michael Zemlin, Sascha Meyer
المصدر: Frontiers in Pediatrics, Vol 6 (2018)
مصطلحات موضوعية: Translarna, Duchenne muscular dystrophy, DMD, non-ambulatory, nmDMD, stop codon read-through therapy, Pediatrics, RJ1-570
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/article/10.3389/fped.2018.00316/fullTest; https://doaj.org/toc/2296-2360Test
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4
المؤلفون: Hashim Abdul-Khaliq, Daniel Ebrahimi-Fakhari, Michael Zemlin, Mohammed Ghiath Shamdeen, Ulrich Dillmann, Marina Flotats-Bastardas, Martin Poryo, Sascha Meyer, Bernhard Mischo
المصدر: Frontiers in Pediatrics, Vol 7 (2019)
مصطلحات موضوعية: 0301 basic medicine, Cardiac function curve, Duchenne muscular dystrophy, medicine.medical_specialty, Side effect, stop codon read-through therapy, non-ambulatory, Pulmonary function testing, 03 medical and health sciences, chemistry.chemical_compound, 0302 clinical medicine, Internal medicine, DMD, Medicine, 030102 biochemistry & molecular biology, biology, business.industry, lcsh:RJ1-570, lcsh:Pediatrics, medicine.disease, Ataluren, Clinical trial, chemistry, Pediatrics, Perinatology and Child Health, Ambulatory, biology.protein, Cardiology, Translarna, Dystrophin, business, nmDMD, 030217 neurology & neurosurgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::fa84394abf405459a72c1be4597f8a52Test
https://www.frontiersin.org/article/10.3389/fped.2019.00284/fullTest